Works by Biffi, Alessandra

Results: 82

Haploinsufficiency at the CX3CR1 locus of hematopoietic stem cells favors the appearance of microglia-like cells in the central nervous system of transplant recipients.

Published in:

Nature Communications, 2024, v. 15, n. 1, p. 1, doi. 10.1038/s41467-024-54515-4

By:

Montepeloso, Annita;
Mattioli, Davide;
Pellin, Danilo;
Peviani, Marco;
Genovese, Pietro;
Biffi, Alessandra

Publication type:

Article

Therapeutic efficacy of intracerebral hematopoietic stem cell gene therapy in an Alzheimer's disease mouse model.

Published in:

Nature Communications, 2024, v. 15, n. 1, p. 1, doi. 10.1038/s41467-024-52301-w

By:

Milazzo, Rita;
Montepeloso, Annita;
Kumar, Rajesh;
Ferro, Francesca;
Cavalca, Eleonora;
Rigoni, Pietro;
Cabras, Paolo;
Ciervo, Yuri;
Das, Sabyasachi;
Capotondo, Alessia;
Pellin, Danilo;
Peviani, Marco;
Biffi, Alessandra

Publication type:

Article

Identification of Hematopoietic Stem Cell-Specific miRNAs Enables Gene Therapy of Globoid Cell Leukodystrophy.

Published in:

Science Translational Medicine, 2010, v. 2, n. 58, p. 1, doi. 10.1126/scitranslmed.3001522

By:

Gentner, Bernhard;
Visigalli, Ilaria;
Hiramatsu, Hidefumi;
Lechman, Eric;
Ungari, Silvia;
Giustacchini, Alice;
Schira, Giulia;
Amendola, Mario;
Quattrini, Angelo;
Martino, Sabata;
Orlacchio, Aldo;
Dick, John E.;
Biffi, Alessandra;
Naldini, Luigi

Publication type:

Article

Early Treatments of Fragile Children with COVID-19—Results of CLEVER (Children COVID Early Treatment), a Retrospective, Observational Study.

Published in:

Viruses (1999-4915), 2023, v. 15, n. 1, p. 192, doi. 10.3390/v15010192

By:

Minotti, Chiara;
Mengato, Daniele;
De Pieri, Marica;
Trivellato, Sabrina;
Francavilla, Andrea;
Di Chiara, Costanza;
Liberati, Cecilia;
Mattera, Raffaele;
Biffi, Alessandra;
Giaquinto, Carlo;
Venturini, Francesca;
Donà, Daniele

Publication type:

Article

Coordinate dual-gene transgenesis by lentiviral vectors carrying synthetic bidirectional promoters.

Published in:

Nature Biotechnology, 2005, v. 23, n. 1, p. 108, doi. 10.1038/nbt1049

By:

Amendola, Mario;
Venneri, Mary Anna;
Biffi, Alessandra;
Vigna, Elisa;
Naldini, Luigi

Publication type:

Article

Psychological Wellbeing in Adolescents with Leukaemia: A Comparative Study with Typical Development Peers.

Published in:

International Journal of Environmental Research & Public Health, 2020, v. 17, n. 2, p. 567, doi. 10.3390/ijerph17020567

By:

Tremolada, Marta;
Taverna, Livia;
Chiavetta, Ilaria Tamara;
Bonichini, Sabrina;
Putti, Maria Caterina;
Biffi, Alessandra

Publication type:

Article

Residual Cerebrovascular Morbidity Despite Treatment in Pediatric Sickle Cell Disease Highlights Opportunities for Earlier, Intensified Monitoring and Treatment.

Published in:

American Journal of Hematology, 2025, v. 100, n. 4, p. 717, doi. 10.1002/ajh.27596

By:

Reggiani, Giulia;
Coppadoro, Beatrice;
Boaro, Maria Paola;
Trapanese, Roberta;
Baido, Ilaria;
Biffi, Alessandra;
Viaro, Federica;
Pieroni, Alessio;
Minerva, Matteo;
Barcelos, Giovanna;
Manara, Renzo;
Baracchini, Claudia;
Colombatti, Raffaella

Publication type:

Article

A novel germline variant in PIK3R1 results in SHORT syndrome associated with TAL/LMO T‐cell acute lymphoblastic leukemia.

