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A double-blind, placebo-controlled phase II study of the efficacy and safety of 2,2-dimethylbutyrate (HQK-1001), an oral fetal globin inducer, in sickle cell disease.
- Published in:
- American Journal of Hematology, 2014, v. 89, n. 7, p. 709, doi. 10.1002/ajh.23725
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- Publication type:
- Article
A dose-escalation phase IIa study of 2,2-dimethylbutyrate (HQK-1001), an oral fetal globin inducer, in sickle cell disease.
- Published in:
- American Journal of Hematology, 2013, v. 88, n. 11, p. E255, doi. 10.1002/ajh.23533
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- Publication type:
- Article
Iron chelation therapy for patients with sickle cell disease and iron overload.
- Published in:
- American Journal of Hematology, 2010, v. 85, n. 10, p. 782, doi. 10.1002/ajh.21806
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- Publication type:
- Article
Vascular at-risk genotypes and disease severity in Lebanese sickle cell disease patients.
- Published in:
- American Journal of Hematology, 2010, v. 85, n. 5, p. 395, doi. 10.1002/ajh.21688
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- Publication type:
- Article
Complications of β-thalassemia intermedia: A 12-year Lebanese experience.
- Published in:
- American Journal of Hematology, 2008, v. 83, n. 7, p. 605, doi. 10.1002/ajh.21174
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- Publication type:
- Article
Pregnancy in patients with β‐thalassemia intermedia: Outcome of mothers and newborns.
- Published in:
- American Journal of Hematology, 2006, v. 81, n. 7, p. 499, doi. 10.1002/ajh.20654
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- Publication type:
- Article
Endocrine and Bone Complications in β-Thalassemia Intermedia: Current Understanding and Treatment.
- Published in:
- BioMed Research International, 2015, v. 2015, p. 1, doi. 10.1155/2015/813098
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- Publication type:
- Article
Wide Variability in the Sensitivity and Specificity of Rotavirus Immunoassay Diagnostic Kits in Practice.
- Published in:
- Journal of Infection in Developing Countries, 2021, v. 15, n. 11, p. 1701, doi. 10.3855/jidc.11922
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- Publication type:
- Article
Safety and Effectiveness of 100 mg/kg/day Deferiprone in Patients with Thalassemia Major: A Two-Year Study.
- Published in:
- Acta Haematologica, 2005, v. 114, n. 3, p. 146, doi. 10.1159/000087888
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- Publication type:
- Article
A homozygous frameshift variant expands the clinical spectrum of SAMD9 gene defects.
- Published in:
- Clinical Genetics, 2024, v. 105, n. 2, p. 202, doi. 10.1111/cge.14439
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- Publication type:
- Article
Rotavirus Genotypes and Vaccine Effectiveness from a Sentinel, Hospital-Based, Surveillance Study for Three Consecutive Rotavirus Seasons in Lebanon.
- Published in:
- 2023
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- Publication type:
- Correction Notice
A randomized phase I/II trial of HQK-1001, an oral fetal globin gene inducer, in β-thalassaemia intermedia and Hb E/β-thalassaemia.
- Published in:
- British Journal of Haematology, 2013, v. 161, n. 4, p. 587, doi. 10.1111/bjh.12304
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- Publication type:
- Article
Levels of non-transferrin-bound iron as an index of iron overload in patients with thalassaemia intermedia.
- Published in:
- British Journal of Haematology, 2009, v. 146, n. 5, p. 569, doi. 10.1111/j.1365-2141.2009.07810.x
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- Publication type:
- Article
Efficacy and tolerability of peginterferon alpha-2a with or without ribavirin in thalassaemia major patients with chronic hepatitis C virus infection.
- Published in:
- British Journal of Haematology, 2005, v. 130, n. 4, p. 644, doi. 10.1111/j.1365-2141.2005.05645.x
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- Publication type:
- Article
Absence of cardiac siderosis by MRI T2* despite transfusion burden, hepatic and serum iron overload in Lebanese patients with sickle cell disease.
- Published in:
- European Journal of Haematology, 2009, v. 83, n. 6, p. 565, doi. 10.1111/j.1600-0609.2009.01345.x
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- Publication type:
- Article
Comparison between deferoxamine and deferiprone (L1) in iron-loaded thalassemia patients.
- Published in:
- European Journal of Haematology, 2001, v. 67, n. 1, p. 30, doi. 10.1034/j.1600-0609.2001.067001030.x
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- Publication type:
- Article
Incidence of Sickle Cell Disease and Other Hemoglobin Variants in 10,095 Lebanese Neonates.
- Published in:
- PLoS ONE, 2014, v. 9, n. 9, p. 1, doi. 10.1371/journal.pone.0105109
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- Publication type:
- Article
A phase 2 study of HQK-1001, an oral fetal haemoglobin inducer, in β-thalassaemia intermedia.
- Published in:
- British Journal of Haematology, 2014, v. 164, n. 3, p. 456, doi. 10.1111/bjh.12635
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- Publication type:
- Article
Safety and efficacy of voxelotor in pediatric patients with sickle cell disease aged 4 to 11 years.
