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Acute liver injury after SARS-CoV-2 vaccination and luspatercept administration in a patient with β-thalassemia.
- Published in:
- Annals of Hematology, 2024, v. 103, n. 3, p. 1025, doi. 10.1007/s00277-023-05591-x
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- Publication type:
- Article
Health‐related quality of life in patients with β‐thalassemia: Data from the phase 3 BELIEVE trial of luspatercept.
- Published in:
- European Journal of Haematology, 2023, v. 111, n. 1, p. 113, doi. 10.1111/ejh.13975
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- Publication type:
- Article
Key terms and definitions in acute porphyrias: Results of an international Delphi consensus led by the European porphyria network.
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- Journal of Inherited Metabolic Disease, 2023, v. 46, n. 4, p. 662, doi. 10.1002/jimd.12612
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- Publication type:
- Article
Management of luspatercept therapy in patients with transfusion‐dependent β‐thalassaemia.
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- British Journal of Haematology, 2023, v. 201, n. 5, p. 824, doi. 10.1111/bjh.18801
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- Publication type:
- Article
Therapeutic perspective for children and young adults living with thalassemia and sickle cell disease.
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- European Journal of Pediatrics, 2023, v. 182, n. 6, p. 2509, doi. 10.1007/s00431-023-04900-w
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- Publication type:
- Article
Inhibition of FGF23 is a therapeutic strategy to target hematopoietic stem cell niche defects in β-thalassemia.
- Published in:
- Science Translational Medicine, 2023, v. 15, n. 698, p. 1, doi. 10.1126/scitranslmed.abq3679
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- Publication type:
- Article
Profile of Luspatercept in the Treatment of Anemia in Adults with Non-Transfusion-Dependent β-Thalassemia (NTDT): Design, Development and Potential Place in Therapy.
- Published in:
- Drug Design, Development & Therapy, 2023, v. 17, p. 1583, doi. 10.2147/DDDT.S368584
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- Publication type:
- Article
Overall and complication‐free survival in a large cohort of patients with β‐thalassemia major followed over 50 years.
- Published in:
- American Journal of Hematology, 2023, v. 98, n. 3, p. 381, doi. 10.1002/ajh.26798
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- Publication type:
- Article
Magnitude of cumulative iron overload correlates with the severity of anemia in untreated non-transfusion-dependent β-thalassemia.
- Published in:
- Annals of Hematology, 2023, v. 102, n. 2, p. 467, doi. 10.1007/s00277-022-05046-9
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- Publication type:
- Article
Dysregulation of Iron Metabolism-Linked Genes at Myocardial Tissue and Cell Levels in Dilated Cardiomyopathy.
- Published in:
- International Journal of Molecular Sciences, 2023, v. 24, n. 3, p. 2887, doi. 10.3390/ijms24032887
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- Publication type:
- Article
Luspatercept for transfusion-dependent β-thalassemia: time to get real.
- Published in:
- 2023
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- Publication type:
- Editorial
Cancer risk and gammopathies in 2123 adults with Gaucher disease type 1 in the International Gaucher Group Gaucher Registry.
- Published in:
- American Journal of Hematology, 2022, v. 97, n. 10, p. 1337, doi. 10.1002/ajh.26675
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- Publication type:
- Article
Splenomegaly: Dare to think rare.
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- American Journal of Hematology, 2022, v. 97, n. 9, p. 1259, doi. 10.1002/ajh.26559
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- Publication type:
- Article
An open‐label, multicenter, efficacy, and safety study of deferasirox in iron‐overloaded patients with non‐transfusion‐dependent thalassemia (THETIS): 5‐year results.
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- American Journal of Hematology, 2022, v. 97, n. 8, p. E281, doi. 10.1002/ajh.26592
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- Publication type:
- Article
Pharmacological Induction of Fetal Hemoglobin in β-Thalassemia and Sickle Cell Disease: An Updated Perspective.
- Published in:
- Pharmaceuticals (14248247), 2022, v. 15, n. 6, p. 753, doi. 10.3390/ph15060753
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- Publication type:
- Article
Redox Balance in β-Thalassemia and Sickle Cell Disease: A Love and Hate Relationship.