Published in:

American Journal of Hematology, 2020, v. 95, n. 12, p. E335, doi. 10.1002/ajh.25998

By:

Marzollo, Antonio;
Maestrini, Giacomo;
La Starza, Roberta;
Elia, Loredana;
Malfona, Francesco;
Pierini, Tiziana;
Tretti Parenzan, Caterina;
Coppe, Alessandro;
Bortoluzzi, Stefania;
Biffi, Alessandra;
Mecucci, Cristina;
Bresolin, Silvia;
Testi, Anna Maria

Publication type:

Article

Metachromatic Leukodystrophy: Too Frequent (Mis)Diagnosis?

Published in:

2018

By:

Politi, Letterio S.;
Salsano, Ettore;
Biffi, Alessandra

Publication type:

Letter

Integrated CGH/WES Analyses Advance Understanding of Aggressive Neuroblastoma Evolution: A Case Study.

Published in:

2021

By:

Corallo, Diana;
Zanon, Carlo;
Pantile, Marcella;
Tonini, Gian Paolo;
Zin, Angelica;
Francescato, Samuela;
Rossi, Bartolomeo;
Trevisson, Eva;
Pinato, Claudia;
Monferrer, Ezequiel;
Noguera, Rosa;
Aliño, Salvador F.;
Herrero, Maria Jose;
Biffi, Alessandra;
Viscardi, Elisabetta;
Aveic, Sanja

Publication type:

Case Study

MiR-26a-5p as a Reference to Normalize MicroRNA qRT-PCR Levels in Plasma Exosomes of Pediatric Hematological Malignancies.

Published in:

Cells (2073-4409), 2021, v. 10, n. 1, p. 101, doi. 10.3390/cells10010101

By:

Damanti, Carlotta C.;
Gaffo, Enrico;
Lovisa, Federica;
Garbin, Anna;
Di Battista, Piero;
Gallingani, Ilaria;
Tosato, Anna;
Pillon, Marta;
Carraro, Elisa;
Mascarin, Maurizio;
Elia, Caterina;
Biffi, Alessandra;
Bortoluzzi, Stefania;
Mussolin, Lara

Publication type:

Article

Adolescents and young adults with oncohematological disease: use of social networks, impact of SARS-COV-2, and psychosocial well-being.

Published in:

Frontiers in Psychiatry, 2023, p. 1, doi. 10.3389/fpsyt.2023.1239131

By:

Tremolada, Marta;
Taverna, Livia;
Vietina, Francesco;
Incardona, Roberta Maria;
Pierobon, Marta;
Bonichini, Sabrina;
Biffi, Alessandra;
Bisogno, Gianni

Publication type:

Article

Low miR-214-5p Expression Correlates With Aggressive Subtypes of Pediatric ALCL With Non-Common Histology.

Published in:

Frontiers in Oncology, 2021, v. 11, p. 1, doi. 10.3389/fonc.2021.663221

By:

Di Battista, Piero;
Lovisa, Federica;
Gaffo, Enrico;
Gallingani, Ilaria;
Damanti, Carlotta C.;
Garbin, Anna;
Ferrone, Lavinia;
Carraro, Elisa;
Pillon, Marta;
Lo Nigro, Luca;
Mura, Rossella;
Pizzi, Marco;
Guzzardo, Vincenza;
Dei Tos, Angelo Paolo;
Biffi, Alessandra;
Bortoluzzi, Stefania;
Mussolin, Lara

Publication type:

Article

NFATc1 and NFATc2 transcription factors drive the resistance to glucocorticoids in Acute Lymphoblastic Leukemia pediatric patients.

