Works matching AU Kaminsky, Stephen M.


Results: 22
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    Intracranial Delivery of CLN2 Reduces Brain Pathology in a Mouse Model of Classical Late Infantile Neuronal Ceroid Lipofuscinosis.

    Published in:
    Journal of Neuroscience, 2006, v. 26, n. 5, p. 1334, doi. 10.1523/JNEUROSCI.2676-05.2006
    By:
    • Passini, Marco A.;
    • Dodge, James C.;
    • Bu, Jie;
    • Yang, Wendy;
    • Qi Zhao;
    • Sondhi, Dolan;
    • Hackett, Neil R.;
    • Kaminsky, Stephen M.;
    • Qinwen Mao;
    • Shihabuddin, Lamya S.;
    • Cheng, Seng H.;
    • Sleat, David E.;
    • Stewart, Gregory R.;
    • Davidson, Beverly L.;
    • Lobel, Peter;
    • Crystal, Ronald G.
    Publication type:
    Article
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    Anti-Epidermal Growth Factor Receptor Gene Therapy for Glioblastoma.

    Published in:
    PLoS ONE, 2016, v. 11, n. 10, p. 1, doi. 10.1371/journal.pone.0162978
    By:
    • Hicks, Martin J.;
    • Chiuchiolo, Maria J.;
    • Ballon, Douglas;
    • Dyke, Jonathan P.;
    • Aronowitz, Eric;
    • Funato, Kosuke;
    • Tabar, Viviane;
    • Havlicek, David;
    • Fan, Fan;
    • Sondhi, Dolan;
    • Kaminsky, Stephen M.;
    • Crystal, Ronald G.
    Publication type:
    Article
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    Gene therapy for metachromatic leukodystrophy.

    Published in:
    Journal of Neuroscience Research, 2016, v. 94, n. 11, p. 1169, doi. 10.1002/jnr.23792
    By:
    • Rosenberg, Jonathan B.;
    • Kaminsky, Stephen M.;
    • Aubourg, Patrick;
    • Crystal, Ronald G.;
    • Sondhi, Dolan
    Publication type:
    Article
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    Spectrum of Ocular Manifestations in CLN2-Associated Batten (Jansky-Bielschowsky) Disease Correlate with Advancing Age and Deteriorating Neurological Function.

    Published in:
    PLoS ONE, 2013, v. 8, n. 8, p. 1, doi. 10.1371/journal.pone.0073128
    By:
    • Orlin, Anton;
    • Sondhi, Dolan;
    • Witmer, Matthew T.;
    • Wessel, Matthew M.;
    • Mezey, Jason G.;
    • Kaminsky, Stephen M.;
    • Hackett, Neil R.;
    • Yohay, Kaleb;
    • Kosofsky, Barry;
    • Souweidane, Mark M.;
    • Kaplitt, Michael G.;
    • D’Amico, Donald J.;
    • Crystal, Ronald G.;
    • Kiss, Szilárd
    Publication type:
    Article
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    Slowing late infantile Batten disease by direct brain parenchymal administration of a rh.10 adeno-associated virus expressing CLN2.

    Published in:
    Science Translational Medicine, 2020, v. 12, n. 572, p. 1, doi. 10.1126/scitranslmed.abb5413
    By:
    • Sondhi, Dolan;
    • Kaminsky, Stephen M.;
    • Hackett, Neil R.;
    • Pagovich, Odelya E.;
    • Rosenberg, Jonathan B.;
    • De, Bishnu P.;
    • Chen, Alvin;
    • Van de Graaf, Benjamin;
    • Mezey, Jason G.;
    • Mammen, Grace W.;
    • Mancenido, Denesy;
    • Xu, Fang;
    • Kosofsky, Barry;
    • Yohay, Kaleb;
    • Worgall, Stefan;
    • Kaner, Robert J.;
    • Souwedaine, Mark;
    • Greenwald, Bruce M.;
    • Kaplitt, Michael;
    • Dyke, Jonathan P.
    Publication type:
    Article
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