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Therapeutic gene editing in CD34<sup>+</sup> hematopoietic progenitors from Fanconi anemia patients.
- Published in:
- EMBO Molecular Medicine, 2017, v. 9, n. 11, p. 1574, doi. 10.15252/emmm.201707540
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- Publication type:
- Article
Genome editing for scalable production of alloantigen-free lentiviral vectors for in vivo gene therapy.
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- EMBO Molecular Medicine, 2017, v. 9, n. 11, p. 1558, doi. 10.15252/emmm.201708148
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- Publication type:
- Article
Targeted gene therapy and cell reprogramming in Fanconi anemia.
- Published in:
- EMBO Molecular Medicine, 2014, v. 6, n. 6, p. 835, doi. 10.15252/emmm.201303374
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- Publication type:
- Article
Highly efficient homology-driven genome editing in human T cells by combining zinc-finger nuclease mRNA and AAV6 donor delivery.
- Published in:
- Nucleic Acids Research, 2016, v. 44, n. 3, p. 1, doi. 10.1093/nar/gkv1121
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- Publication type:
- Article
Zinc-finger nuclease-driven targeted integration into mammalian genomes using donors with limited chromosomal homology.
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- Nucleic Acids Research, 2010, v. 38, n. 15, p. e152, doi. 10.1093/nar/gkq512
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- Publication type:
- Article
Homology-driven genome editing in hematopoietic stem and progenitor cells using ZFN mRNA and AAV6 donors.
- Published in:
- Nature Biotechnology, 2015, v. 33, n. 12, p. 1256, doi. 10.1038/nbt.3408
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- Publication type:
- Article
An unbiased genome-wide analysis of zinc-finger nuclease specificity.
- Published in:
- Nature Biotechnology, 2011, v. 29, n. 9, p. 816, doi. 10.1038/nbt.1948
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- Publication type:
- Article
A TALE nuclease architecture for efficient genome editing.
- Published in:
- Nature Biotechnology, 2011, v. 29, n. 2, p. 143, doi. 10.1038/nbt.1755
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- Publication type:
- Article
Human hematopoietic stem/progenitor cells modified by zinc-finger nucleases targeted to CCR5 control HIV-1 in vivo.
- Published in:
- Nature Biotechnology, 2010, v. 28, n. 8, p. 839, doi. 10.1038/nbt.1663
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- Publication type:
- Article
Gene editing in human stem cells using zinc finger nucleases and integrase-defective lentiviral vector delivery.
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- Nature Biotechnology, 2007, v. 25, n. 11, p. 1298, doi. 10.1038/nbt1353
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- Publication type:
- Article
An improved zinc-finger nuclease architecture for highly specific genome editing.
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- Nature Biotechnology, 2007, v. 25, n. 7, p. 778, doi. 10.1038/nbt1319
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- Publication type:
- Article
Editing T cell specificity towards leukemia by zinc finger nucleases and lentiviral gene transfer.
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- Nature Medicine, 2012, v. 18, n. 5, p. 807, doi. 10.1038/nm.2700
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- Publication type:
- Article
Functional footprinting of regulatory DNA.
- Published in:
- Nature Methods, 2015, v. 12, n. 10, p. 927, doi. 10.1038/nmeth.3554
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- Publication type:
- Article
Site-specific integration and tailoring of cassette design for sustainable gene transfer.
- Published in:
- Nature Methods, 2011, v. 8, n. 10, p. 861, doi. 10.1038/nmeth.1674
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- Publication type:
- Article
Enhancing zinc-finger-nuclease activity with improved obligate heterodimeric architectures.
- Published in:
- Nature Methods, 2011, v. 8, n. 1, p. 74, doi. 10.1038/nmeth.1539
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- Publication type:
- Article
Transient cold shock enhances zinc-finger nuclease–mediated gene disruption.
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- Nature Methods, 2010, v. 7, n. 6, p. 459, doi. 10.1038/nmeth.1456
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- Publication type:
- Article
Genetic editing of HLA expression in hematopoietic stem cells to broaden their human application.
- Published in:
- Scientific Reports, 2016, p. 21757, doi. 10.1038/srep21757
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- Publication type:
- Article
In vivo cleavage of transgene donors promotes nuclease-mediated targeted integration.
- Published in:
- Biotechnology & Bioengineering, 2013, v. 110, n. 3, p. 871, doi. 10.1002/bit.24733
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- Publication type:
- Article
Generation of a triple-gene knockout mammalian cell line using engineered zinc-finger nucleases.
- Published in:
- Biotechnology & Bioengineering, 2010, v. 106, n. 1, p. 97, doi. 10.1002/bit.22654
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- Publication type:
- Article
Genome editing with engineered zinc finger nucleases.
- Published in:
- 2010
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- Publication type:
- journal article
Diversifying the structure of zinc finger nucleases for high-precision genome editing.
- Published in:
- Nature Communications, 2019, v. 10, n. 1, p. 1, doi. 10.1038/s41467-019-08867-x
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- Publication type:
- Article
Differential impact of transplantation on peripheral and tissue-associated viral reservoirs: Implications for HIV gene therapy.
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- PLoS Pathogens, 2018, v. 14, n. 3, p. 1, doi. 10.1371/journal.ppat.1006956
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- Publication type:
- Article
In vivo genome editing restores haemostasis in a mouse model of haemophilia.
