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Genetic justification of COVID‐19 patient outcomes using DERGA, a novel data ensemble refinement greedy algorithm.
- Published in:
- Journal of Cellular & Molecular Medicine, 2024, v. 28, n. 4, p. 1, doi. 10.1111/jcmm.18105
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- Publication type:
- Article
Novel Functional Assay to Characterize Mutations in Alternative Pathway of Complement.
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- Journal of Clinical Immunology, 2023, v. 43, n. 6, p. 1134, doi. 10.1007/s10875-023-01496-6
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- Publication type:
- Article
Concomitant Immunosuppressive Therapy and Eculizumab Use in Patients with Paroxysmal Nocturnal Hemoglobinuria: An International PNH Registry Analysis.
- Published in:
- Acta Haematologica, 2023, v. 146, n. 1, p. 1, doi. 10.1159/000526979
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- Publication type:
- Article
Maternal and fetal outcomes of pregnancy occurring after a diagnosis of immune-mediated thrombotic thrombocytopenic purpura.
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- Annals of Hematology, 2022, v. 101, n. 10, p. 2159, doi. 10.1007/s00277-022-04936-2
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- Publication type:
- Article
A 15‐year, single institution experience of anticoagulation management in paroxysmal nocturnal hemoglobinuria patients on terminal complement inhibition with history of thromboembolism.
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- American Journal of Hematology, 2022, v. 97, n. 2, p. E59, doi. 10.1002/ajh.26414
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- Publication type:
- Article
Lactate dehydrogenase versus haemoglobin: which one is the better marker in paroxysmal nocturnal haemoglobinuria?
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- British Journal of Haematology, 2022, v. 196, n. 2, p. 264, doi. 10.1111/bjh.17860
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- Publication type:
- Article
The importance of terminal complement inhibition in paroxysmal nocturnal hemoglobinuria.
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- Therapeutic Advances in Hematology, 2022, v. 13, p. 1, doi. 10.1177/20406207221091046
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- Publication type:
- Article
Major adverse cardiovascular events in survivors of immune‐mediated thrombotic thrombocytopenic purpura.
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- American Journal of Hematology, 2021, v. 96, n. 12, p. 1587, doi. 10.1002/ajh.26341
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- Publication type:
- Article
PIGN spatiotemporally regulates the spindle assembly checkpoint proteins in leukemia transformation and progression.
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- Scientific Reports, 2021, v. 11, n. 1, p. 1, doi. 10.1038/s41598-021-98218-y
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- Publication type:
- Article
Monitoring of patients with paroxysmal nocturnal hemoglobinuria on a complement inhibitor.
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- American Journal of Hematology, 2021, v. 96, n. 7, p. E232, doi. 10.1002/ajh.26176
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- Publication type:
- Article
One‐year outcomes from a phase 3 randomized trial of ravulizumab in adults with paroxysmal nocturnal hemoglobinuria who received prior eculizumab.
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- European Journal of Haematology, 2021, v. 106, n. 3, p. 389, doi. 10.1111/ejh.13564
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- Article
Reduced sensitivity of PLASMIC and French scores for the diagnosis of thrombotic thrombocytopenic purpura in older individuals.
- Published in:
- Transfusion, 2021, v. 61, n. 1, p. 266, doi. 10.1111/trf.16188
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- Publication type:
- Article
C3 inhibition with pegcetacoplan in subjects with paroxysmal nocturnal hemoglobinuria treated with eculizumab.
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- American Journal of Hematology, 2020, v. 95, n. 11, p. 1334, doi. 10.1002/ajh.25960
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- Publication type:
- Article
Pharmacokinetic and pharmacodynamic effects of ravulizumab and eculizumab on complement component 5 in adults with paroxysmal nocturnal haemoglobinuria: results of two phase 3 randomised, multicentre studies.
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- British Journal of Haematology, 2020, v. 191, n. 3, p. 476, doi. 10.1111/bjh.16711
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- Publication type:
- Article
Properdin Is a Key Player in Lysis of Red Blood Cells and Complement Activation on Endothelial Cells in Hemolytic Anemias Caused by Complement Dysregulation.
- Published in:
- Frontiers in Immunology, 2020, v. 11, p. 1, doi. 10.3389/fimmu.2020.01460
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- Publication type:
- Article
Severe COVID‐19 infection and thrombotic microangiopathy: success does not come easily.
