Works by Cantore, Alessio


Results: 15
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    Liver fibrosis negatively impacts in vivo gene transfer to murine hepatocytes.

    Published in:
    Nature Communications, 2025, v. 16, n. 1, p. 1, doi. 10.1038/s41467-025-57383-8
    By:
    • Simoni, Chiara;
    • Nozi, Justine;
    • Starinieri, Francesco;
    • La Bella, Tiziana;
    • Manta, Elisabetta;
    • Negri, Camilla;
    • Biffi, Mauro;
    • Norata, Rossana;
    • Rocchi, Martina;
    • Sanvito, Francesca;
    • Ronzitti, Giuseppe;
    • Barbon, Elena;
    • Cantore, Alessio
    Publication type:
    Article
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    Phagocytosis-shielded lentiviral vectors improve liver gene therapy in nonhuman primates.

    Published in:
    Science Translational Medicine, 2019, v. 11, n. 493, p. N.PAG, doi. 10.1126/scitranslmed.aav7325
    By:
    • Milani, Michela;
    • Annoni, Andrea;
    • Moalli, Federica;
    • Liu, Tongyao;
    • Cesana, Daniela;
    • Calabria, Andrea;
    • Bartolaccini, Sara;
    • Biffi, Mauro;
    • Russo, Fabio;
    • Visigalli, Ilaria;
    • Raimondi, Andrea;
    • Patarroyo-White, Susannah;
    • Drager, Douglas;
    • Cristofori, Patrizia;
    • Ayuso, Eduard;
    • Montini, Eugenio;
    • Peters, Robert;
    • Iannacone, Matteo;
    • Cantore, Alessio;
    • Naldini, Luigi
    Publication type:
    Article
    7

    Site-specific integration and tailoring of cassette design for sustainable gene transfer.

    Published in:
    Nature Methods, 2011, v. 8, n. 10, p. 861, doi. 10.1038/nmeth.1674
    By:
    • Lombardo, Angelo;
    • Cesana, Daniela;
    • Genovese, Pietro;
    • Di Stefano, Bruno;
    • Provasi, Elena;
    • Colombo, Daniele F;
    • Neri, Margherita;
    • Magnani, Zulma;
    • Cantore, Alessio;
    • Lo Riso, Pietro;
    • Damo, Martina;
    • Pello, Oscar M;
    • Holmes, Michael C;
    • Gregory, Philip D;
    • Gritti, Angela;
    • Broccoli, Vania;
    • Bonini, Chiara;
    • Naldini, Luigi
    Publication type:
    Article
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    Liver-directed lentiviral gene therapy in a dog model of hemophilia B.

    Published in:
    Science Translational Medicine, 2015, v. 7, n. 277, p. 1, doi. 10.1126/scitranslmed.aaa1405
    By:
    • Cantore, Alessio;
    • Ranzani, Marco;
    • Bartholomae, Cynthia C.;
    • Volpin, Monica;
    • Valle, Patrizia Della;
    • Sanvito, Francesca;
    • Sergi, Lucia Sergi;
    • Gallina, Pierangela;
    • Benedicenti, Fabrizio;
    • Bellinger, Dwight;
    • Raymer, Robin;
    • Merricks, Elizabeth;
    • Bellintani, Francesca;
    • Martin, Samia;
    • Doglioni, Claudio;
    • D’Angelo, Armando;
    • VandenDriessche, Thierry;
    • Chuah, Marinee K.;
    • Schmidt, Manfred;
    • Nichols, Timothy
    Publication type:
    Article
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    Liver-directed lentiviral gene therapy corrects hemophilia A mice and achieves normal-range factor VIII activity in non-human primates.

    Published in:
    Nature Communications, 2022, v. 13, n. 1, p. 1, doi. 10.1038/s41467-022-30102-3
    By:
    • Milani, Michela;
    • Canepari, Cesare;
    • Liu, Tongyao;
    • Biffi, Mauro;
    • Russo, Fabio;
    • Plati, Tiziana;
    • Curto, Rosalia;
    • Patarroyo-White, Susannah;
    • Drager, Douglas;
    • Visigalli, Ilaria;
    • Brombin, Chiara;
    • Albertini, Paola;
    • Follenzi, Antonia;
    • Ayuso, Eduard;
    • Mueller, Christian;
    • Annoni, Andrea;
    • Naldini, Luigi;
    • Cantore, Alessio
    Publication type:
    Article