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  • Ambroxol chaperone therapy for neuronopathic Gaucher disease: A pilot study.

    Published in:
    Annals of Clinical & Translational Neurology, 2016, v. 3, n. 3, p. 200, doi. 10.1002/acn3.292
    By:
    • Narita, Aya;
    • Shirai, Kentarou;
    • Itamura, Shinji;
    • Matsuda, Atsue;
    • Ishihara, Akiko;
    • Matsushita, Kumi;
    • Fukuda, Chisako;
    • Kubota, Norika;
    • Takayama, Rumiko;
    • Shigematsu, Hideo;
    • Hayashi, Anri;
    • Kumada, Tomohiro;
    • Yuge, Kotaro;
    • Watanabe, Yoriko;
    • Kosugi, Saori;
    • Nishida, Hiroshi;
    • Kimura, Yukiko;
    • Endo, Yusuke;
    • Higaki, Katsumi;
    • Nanba, Eiji
    Publication type:
    Article