Works by Hauswirth, William W.

Results: 91

Nucleotide sequence evidence for rapid genotypic shifts in the bovine mitochondrial DNA D-loop.

Published in:

Nature, 1983, v. 306, n. 5941, p. 400, doi. 10.1038/306400a0

By:

Olivo, Paul D.;
Van de Walle, Michael J.;
Laipis, Philip J.;
Hauswirth, William W.

Publication type:

Article

Numb Regulates the Polarized Delivery of Cyclic Nucleotide-Gated Ion Channels in Rod Photoreceptor Cilia.

Published in:

Journal of Neuroscience, 2014, v. 34, n. 42, p. 13976, doi. 10.1523/JNEUROSCI.1938-14.2014

By:

Ramamurthy, Vasanth;
Jolicoeur, Christine;
Koutroumbas, Demetra;
Mühlhans, Johanna;
Yun-Zheng Le;
Hauswirth, William W.;
Giessl, Andreas;
Cayouette, Michel

Publication type:

Article

Disease mechanisms of X‐linked cone dystrophy caused by missense mutations in the red and green cone opsins.

Published in:

FASEB Journal, 2021, v. 35, n. 10, p. 1, doi. 10.1096/fj.202101066R

By:

Zhu, Ping;
Dyka, Frank;
Ma, Xiaojie;
Yin, Ling;
Yu, Heather;
Baehr, Wolfgang;
Hauswirth, William W.;
Deng, Wen‐Tao

Publication type:

Article

Human L- and M-opsins restore M-cone function in a mouse model for human blue cone monochromacy.

Published in:

Molecular Vision, 2018, v. 24, p. 17

By:

Wen-Tao Deng;
Jie Li;
Ping Zhu;
Chiodo, Vince A.;
Smith, W. Clay;
Freedman, Beau;
Baehr, Wolfgang;
Jijing Pang;
Hauswirth, William W.

Publication type:

Article

Safety and Effects of the Vector for the Leber Hereditary Optic Neuropathy Gene Therapy Clinical Trial.

Published in:

JAMA Ophthalmology, 2014, v. 132, n. 4, p. 409, doi. 10.1001/jamaophthalmol.2013.7630

By:

Koilkonda, Rajeshwari D.;
Hong Yu;
Tsung-Han Chou;
Feuer, William J.;
Ruggeri, Marco;
Porciatti, Vittorio;
Tse, David;
Hauswirth, William W.;
Chiodo, Vince;
Boye, Sanford L.;
Lewin, Alfred S.;
Neuringer, Martha;
Renner, Lauren;
Guy, John

Publication type:

Article

Efficient mutagenesis of the rhodopsin gene in rod photoreceptor neurons in mice.

Published in:

Nucleic Acids Research, 2011, v. 39, n. 14, p. 5955, doi. 10.1093/nar/gkr196

By:

Chan, Fung;
Hauswirth, William W.;
Wensel, Theodore G.;
Wilson, John H.

Publication type:

Article

Alternative splice variants of the USH3A gene Clarin 1 (CLRN1).

Published in:

European Journal of Human Genetics, 2011, v. 19, n. 1, p. 30, doi. 10.1038/ejhg.2010.140

By:

Västinsalo, Hanna;
Jalkanen, Reetta;
Dinculescu, Astra;
Isosomppi, Juha;
Geller, Scott;
Flannery, John G.;
Hauswirth, William W.;
Sankila, Eeva-Marja

Publication type:

Article

Dicer Inactivation Leads to Progressive Functional and Structural Degeneration of the Mouse Retina.

Published in:

Journal of Neuroscience, 2008, v. 28, n. 19, p. 4878, doi. 10.1523/JNEUROSCI.0828-08.2008

By:

Damiani, Devid;
Alexander, John J.;
O'Rourke, Jason R.;
McManus, Mike;
Jadhav, Ashutosh P.;
Cepko, Constance L.;
Hauswirth, William W.;
Harfe, Brian D.;
Strettoi, Enrica

Publication type:

Article

Gene therapy restores vision in a canine model of childhood blindness.

