Works by Canepari, Cesare

Results: 2
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    Liver-directed lentiviral gene therapy corrects hemophilia A mice and achieves normal-range factor VIII activity in non-human primates.

    Published in:
    Nature Communications, 2022, v. 13, n. 1, p. 1, doi. 10.1038/s41467-022-30102-3
    By:
    • Milani, Michela;
    • Canepari, Cesare;
    • Liu, Tongyao;
    • Biffi, Mauro;
    • Russo, Fabio;
    • Plati, Tiziana;
    • Curto, Rosalia;
    • Patarroyo-White, Susannah;
    • Drager, Douglas;
    • Visigalli, Ilaria;
    • Brombin, Chiara;
    • Albertini, Paola;
    • Follenzi, Antonia;
    • Ayuso, Eduard;
    • Mueller, Christian;
    • Annoni, Andrea;
    • Naldini, Luigi;
    • Cantore, Alessio
    Publication type:
    Article