Found: 10
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Laminin-111 improves muscle repair in a mouse model of merosin-deficient congenital muscular dystrophy.
- Published in:
- Human Molecular Genetics, 2014, v. 23, n. 2, p. 383, doi. 10.1093/hmg/ddt428
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- Publication type:
- Article
Systemic Administration of AAV8-α-galactosidase A Induces Humoral Tolerance in Nonhuman Primates Despite Low Hepatic Expression.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 11, p. 1999, doi. 10.1038/mt.2011.119
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- Publication type:
- Article
Timing of Therapeutic Intervention Determines Functional and Survival Outcomes in a Mouse Model of Late Infantile Batten Disease.
- Published in:
- Molecular Therapy, 2007, v. 15, n. 10, p. 1782, doi. 10.1038/sj.mt.6300249
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- Publication type:
- Article
893. Second Generation Gene Therapy Vector for Classical Late Infantile Neuronal Ceroid Lipofuscinosis.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S344, doi. 10.1016/j.ymthe.2006.08.982
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- Publication type:
- Article
217. Comparison of Hepatic Vein and Peripheral Vein Delivery of an AAV2/8 Vector Encoding Human a-Galactosidase A to Rhesus Macaques.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S84, doi. 10.1016/j.ymthe.2006.08.242
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- Publication type:
- Article
Local Delivery of a Viral Vector Mitigates Neutralization by Antiviral Antibodies and Results in Efficient Transduction of Rabbit Liver
- Published in:
- Molecular Therapy, 2005, v. 12, n. 6, p. 1043, doi. 10.1016/j.ymthe.2005.06.475
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- Publication type:
- Article
531. Balloon Catheter-Mediated Hepatic Vein Delivery of a Viral Vector Mitigates Neutralization by Anti-Viral Antibodies and Results in Efficient Transduction of Rabbit Liver
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- 2005
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- Publication type:
- Abstract
Long-term Transgene Expression from Plasmid DNA Gene Therapy Vectors Is Negatively Affected by CpG Dinucleotides
- Published in:
- Molecular Therapy, 2004, v. 10, n. 2, p. 269, doi. 10.1016/j.ymthe.2004.04.018
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- Publication type:
- Article
Efficacy of Gene Therapy for a Prototypical Lysosomal Storage Disease (GSD-II) Is Critically Dependent on Vector Dose, Transgene Promoter, and the Tissues Targeted for Vector Transduction
- Published in:
- Molecular Therapy, 2002, v. 5, n. 4, p. 436, doi. 10.1006/mthe.2002.0563
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- Publication type:
- Article
Multiply deleted [E1, polymerase-, and pTP-] adenovirus vector persists despite deletion of the preterminal protein.
- Published in:
- Journal of Gene Medicine, 2000, v. 2, n. 4, p. 250, doi. 10.1002/1521-2254(200007/08)2:4<250::AID-JGM113>3.0.CO;2-3
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- Publication type:
- Article