Published in:

Nature Genetics, 2001, v. 28, n. 1, p. 92, doi. 10.1038/88327

By:

Acland, Gregory M.;
Aguirre, Gustavo D.;
Ray, Jharna;
Zhang, Qi;
Aleman, Tomas S.;
Cideciyan, Artur V.;
Pearce-Kelling, Susan E.;
Anand, Vibha;
Zeng, Yong;
Maguire, Albert M.;
Jacobson, Samuel G.;
Hauswirth, William W.;
Bennett, Jean

Publication type:

Article

Patients and animal models of CNGβ1-deficient retinitis pigmentosa support gene augmentation approach.

Published in:

2018

By:

Petersen-Jones, Simon M.;
Occelli, Laurence M.;
Winkler, Paige A.;
Lee, Winston;
Sparrow, Janet R.;
Mai Tsukikawa;
Boye, Sanford L.;
Chiodo, Vince;
Capasso, Jenina E.;
Becirovic, Elvir;
Schön, Christian;
Seeliger, Mathias W.;
Levin, Alex V.;
Michalakis, Stylianos;
Hauswirth, William W.;
Tsang, Stephen H.;
Tsukikawa, Mai

Publication type:

journal article

Retinal angiogenesis suppression through small molecule activation of p53.

Published in:

Journal of Clinical Investigation, 2013, v. 123, n. 10, p. 4170, doi. 10.1172/JCI67315

By:

Chavala, Sai H.;
Younghee Kim;
Tudisco, Laura;
Cicatiello, Valeria;
Milde, Till;
Kerur, Nagaraj;
Claros, Nidia;
Yanni, Susan;
Guaiquil, Victor H.;
Hauswirth, William W.;
Penn, John S.;
Rafii, Shahin;
De Falco, Sandro;
Lee, Thomas C.;
Ambati, Jayakrishna

Publication type:

Article

Canine and human visual cortex intact and responsive despite early retinal blindness from RPE65 mutation.

Published in:

2007

By:

Aguirre, Geoffrey K.;
Komáromy, András M.;
Cideciyan, Artur V.;
Brainard, David H.;
Aleman, Tomas S.;
Roman, Alejandro J.;
Avants, Brian B.;
Gee, James C.;
Korczykowski, Marc;
Hauswirth, William W.;
Acland, Gregory M.;
Aguirre, Gustavo D.;
Jacobson, Samuel G.;
Komáromy, András M

Publication type:

journal article

Lentiviral Gene Transfer of Rpe65 Rescues Survival and Function of Cones in a Mouse Model of Leber Congenital Amaurosis.

Published in:

PLoS Medicine, 2006, v. 3, n. 10, p. 1892, doi. 10.1371/journal.pmed.0030347

By:

Bemelmans, Alexis-Pierre;
Kostic, Corinne;
Crippa, Sylvain V.;
Hauswirth, William W.;
Lem, Janis;
Munier, Francis L.;
Seeliger, Mathias W.;
Wenzel, Andreas;
Arsenijevic, Yvan

Publication type:

Article

Pharmacological and rAAV Gene Therapy Rescue of Visual Functions in a Blind Mouse Model of Leber Congenital Amaurosis.

Published in:

PLoS Medicine, 2005, v. 2, n. 11, p. 1177, doi. 10.1371/journal.pmed.0020333

By:

Batten, Matthew L.;
Imanishi, Yoshikazu;
Tu, Daniel C.;
Doan, Thuy;
Zhu, Li;
Pang, Jijing;
Glushakova, Lyudmila;
Moise, Alexander R.;
Baehr, Wolfgang;
Gelder, Russell N. Van;
Hauswirth, William W.;
Rieke, Fred;
Palczewski, Krzysztof

Publication type:

Article

Small GTPases Rab8a and Rab11a Are Dispensable for Rhodopsin Transport in Mouse Photoreceptors.

Published in:

PLoS ONE, 2016, v. 11, n. 8, p. 1, doi. 10.1371/journal.pone.0161236

By:

Ying, Guoxin;
Gerstner, Cecilia D.;
Frederick, Jeanne M.;
Boye, Sanford L.;
Hauswirth, William W.;
Baehr, Wolfgang

Publication type:

Article

AAV-Mediated Clarin-1 Expression in the Mouse Retina: Implications for USH3A Gene Therapy.