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- British Journal of Haematology, 2020, v. 189, n. 6, p. e227, doi. 10.1111/bjh.16783
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- Article
Complementopathies and precision medicine.
- Published in:
- 2020
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- Publication type:
- journal article
Are genetic approaches still needed to cure sickle cell disease?
- Published in:
- 2020
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- Publication type:
- journal article
Are genetic approaches still needed to cure sickle cell disease?
- Published in:
- Journal of Clinical Investigation, 2020, v. 130, n. 1, p. 7, doi. 10.1172/JCI133856
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- Publication type:
- Article
Paroxysmal nocturnal hemoglobinuria without GPI-anchor deficiency.
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- 2019
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- Publication type:
- journal article
A case-control analysis of hyperhemolysis syndrome in adults and laboratory correlates of complement involvement.
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- 2019
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- Publication type:
- journal article
Defining early hematopoietic‐fated primitive streak specification of human pluripotent stem cells by the orchestrated balance of Wnt, activin, and BMP signaling.
- Published in:
- Journal of Cellular Physiology, 2019, v. 234, n. 9, p. 16136, doi. 10.1002/jcp.28272
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- Publication type:
- Article
Complement in the Pathophysiology of the Antiphospholipid Syndrome.
- Published in:
- Frontiers in Immunology, 2019, p. N.PAG, doi. 10.3389/fimmu.2019.00449
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- Publication type:
- Article
Effectiveness of eculizumab in patients with paroxysmal nocturnal hemoglobinuria (PNH) with or without aplastic anemia in the International PNH Registry.
- Published in:
- American Journal of Hematology, 2019, v. 94, n. 1, p. E37, doi. 10.1002/ajh.25334
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- Publication type:
- Article
Hypotonia and intellectual disability without dysmorphic features in a patient with PIGN-related disease.
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- BMC Medical Genetics, 2017, v. 18, p. 1, doi. 10.1186/s12881-017-0481-9
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- Publication type:
- Article
A hypomorphic PIGA gene mutation causes severe defects in neuron development and susceptibility to complement-mediated toxicity in a human iPSC model.
- Published in:
- PLoS ONE, 2017, v. 12, n. 4, p. 1, doi. 10.1371/journal.pone.0174074
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- Publication type:
- Article
Balancing Therapy with Thrombopoietin Receptor Agonists and Splenectomy in Refractory Immune Thrombocytopenic Purpura: A Case of Postsplenectomy Thrombocytosis Requiring Plateletpheresis.
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- 2016
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- Publication type:
- Case Study
Definitive Hematopoietic Multipotent Progenitor Cells Are Transiently Generated From Hemogenic Endothelial Cells in Human Pluripotent Stem Cells.
- Published in:
- Journal of Cellular Physiology, 2016, v. 231, n. 5, p. 1065, doi. 10.1002/jcp.25199
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- Publication type:
- Article
Idiopathic Inflammatory Myopathy Treated With High-Dose Immunoablative Cyclophosphamide--A Long-term Follow-up Study.
- Published in:
- JAMA Neurology, 2015, v. 72, n. 10, p. 1205, doi. 10.1001/jamaneurol.2015.1425
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- Publication type:
- Article
Detection of paroxysmal nocturnal hemoglobinuria clones to exclude inherited bone marrow failure syndromes.
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- European Journal of Haematology, 2014, v. 92, n. 6, p. 467, doi. 10.1111/ejh.12299
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- Publication type:
- Article
Early Frameshift Mutation in PIGA Identified in a Large XLID Family Without Neonatal Lethality.
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- Human Mutation, 2014, v. 35, n. 3, p. 350, doi. 10.1002/humu.22498
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- Publication type:
- Article
Differential Sensitivity to JAK Inhibitory Drugs by Isogenic Human Erythroblasts and Hematopoietic Progenitors Generated from Patient-Specific Induced Pluripotent Stem Cells.
- Published in:
- Stem Cells, 2014, v. 32, n. 1, p. 269, doi. 10.1002/stem.1545
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- Publication type:
- Article
Generation of Glycosylphosphatidylinositol Anchor Protein-Deficient Blood Cells From Human Induced Pluripotent Stem Cells.
- Published in:
- Stem Cells Translational Medicine, 2013, v. 2, n. 11, p. 819, doi. 10.5966/sctm.2013-0069
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- Publication type:
- Article
Long-term safety and efficacy of sustained eculizumab treatment in patients with paroxysmal nocturnal haemoglobinuria.