- Published in:
- Nature, 2011, v. 475, n. 7355, p. 217, doi. 10.1038/nature10177
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- Publication type:
- Article
Clinical Scale Zinc Finger Nuclease-mediated Gene Editing of PD-1 in Tumor Infiltrating Lymphocytes for the Treatment of Metastatic Melanoma.
- Published in:
- Molecular Therapy, 2015, v. 23, n. 8, p. 1380, doi. 10.1038/mt.2015.71
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- Publication type:
- Article
Genomic Editing of the HIV-1 Coreceptor CCR5 in Adult Hematopoietic Stem and Progenitor Cells Using Zinc Finger Nucleases.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 6, p. 1259, doi. 10.1038/mt.2013.65
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- Publication type:
- Article
Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1.
- Published in:
- Science Translational Medicine, 2017, v. 9, n. 411, p. 1, doi. 10.1126/scitranslmed.aan0820
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- Publication type:
- Article
Highly efficient endogenous human gene correction using designed zinc-finger nucleases.
- Published in:
- Nature, 2005, v. 435, n. 7042, p. 646, doi. 10.1038/nature03556
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- Publication type:
- Article
TRF2 associates with DREF and directs promoter-selective gene expression in Drosophila.
- Published in:
- Nature, 2002, v. 420, n. 6914, p. 439, doi. 10.1038/nature01167
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- Publication type:
- Article
Supraphysiologic control over HIV-1 replication mediated by CD8 T cells expressing a re-engineered CD4-based chimeric antigen receptor.
- Published in:
- PLoS Pathogens, 2017, v. 13, n. 10, p. 1, doi. 10.1371/journal.ppat.1006613
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- Publication type:
- Article
Potent and Broad Inhibition of HIV-1 by a Peptide from the gp41 Heptad Repeat-2 Domain Conjugated to the CXCR4 Amino Terminus.
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- PLoS Pathogens, 2016, v. 12, n. 11, p. 1, doi. 10.1371/journal.ppat.1005983
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- Publication type:
- Article
Targeted genome editing in human repopulating haematopoietic stem cells.
- Published in:
- Nature, 2014, v. 510, n. 7504, p. 235, doi. 10.1038/nature13420
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- Publication type:
- Article
Targeted gene correction of ?<sub>1</sub>-antitrypsin deficiency in induced pluripotent stem cells.
- Published in:
- Nature, 2011, v. 478, n. 7369, p. 391, doi. 10.1038/nature10424
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- Publication type:
- Article
Zinc-finger Nuclease Editing of Human cxcr4 Promotes HIV-1 CD4<sup>+</sup> T Cell Resistance and Enrichment.
- Published in:
- 2012
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- Publication type:
- Art Reproduction
1003. Targeted Site-Specific Integration in Human Cells Using Designed Zinc Finger Nucleases.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S386, doi. 10.1016/j.ymthe.2006.08.1097
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- Publication type:
- Article
1040. Towards Gene Correction Therapy for Wiskott-Aldrich Syndrome Using Designed Zinc Finger Endonucleases.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S398, doi. 10.1016/j.ymthe.2006.08.1136
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- Publication type:
- Article
555. Large-Scale, Flow-Based Electroporation To Deliver Engineered Zinc Finger Protein Nucleases That Mediate High-Efficiency Disruption of the Human CCR5 Gene.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S214, doi. 10.1016/j.ymthe.2006.08.627
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- Publication type:
- Article
738. Towards Gene Correction of X-Linked SCID Using Engineered Zinc Finger Nucleases and Integrase Defective Lentiviral Delivery<sup>*</sup>.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S285, doi. 10.1016/j.ymthe.2006.08.819
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- Publication type:
- Article
758. Towards Gene Knock out Therapy for AIDS/HIV: Targeted Disruption of CCR5 Using Engineered Zinc Finger Protein Nucleases (ZFNs).
- Published in:
- Molecular Therapy, 2006, v. 13, p. S293, doi. 10.1016/j.ymthe.2006.08.842
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- Publication type:
- Article
974. Towards Gene Knock out Therapy for AIDS/HIV: Targeted Disruption of CCR5 Using Engineered Zinc Finger Protein Nucleases (ZFNs)
- Published in:
- 2005
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- Publication type:
- Abstract
379. New Zinc Finger Protein Nuclease Architectures for More Efficient Gene Modification Therapies
- Published in:
- 2005
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- Publication type:
- Abstract
337. Towards Gene Correction Therapy for Wiskott-Aldrich Syndrome with Engineered Zinc Finger Nucleases
- Published in:
- 2005
- By:
- Publication type:
- Abstract
346. Gene Correction of X-Linked SCID Using Engineered Zinc Finger Nucleases and Integration Defective Lentiviral Delivery
- Published in:
- 2005
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- Publication type:
- Abstract
85. Development of Zinc Finger Nucleases for Therapeutic Gene Correction of Sickle Cell Anemia
- Published in:
- 2005
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- Publication type:
- Abstract
DNA Ligase III Promotes Alternative Nonhomologous End-Joining during Chromosomal Translocation Formation.
- Published in:
- PLoS Genetics, 2011, v. 7, n. 6, p. 1, doi. 10.1371/journal.pgen.1002080
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- Publication type:
- Article
Off-the-shelf, steroid-resistant, IL13Rα2-specific CAR T cells for treatment of glioblastoma.
- Published in:
- Neuro-Oncology, 2022, v. 24, n. 8, p. 1318, doi. 10.1093/neuonc/noac024
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- Publication type:
- Article