Published in:

PLoS ONE, 2016, v. 11, n. 2, p. 1, doi. 10.1371/journal.pone.0148874

By:

Dinculescu, Astra;
Stupay, Rachel M.;
Deng, Wen-Tao;
Dyka, Frank M.;
Min, Seok-Hong;
Boye, Sanford L.;
Chiodo, Vince A.;
Abrahan, Carolina E.;
Zhu, Ping;
Li, Qiuhong;
Strettoi, Enrica;
Novelli, Elena;
Nagel-Wolfrum, Kerstin;
Wolfrum, Uwe;
Smith, W. Clay;
Hauswirth, William W.

Publication type:

Article

Extracellular signal‐regulated kinases 1/2 are required for adult retinal ganglion cell axon regeneration induced by fibroblast growth factor‐2.

Published in:

Journal of Neuroscience Research, 2006, v. 83, n. 6, p. 985, doi. 10.1002/jnr.20803

By:

Przemyslaw S. Sapieha;
William W. Hauswirth;
Adriana Di Polo

Publication type:

Article

Gene Therapy in a Large Animal Model of PDE6A-Retinitis Pigmentosa.

Published in:

Frontiers in Neuroscience, 2017, p. 1, doi. 10.3389/fnins.2017.00342

By:

Mowat, Freya M.;
Occelli, Laurence M.;
Bartoe, Joshua T.;
Gervais, Kristen J.;
Bruewer, Ashlee R.;
Querubin, Janice;
Dinculescu, Astra;
Boye, Sanford L.;
Hauswirth, William W.;
Petersen-Jones, Simon M.

Publication type:

Article

Genetically Targeted Binary Labeling of Retinal Neurons.

Published in:

Journal of Neuroscience, 2014, v. 34, n. 23, p. 7845, doi. 10.1523/JNEUROSCI.2960-13.2014

By:

Yongling Zhu;
Jian Xu;
Hauswirth, William W.;
DeVries, Steven H.

Publication type:

Article

Cone Phosphodiesterase-6α' Restores Rod Function and Confers Distinct Physiological Properties in the Rod Phosphodiesterase-6β-Deficient rd1O Mouse.

Published in:

Journal of Neuroscience, 2013, v. 33, n. 29, p. 11745, doi. 10.1523/JNEUROSCI.1536-13.2013

By:

Wen-Tao Deng;
Sakurai, Keisuke;
Kolandaivelu, Saravanan;
Kolesnikov, Alexander V.;
Dinculescu, Astra;
Jie Li;
Ping Zhu;
Xuan Liu;
Jijing Pang;
Chiodo, Vince A.;
Boye, Sanford L.;
Bo Chang;
Ramamurthy, Visvanathan;
Kefalov, Vladimir J.;
Hauswirth, William W.

Publication type:

Article

Regenerative Medicine for the Special Senses: Restoring the Inputs.

Published in:

Journal of Neuroscience, 2012, v. 32, n. 41, p. 14053, doi. 10.1523/JNEUROSCI.3336-12.2012

By:

Bermingham-McDonogh, Olivia;
Corwin, Jeffrey T.;
Hauswirth, William W.;
Heller, Stefan;
Reed, Randall;
Reh, Thomas A.

Publication type:

Article

Mechanistic Basis for the Failure of Cone Transducin to Translocate: Why Cones Are Never Blinded by Light.

Published in:

Journal of Neuroscience, 2010, v. 30, n. 20, p. 6815, doi. 10.1523/JNEUROSCI.0613-10.2010

By:

Lobanova, Ekaterina S.;
Herrmann, Rolf;
Finkelstein, Stella;
Reidel, Boris;
Skiba, Nikolai P.;
Wen-Tao Deng;
Jo, Rebecca;
Weiss, Ellen R.;
Hauswirth, William W.;
Arshavsky, Vadim Y.

Publication type:

Article

SOD2 gene transfer protects against optic neuropathy induced by deficiency of complex I.