- Published in:
- Antioxidants, 2022, v. 11, n. 5, p. 967, doi. 10.3390/antiox11050967
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- Publication type:
- Article
Ultraviolet A phototest positivity is associated with higher free erythrocyte protoporphyrin IX concentration and lower transferrin saturation values in erythropoietic protoporphyria.
- Published in:
- Photodermatology, Photoimmunology & Photomedicine, 2022, v. 38, n. 2, p. 141, doi. 10.1111/phpp.12727
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- Publication type:
- Article
Morbidity-free survival and hemoglobin level in non-transfusion-dependent β-thalassemia: a 10-year cohort study.
- Published in:
- 2022
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- Publication type:
- Letter
Advancing the care of β-thalassaemia patients with novel therapies.
- Published in:
- Blood Transfusion (17232007), 2022, v. 20, n. 1, p. 78, doi. 10.2450/2021.0265-21
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- Publication type:
- Article
Kidney Tubular Damage Secondary to Deferasirox: Systematic Literature Review.
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- Children, 2021, v. 8, n. 12, p. 1, doi. 10.3390/children8121104
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- Publication type:
- Article
2021 update on clinical trials in β‐thalassemia.
- Published in:
- American Journal of Hematology, 2021, v. 96, n. 11, p. 1518, doi. 10.1002/ajh.26316
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- Publication type:
- Article
Experts' views on COVID‐19 vaccination and the impact of the pandemic on patients with Gaucher disease.
- Published in:
- British Journal of Haematology, 2021, v. 195, n. 2, p. e135, doi. 10.1111/bjh.17693
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- Publication type:
- Article
Muscular de‐conditioning and reduced cardiac inotropism due to iron deposition reduce exercise tolerance in beta thalassemia major.
- Published in:
- American Journal of Hematology, 2021, v. 96, n. 10, p. E370, doi. 10.1002/ajh.26278
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- Publication type:
- Article
Haematological effects of oral administration of bitopertin, a glycine transport inhibitor, in patients with non‐transfusion‐dependent β‐thalassaemia.
- Published in:
- British Journal of Haematology, 2021, v. 194, n. 2, p. 474, doi. 10.1111/bjh.17479
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- Publication type:
- Article
Variations in hemoglobin level and morbidity burden in non-transfusion-dependent β-thalassemia.
- Published in:
- 2021
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- Publication type:
- Letter
CYP450 Mediates Reactive Oxygen Species Production in a Mouse Model of β-Thalassemia through an Increase in 20-HETE Activity.
- Published in:
- International Journal of Molecular Sciences, 2021, v. 22, n. 3, p. 1106, doi. 10.3390/ijms22031106
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- Publication type:
- Article
Predicting the probability of Gaucher disease in subjects with splenomegaly and thrombocytopenia.
- Published in:
- Scientific Reports, 2021, v. 11, n. 1, p. 1, doi. 10.1038/s41598-021-82296-z
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- Publication type:
- Article
Liver steatosis is highly prevalent and is associated with metabolic risk factors and liver fibrosis in adult patients with type 1 Gaucher disease.
- Published in:
- Liver International, 2020, v. 40, n. 12, p. 3061, doi. 10.1111/liv.14640
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- Publication type:
- Article
Parkinson's disease in Gaucher disease patients: what's changing in the counseling and management of patients and their relatives?
- Published in:
- 2020
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- Publication type:
- journal article
A holistic approach to iron chelation therapy in transfusion‐dependent thalassemia patients with serum ferritin below 500 μg/L.
- Published in:
- American Journal of Hematology, 2020, v. 95, n. 9, p. E230, doi. 10.1002/ajh.25860
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- Publication type:
- Article
Care of patients with hemoglobin disorders during the COVID‐19 pandemic: An overview of recommendations.
- Published in:
- American Journal of Hematology, 2020, v. 95, n. 8, p. E208, doi. 10.1002/ajh.25857
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- Publication type:
- Article
Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation.
- Published in:
- Drugs, 2020, v. 80, n. 11, p. 1053, doi. 10.1007/s40265-020-01341-9
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- Publication type:
- Article
Treatment with ferric carboxymaltose in stable patients with severe iron deficiency anemia in the emergency department.