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- British Journal of Haematology, 2013, v. 162, n. 1, p. 62, doi. 10.1111/bjh.12347
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- Publication type:
- Article
Bronchobiliary Fistula and Lithoptysis after Endoscopic Retrograde Cholangiopancreatography and Liver Biopsy in a Patient with Paroxysmal Nocturnal Hemoglobinuria.
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- American Journal of Respiratory & Critical Care Medicine, 2013, v. 187, n. 4, p. 451, doi. 10.1164/ajrccm.187.4.451a
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- Article
Predictors of hemoglobin response to eculizumab therapy in paroxysmal nocturnal hemoglobinuria.
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- European Journal of Haematology, 2013, v. 90, n. 1, p. 16, doi. 10.1111/ejh.12021
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- Publication type:
- Article
Treatment of relapsing–remitting multiple sclerosis with high-dose cyclophosphamide induction followed by glatiramer acetate maintenance.
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- Multiple Sclerosis Journal, 2012, v. 18, n. 2, p. 202, doi. 10.1177/1352458511419701
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- Publication type:
- Article
Natural history of paroxysmal nocturnal hemoglobinuria clones in patients presenting as aplastic anemia.
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- European Journal of Haematology, 2011, v. 87, n. 1, p. 37, doi. 10.1111/j.1600-0609.2011.01615.x
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- Publication type:
- Article
Paroxysmal Nocturnal Hemoglobinuria from Bench to Bedside.
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- CTS: Clinical & Translational Science, 2011, v. 4, n. 3, p. 219, doi. 10.1111/j.1752-8062.2011.00262.x
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- Publication type:
- Article
High-dose cyclophosphamide for autoimmunity and alloimmunity.
- Published in:
- Immunologic Research, 2010, v. 47, n. 1-3, p. 179, doi. 10.1007/s12026-009-8149-y
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- Publication type:
- Article
Butyrate Greatly Enhances Derivation of Human Induced Pluripotent Stem Cells by Promoting Epigenetic Remodeling and the Expression of Pluripotency-Associated Genes.
- Published in:
- Stem Cells, 2010, v. 28, n. 4, p. 713, doi. 10.1002/stem.402
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- Publication type:
- Article
Successful discontinuation of anticoagulation following eculizumab administration in paroxysmal nocturnal hemoglobinuria.
- Published in:
- American Journal of Hematology, 2009, v. 84, n. 10, p. 699, doi. 10.1002/ajh.21506
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- Publication type:
- Article
Rebooting the Immune System with High-Dose Cyclophosphamide for Treatment of Refractory Myasthenia Gravis.
- Published in:
- Annals of the New York Academy of Sciences, 2008, v. 1132, p. 305, doi. 10.1196/annals.1405.033
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- Publication type:
- Article
Narrative Review: Paroxysmal Nocturnal Hemoglobinuria: The Physiology of Complement-Related Hemolytic Anemia.
- Published in:
- Annals of Internal Medicine, 2008, v. 148, n. 8, p. 587, doi. 10.7326/0003-4819-148-8-200804150-00003
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- Publication type:
- Article
Erratum: Discovery and development of the complement inhibitor eculizumab for the treatment of paroxysmal nocturnal hemoglobinuria.
- Published in:
- 2007
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- Publication type:
- Correction notice
Treatment of hepatitis-associated aplastic anemia with high-dose cyclophosphamide.
- Published in:
- Pediatric Blood & Cancer, 2007, v. 49, n. 7, p. 947, doi. 10.1002/pbc.21143
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- Publication type:
- Article
Discovery and development of the complement inhibitor eculizumab for the treatment of paroxysmal nocturnal hemoglobinuria.
- Published in:
- Nature Biotechnology, 2007, v. 25, n. 11, p. 1256, doi. 10.1038/nbt1344
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- Publication type:
- Article
High-Dose Cyclophosphamide and Stem Cell Transplantation for Refractory Systemic Lupus Erythamatosus.
- Published in:
- 2006
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- Publication type:
- Editorial
Acquired severe aplastic anemia in children: Is there a standard of care?
- Published in:
- Pediatric Blood & Cancer, 2005, v. 45, n. 3, p. 361, doi. 10.1002/pbc.20417
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- Publication type:
- Article
Acquired severe aplastic anemia in children: Is there a standard of care?
- Published in:
- Pediatric Blood & Cancer, 2004, v. 43, n. 7, p. 711, doi. 10.1002/pbc.20173
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- Publication type:
- Article