Published in:

Annals of Neurology, 2004, v. 56, n. 2, p. 182

By:

Xiaoping Qi;
Alfred S. Lewin;
Liang Sun;
William W. Hauswirth;
John Guy

Publication type:

Article

Rescue of a mitochondrial deficiency causing Leber hereditary optic neuropathy.

Published in:

Annals of Neurology, 2002, v. 52, n. 5, p. 534, doi. 10.1002/ana.10354

By:

Guy, John;
Qi, Xiaoping;
Pallotti, Francesco;
Schon, Eric A.;
Manfredi, Giovanni;
Carelli, Valerio;
Martinuzzi, Andrea;
Hauswirth, William W.;
Lewin, Alfred S.

Publication type:

Article

Optimal Inhibition of Choroidal Neovascularization by scAAV2 with VMD2 Promoter-driven Active Rap1a in the RPE.

Published in:

Scientific Reports, 2019, v. 9, n. 1, p. N.PAG, doi. 10.1038/s41598-019-52163-z

By:

Wang, Haibo;
Kunz, Eric;
Stoddard, Gregory J.;
Hauswirth, William W.;
Hartnett, M. Elizabeth

Publication type:

Article

Organizational motifs for ground squirrel cone bipolar cells.

Published in:

Journal of Comparative Neurology, 2012, v. 520, n. 13, p. 2864, doi. 10.1002/cne.23068

By:

Light, Adam C.;
Zhu, Yongling;
Shi, Jun;
Saszik, Shannon;
Lindstrom, Sarah;
Davidson, Laura;
Li, Xiaoyu;
Chiodo, Vince A.;
Hauswirth, William W.;
Li, Wei;
DeVries, Steven H.

Publication type:

Article

Cone Phosphodiesterase-6γ’ Subunit Augments Cone PDE6 Holoenzyme Assembly and Stability in a Mouse Model Lacking Both Rod and Cone PDE6 Catalytic Subunits.

Published in:

Frontiers in Molecular Neuroscience, 2018, p. N.PAG, doi. 10.3389/fnmol.2018.00233

By:

Deng, Wen-Tao;
Kolandaivelu, Saravanan;
Dinculescu, Astra;
Li, Jie;
Zhu, Ping;
Chiodo, Vince A.;
Ramamurthy, Visvanathan;
Hauswirth, William W.

Publication type:

Article

Selective tropism of the recombinant adeno-associated virus 9 serotype for rat cardiac tissue.

Published in:

Journal of Gene Medicine, 2010, v. 12, n. 1, p. 22, doi. 10.1002/jgm.1404

By:

Qi, Yanfei;
Liu, Xuan;
Li, Hongwei;
Shenoy, Vinayak;
Li, Qiuhong;
Hauswirth, William W.;
Sumners, Colin;
Katovich, Michael J.

Publication type:

Article

Gene Augmentation Therapy Restores Retinal Function and Visual Behavior in a Sheep Model of CNGA3 Achromatopsia.

Published in:

Molecular Therapy, 2015, v. 23, n. 9, p. 1423, doi. 10.1038/mt.2015.114

By:

Banin, Eyal;
Gootwine, Elisha;
Obolensky, Alexey;
Ezra-Elia, Raaya;
Ejzenberg, Ayala;
Zelinger, Lina;
Honig, Hen;
Rosov, Alexander;
Yamin, Esther;
Sharon, Dror;
Averbukh, Edward;
Hauswirth, William W;
Ofri, Ron

Publication type:

Article

Gene Therapy With the Caspase Activation and Recruitment Domain Reduces the Ocular Inflammatory Response.

Published in:

Molecular Therapy, 2015, v. 23, n. 5, p. 875, doi. 10.1038/mt.2015.30

By:

Ildefonso, Cristhian J;
Jaime, Henrique;
Biswal, Manas R;
Boye, Shannon E;
Li, Qiuhong;
Hauswirth, William W;
Lewin, Alfred S

Publication type:

Article

Targeted Gene Delivery to the Enteric Nervous System Using AAV: A Comparison Across Serotypes and Capsid Mutants.