- Published in:
- Pediatric Blood & Cancer, 2022, v. 69, n. 8, p. 1, doi. 10.1002/pbc.29716
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- Publication type:
- Article
Pharmacokinetics and safety of ticagrelor in infants and toddlers with sickle cell disease aged <24 months.
- Published in:
- 2021
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- Publication type:
- journal article
Establishment of a formal program for retinoblastoma: Feasibility of clinical coordination across borders and impact on outcome.
- Published in:
- 2019
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- Publication type:
- journal article
One-year results from a prospective randomized trial comparing phlebotomy with deferasirox for the treatment of iron overload in pediatric patients with thalassemia major following curative stem cell transplantation.
- Published in:
- 2017
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- Publication type:
- journal article
Pediatric Immune Thrombocytopenia in Lebanon: Treatment and Predictors of Outcome.
- Published in:
- 2016
- By:
- Publication type:
- letter
13-valent pneumococcal conjugate vaccine (PCV13) is immunogenic and safe in children 6-17 years of age with sickle cell disease previously vaccinated with 23-valent pneumococcal polysaccharide vaccine (PPSV23): Results of a phase 3 study.
- Published in:
- Pediatric Blood & Cancer, 2015, v. 62, n. 8, p. 1427, doi. 10.1002/pbc.25502
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- Publication type:
- Article
A multicenter study on the Lebanese experience with hereditary spherocytosis.
- Published in:
- Pediatric Blood & Cancer, 2014, v. 61, n. 10, p. 1895, doi. 10.1002/pbc.24992
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- Publication type:
- Article
Treatment of acute hepatitis C in a child with thalassemia major using weight-based peginterferon α-2b.
- Published in:
- 2006
- By:
- Publication type:
- Letter
Effect of Poloxamer 188 vs Placebo on Painful Vaso-Occlusive Episodes in Children and Adults With Sickle Cell Disease: A Randomized Clinical Trial.
- Published in:
- 2021
- By:
- Publication type:
- journal article
A review of acute chest syndrome in pediatric sickle cell disease.
- Published in:
- 2013
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- Publication type:
- journal article
Iron in sickle-cell disease: What have we learned over the years?
- Published in:
- Pediatric Blood & Cancer, 2011, v. 56, n. 2, p. 182, doi. 10.1002/pbc.22721
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- Publication type:
- Article
Prevalence of glucose-6-phosphate dehydrogenase deficiency among neonates at a tertiary care centre in Lebanon.
- Published in:
- Journal of Medical Screening, 2012, v. 19, n. 2, p. 103, doi. 10.1258/jms.2012.011138
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- Publication type:
- Article
A 3-month-old infant with gingival hypertrophy and hepatosplenomegaly. Osteopetrosis.
- Published in:
- 2008
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- Publication type:
- journal article
Beta-thalassemia Intermedia: An Overview.
- Published in:
- Pediatric Annals, 2008, v. 37, n. 5, p. 322, doi. 10.3928/00904481-20080501-06
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- Publication type:
- Article
Dorfman-Chanarin Syndrome: Case Report with Multisystem Involvement.
- Published in:
- Pediatric Annals, 2008, v. 37, n. 5, p. 353, doi. 10.3928/00904481-20080501-11
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- Publication type:
- Article
Sickle Cell Disease: New Insights into Pathophysiology and Treatment.
- Published in:
- Pediatric Annals, 2008, v. 37, n. 5, p. 311, doi. 10.3928/00904481-20080501-07
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- Publication type:
- Article
Childhood Anemias: A Success Story of Basic Science and Clinical Care.
- Published in:
- Pediatric Annals, 2008, v. 37, n. 5, p. 282, doi. 10.3928/00904481-20080501-02
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- Publication type:
- Article
Eltrombopag in pediatric chronic and refractory ITP: data from a retrospective multicenter study from Lebanon.
- Published in:
- Annals of Hematology, 2022, v. 101, n. 5, p. 991, doi. 10.1007/s00277-022-04804-z
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- Publication type:
- Article
Transfusion independence in Diamond-Blackfan anemia after deferasirox therapy.
- Published in:
- 2009
- By:
- Publication type:
- Letter
Intravenous zoledronic acid treatment in thalassemia-induced osteoporosis: results of a phase II clinical trial.
- Published in:
- Annals of Hematology, 2006, v. 85, n. 9, p. 605, doi. 10.1007/s00277-006-0136-y
- By:
- Publication type:
- Article
Rotavirus Genotypes and Vaccine Effectiveness from a Sentinel, Hospital-Based, Surveillance Study for Three Consecutive Rotavirus Seasons in Lebanon.
- Published in:
- PLoS ONE, 2016, v. 11, n. 8, p. 1, doi. 10.1371/journal.pone.0161345
- By:
- Publication type:
- Article
A Case of Pitt-Hopkins Syndrome With Absence of Hyperventilation.
- Published in:
- Journal of Child Neurology, 2013, v. 28, n. 12, p. 1698, doi. 10.1177/0883073812468054
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- Publication type:
- Article