- Published in:
- 2020
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- Publication type:
- journal article
Hyperferritinemia and diagnosis of type 1 Gaucher disease.
- Published in:
- American Journal of Hematology, 2020, v. 95, n. 5, p. 570, doi. 10.1002/ajh.25752
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- Publication type:
- Article
Less 'reds' more 'blues': hemoglobin level and depression in non-transfusion-dependent thalassemia.
- Published in:
- 2020
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- Publication type:
- letter
UGT1A1 genotype does not affect tyrosine kinase inhibitors efficacy and safety in chronic myeloid leukemia.
- Published in:
- American Journal of Hematology, 2019, v. 94, n. 11, p. E283, doi. 10.1002/ajh.25596
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- Publication type:
- Article
Quality of life in patients with β‐thalassemia: A prospective study of transfusion‐dependent and non‐transfusion‐dependent patients in Greece, Italy, Lebanon, and Thailand.
- Published in:
- American Journal of Hematology, 2019, v. 94, n. 10, p. E261, doi. 10.1002/ajh.25584
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- Publication type:
- Article
Development of a thalassemia‐related thrombosis risk scoring system.
- Published in:
- American Journal of Hematology, 2019, v. 94, n. 8, p. E207, doi. 10.1002/ajh.25502
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- Publication type:
- Article
Red blood cell distribution width as a prognostic factor of mortality in elderly patients firstly hospitalized due to heart failure.
- Published in:
- Polish Heart Journal / Kardiologia Polska, 2019, v. 77, n. 6, p. 632, doi. 10.33963/KP.14818
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- Publication type:
- Article
Current challenges in the management of patients with sickle cell disease - A report of the Italian experience.
- Published in:
- 2019
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- Publication type:
- journal article
Iron overload in congenital haemolytic anaemias: role of hepcidin and cytokines and predictive value of ferritin and transferrin saturation.
- Published in:
- British Journal of Haematology, 2019, v. 185, n. 3, p. 523, doi. 10.1111/bjh.15811
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- Publication type:
- Article
Common fetal hemoglobin variants in Lebanese patients bearing the codon 29 beta gene mutation associated with different thalassemia phenotypes.
- Published in:
- 2019
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- Publication type:
- journal article
Risk factors for heart disease in transfusion-dependent thalassemia: serum ferritin revisited.
- Published in:
- 2019
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- Publication type:
- journal article
Development of a patient‐reported outcomes symptom measure for patients with nontransfusion‐dependent thalassemia (NTDT‐PRO<sup>©</sup>).
- Published in:
- American Journal of Hematology, 2019, v. 94, n. 2, p. 171, doi. 10.1002/ajh.25343
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- Publication type:
- Article
Validation of a patient‐reported outcomes symptom measure for patients with nontransfusion‐dependent thalassemia (NTDT‐PRO<sup>©</sup>).
- Published in:
- American Journal of Hematology, 2019, v. 94, n. 2, p. 177, doi. 10.1002/ajh.25344
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- Publication type:
- Article
An unusual diagnosis in a 31-year-old man with abdominal pain and hyponatremia.
- Published in:
- 2018
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- Publication type:
- journal article
Circulating cell‐free DNA and ineffective erythropoiesis in nontransfusion‐dependent β‐thalassemia.
- Published in:
- American Journal of Hematology, 2018, v. 93, n. 11, p. E365, doi. 10.1002/ajh.25248
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- Publication type:
- Article
Non‐transferrin‐bound iron and oxidative stress during allogeneic hemopoietic stem cell transplantation in patients with or without iron overload.
- Published in:
- American Journal of Hematology, 2018, v. 93, n. 9, p. E250, doi. 10.1002/ajh.25201
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- Publication type:
- Article
What is behind a relapse of thrombotic thrombocytopenic purpura?
- Published in:
- 2018
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- Publication type:
- journal article
Low-dose Synachten test with measurement of salivary cortisol in adult patients with β-thalassemia major.
- Published in:
- Endocrine (1355008X), 2018, v. 60, n. 2, p. 348, doi. 10.1007/s12020-018-1562-z
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- Publication type:
- Article