Published in:

Molecular Therapy, 2015, v. 23, n. 3, p. 488, doi. 10.1038/mt.2015.7

By:

Benskey, Matthew J;
Kuhn, Nathan C;
Galligan, James J;
Garcia, Joanna;
Boye, Shannon E;
Hauswirth, William W;
Mueller, Christian;
Boye, Sanford L;
Manfredsson, Fredric P

Publication type:

Article

NADH-dehydrogenase Type-2 Suppresses Irreversible Visual Loss and Neurodegeneration in the EAE Animal Model of MS.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1876, doi. 10.1038/mt.2013.104

By:

Talla, Venu;
Yu, Hong;
Chou, Tsung-Han;
Porciatti, Vittorio;
Chiodo, Vince;
Boye, Sanford L;
Hauswirth, William W;
Lewin, Alfred S;
Guy, John

Publication type:

Article

Transient Photoreceptor Deconstruction by CNTF Enhances rAAV-Mediated Cone Functional Rescue in Late Stage CNGB3-Achromatopsia.

Published in:

Molecular Therapy, 2013, v. 21, n. 6, p. 1131, doi. 10.1038/mt.2013.50

By:

Komáromy, András M;
Rowlan, Jessica S;
Corr, Amanda T Parton;
Reinstein, Shelby L;
Boye, Sanford L;
Cooper, Ann E;
Gonzalez, Amaliris;
Levy, Britt;
Wen, Rong;
Hauswirth, William W;
Beltran, William A;
Aguirre, Gustavo D

Publication type:

Article

A Comprehensive Review of Retinal Gene Therapy.

Published in:

Molecular Therapy, 2013, v. 21, n. 3, p. 509, doi. 10.1038/mt.2012.280

By:

Boye, Shannon E;
Boye, Sanford L;
Lewin, Alfred S;
Hauswirth, William W

Publication type:

Article

ACE2 and Ang-(1-7) Confer Protection Against Development of Diabetic Retinopathy.

Published in:

Molecular Therapy, 2012, v. 20, n. 1, p. 28, doi. 10.1038/mt.2011.155

By:

Verma, Amrisha;
Shan, Zhiying;
Lei, Bo;
Yuan, Lihui;
Liu, Xuan;
Nakagawa, Takahiko;
Grant, Maria B;
Lewin, Alfred S;
Hauswirth, William W;
Raizada, Mohan K;
Li, Qiuhong

Publication type:

Article

Virally delivered Channelrhodopsin-2 Safely and Effectively Restores Visual Function in Multiple Mouse Models of Blindness.

Published in:

Molecular Therapy, 2011, v. 19, n. 7, p. 1220, doi. 10.1038/mt.2011.69

By:

Doroudchi, M. Mehdi;
Greenberg, Kenneth P.;
Jianwen Liu;
Silka, Kimberly A.;
Boyden, Edward S.;
Lockridge, Jennifer A.;
Arman, A Cyrus;
Janani, Ramesh;
Boye, Shannon E.;
Boye, Sanford L.;
Gordon, Gabriel M.;
Matteo, Benjamin C.;
Sampath, Alapakkam P;
Hauswirth, William W.;
Horsager, Alan

Publication type:

Article

Long-term Retinal Function and Structure Rescue Using Capsid Mutant AAV8 Vector in the rd10 Mouse, a Model of Recessive Retinitis Pigmentosa.

Published in:

Molecular Therapy, 2011, v. 19, n. 2, p. 234, doi. 10.1038/mt.2010.273

By:

Ji-jing Pang;
Xufeng Dai;
Boye, Shannon E.;
Barone, Ilaria;
Boye, Sanford L.;
Song Mao;
Everhart, Drew;
Dinculescu, Astra;
Li .Liu;
Umino, Yumiko;
Bo .Lei;
Bo .Chang;
Barlow, Robert;
Strettoi, Enrica;
Hauswirth, William W.

Publication type:

Article

Novel Properties of Tyrosine-mutant AAV2 Vectors in the Mouse Retina.

Published in:

Molecular Therapy, 2011, v. 19, n. 2, p. 293, doi. 10.1038/mt.2010.234

By:

Petrs-Silva, Hilda;
Dinculescu, Astra;
Qiuhong Li;
Wen-Tao Deng;
Ji-jing Pang;
Seok-Hong Min;
Chiodo, Vince;
Neeley, Andy W.;
Govindasamy, Lakshmanan;
Bennett, Antonette;
Agbandje-McKenna, Mavis;
Li Zhong;
Baozheng Li;
Jayandharan, Giridhara R.;
Srivastava, Arun;
Lewin, Alfred S.;
Hauswirth, William W.

Publication type:

Article

High-efficiency Transduction of the Mouse Retina by Tyrosine-mutant AAV Serotype Vectors.

Published in:

Molecular Therapy, 2009, v. 17, n. 3, p. 463, doi. 10.1038/mt.2008.269

By:

Petrs-Silva, Hilda;
Dinculescu, Astra;
Qiuhong Li;
Seok-Hong Min;
Chiodo, Vince;
Ji-Jing Pang;
Li Zhong;
Zolotukhin, Sergei;
Srivastava, Arun;
Lewin, Alfred S.;
Hauswirth, William W.

Publication type:

Article

Downregulation of p22phox in Retinal Pigment Epithelial Cells Inhibits Choroidal Neovascularization in Mice.

Published in:

Molecular Therapy, 2008, v. 16, n. 10, p. 1688, doi. 10.1038/mt.2008.164

By:

Qiuhong Li;
Dinculescu, Astra;
Zhiying Shan;
Miller, Rehae;
Jijing Pang;
Lewin, Alfred S.;
Raizada, Mohan K.;
Hauswirth, William W.

Publication type:

Article

Effect of Late-stage Therapy on Disease Progression in AAV-mediated Rescue of Photoreceptor Cells in the Retinoschisin-deficient Mouse.

Published in:

Molecular Therapy, 2008, v. 16, n. 6, p. 1010, doi. 10.1038/mt.2008.57

By:

Janssen, Andreas;
Min, Seok H.;
Molday, Laurie L.;
Tanimoto, Naoyuki;
Seeliger, Mathias W.;
Hauswirth, William W.;
Molday, Robert S.;
Weber, Bernhard H. F.

Publication type:

Article

881. Safety, Efficacy and Biodistribution of Recombinant AAV2-RPE65 Vector Delivered by Ocular Subretinal Injection.

Published in:

Molecular Therapy, 2006, v. 13, p. S339, doi. 10.1016/j.ymthe.2006.08.970

By:

Jacobson, Samuel G.;
Acland, Gregory M.;
Aguirre, Gustavo D.;
Aleman, Tomas S.;
Boye, Sanford L.;
Schwartz, Sharon B.;
Cideciyan, Artur V.;
Zeiss, Caroline J.;
Komaromy, Andras M.;
Roman, Alejandro J.;
Windsor, Elizabeth A. M.;
Sumaroka, Alexander;
Pearce-Kelling, Susan E.;
Conlon, Thomas J.;
Quihong Li;
Chiodo, Vincent A.;
Flotte, Terence R.;
Maguire, Albert M.;
Bennett, Jean;
Hauswirth, William W.

Publication type:

Article

419. Rescue of Cone Photoreceptors after Lentiviral Gene Transfer of Rpe65 cDNA in Knockout Mouse Models of Leber Congenital Amaurosis.

Published in:

Molecular Therapy, 2006, v. 13, p. S161, doi. 10.1016/j.ymthe.2006.08.483

By:

Bemelmans, Alexis-Pierre;
Kostic, Corinne;
Hornfeld, Dana;
Tekaya, Meriem;
Crippa, Sylvain V.;
Hauswirth, William W.;
Lem, Janis;
Seeliger, Mathias;
Wenzel, Andreas;
Arsenijevic, Yvan

Publication type:

Article

495. Transfer of LEDGF to the Mouse Retina Via Systemic AAV Vector Administration.

Published in:

Molecular Therapy, 2006, v. 13, p. S192, doi. 10.1016/j.ymthe.2006.08.565

By:

Glushakova, Lyudmyla G.;
Gorbatuyk, Marina;
Yuanging Lu;
Sihong Song;
Min Zheng;
Shinohara, Toshimichi;
Hauswirth, William W.

Publication type:

Article

Safety of Recombinant Adeno-Associated Virus Type 2–RPE65 Vector Delivered by Ocular Subretinal Injection.

Published in:

Molecular Therapy, 2006, v. 13, n. 6, p. 1074, doi. 10.1016/j.ymthe.2006.03.005

By:

Jacobson, Samuel G.;
Acland, Gregory M.;
Aguirre, Gustavo D.;
Aleman, Tomas S.;
Schwartz, Sharon B.;
Cideciyan, Artur V.;
Zeiss, Caroline J.;
Komaromy, Andras M.;
Kaushal, Shalesh;
Roman, Alejandro J.;
Windsor, Elizabeth A.M.;
Sumaroka, Alexander;
Pearce-Kelling, Susan E.;
Conlon, Thomas J.;
Chiodo, Vincent A.;
Boye, Sanford L.;
Flotte, Terence R.;
Maguire, Albert M.;
Bennett, Jean;
Hauswirth, William W.

Publication type:

Article

Gene Therapy Restores Vision-Dependent Behavior as Well as Retinal Structure and Function in a Mouse Model of RPE65 Leber Congenital Amaurosis.

Published in:

Molecular Therapy, 2006, v. 13, n. 3, p. 565, doi. 10.1016/j.ymthe.2005.09.001

By:

Pang, Ji-jing;
Chang, Bo;
Kumar, Ashok;
Nusinowitz, Steven;
Noorwez, Syed M.;
Li, Jie;
Rani, Asha;
Foster, Thomas C.;
Chiodo, Vince A.;
Doyle, Thomas;
Li, Huashi;
Malhotra, Ritu;
Teusner, Jacqueline T.;
McDowell, J. Hugh;
Min, Seok-Hong;
Li, Qiuhong;
Kaushal, Shalesh;
Hauswirth, William W.

Publication type:

Article

Long-Term Restoration of Rod and Cone Vision by Single Dose rAAV-Mediated Gene Transfer to the Retina in a Canine Model of Childhood Blindness

Published in:

Molecular Therapy, 2005, v. 12, n. 6, p. 1072, doi. 10.1016/j.ymthe.2005.08.008

By:

Acland, Gregory M.;
Aguirre, Gustavo D.;
Bennett, Jean;
Aleman, Tomas S.;
Cideciyan, Artur V.;
Bennicelli, Jeannette;
Dejneka, Nadine S.;
Pearce-Kelling, Susan E.;
Maguire, Albert M.;
Palczewski, Krzysztof;
Hauswirth, William W.;
Jacobson, Samuel G.

Publication type:

Article

Prolonged Recovery of Retinal Structure/Function after Gene Therapy in an Rs1h-Deficient Mouse Model of X-Linked Juvenile Retinoschisis

Published in:

Molecular Therapy, 2005, v. 12, n. 4, p. 644, doi. 10.1016/j.ymthe.2005.06.002

By:

Min, Seok H.;
Molday, Laurie L.;
Seeliger, Mathias W.;
Dinculescu, Astra;
Timmers, Adrian M.;
Janssen, Andreas;
Tonagel, Felix;
Tanimoto, Naoyuki;
Weber, Bernhard H.F.;
Molday, Robert S.;
Hauswirth, William W.

Publication type:

Article

Activation of the Extracellular Signal-Regulated Kinase 1/2 Pathway by AAV Gene Transfer Protects Retinal Ganglion Cells in Glaucoma

Published in:

Molecular Therapy, 2005, v. 12, n. 3, p. 402, doi. 10.1016/j.ymthe.2005.04.004

By:

Zhou, Yu;
Pernet, Vincent;
Hauswirth, William W.;
Di Polo, Adriana

Publication type:

Article

1080. rAAV Delivered Ribozyme Targeting Mouse Opsin to Rescue Vision in P23H Rats

Published in:

2005

By:

Gorbatyuk, Marina S.;
Timmers, Adrian M.;
Jijing, Pang;
Hauswirth, William W.;
Lewin, Alfred S.

Publication type:

Abstract