Published in:

Italian Journal of Anatomy & Embryology / Archivio Italiano di Anatomia Ed Embriologia, 2023, p. 93

By:

Veltri, Giulia;
Peloso, Alberto;
Cani, Alice;
Borile, Giulia;
Russo, Loris;
Simon, Katharina;
Santinon, Giulia;
Frasson, Chiara;
Minuzzo, Sonia Anna;
Indraccolo, Stefano;
Biffi, Alessandra;
Buldini, Barbara;
Bresolin, Silvia;
Ntziachristos, Panagiotis;
Serafin, Valentina

Publication type:

Article

Mucopolisaccaridosi 1H (MPS-1H): studio del rimodellamento osseo.

Published in:

Italian Journal of Anatomy & Embryology / Archivio Italiano di Anatomia Ed Embriologia, 2022, v. 126, p. 247

By:

Brunetti, Giacomina;
Tummolo, Albina;
Piacente, Laura;
Marzollo, Antonio;
Biffi, Alessandra;
Burlina, Alberto;
Faienza, Maria Felicia

Publication type:

Article

The combined use of enzyme activity and metabolite assays as a strategy for newborn screening of mucopolysaccharidosis type I.

Published in:

Clinical Chemistry & Laboratory Medicine, 2020, v. 58, n. 12, p. 2063, doi. 10.1515/cclm-2020-0064

By:

Polo, Giulia;
Gueraldi, Daniela;
Giuliani, Antonella;
Rubert, Laura;
Cazzorla, Chiara;
Salviati, Leonardo;
Marzollo, Antonio;
Biffi, Alessandra;
Burlina, Alessandro P.;
Burlina, Alberto B.

Publication type:

Article

NUP214–ABL1 fusion in childhood T‐ALL.

Published in:

Pediatric Blood & Cancer, 2022, v. 69, n. 9, p. 1, doi. 10.1002/pbc.29643

By:

Veltri, Giulia;
Sandei, Max;
Silvestri, Daniela;
Bresolin, Silvia;
Pession, Andrea;
Santoro, Nicola;
Ziino, Ottavio;
Veltroni, Marinella;
Rizzari, Carmelo;
Biffi, Alessandra;
Valsecchi, Maria Grazia;
Conter, Valentino;
Buldini, Barbara;
Accordi, Benedetta;
Serafin, Valentina

Publication type:

Article

Hospital‐based home care for children with cancer during the COVID‐19 pandemic in northeastern Italy.

Published in:

Pediatric Blood & Cancer, 2020, v. 67, n. 12, p. 1, doi. 10.1002/pbc.28501

By:

Massano, Davide;
Cosma, Laura;
Garolla, Martina;
Sainati, Laura;
Biffi, Alessandra

Publication type:

Article

Histology of pediatric classic Hodgkin lymphoma: From diagnosis to prognostic stratification.

Published in:

2020

By:

Pizzi, Marco;
Tazzoli, Sara;
Carraro, Elisa;
Chaviano, Felicia;
Massano, Davide;
Lovisa, Federica;
Mussolin, Lara;
Todesco, Alessandra;
Biffi, Alessandra;
d'Amore, Emanuele S.;
Pillon, Marta;
Rugge, Massimo

Publication type:

journal article

Gene therapy of metachromatic leukodystrophy reverses neurological damage and deficits in mice.

Published in:

2006

By:

Biffi, Alessandra;
Capotondo, Alessia;
Fasano, Stefania;
del Carro, Ubaldo;
Marchesini, Sergio;
Azuma, Hisaya;
Malaguti, Maria Chiara;
Amadio, Stefano;
Brambilla, Riccardo;
Grompe, Markus;
Bordignon, Claudio;
Quattrini, Angelo;
Naldini, Luigi

Publication type:

journal article

P374: THROMBOTIC EVENTS IN CHILDREN WITH ACUTE LYMPHOBLASTIC LEUKEMIA: EXPERIENCE OF ITALIAN AIEOP CENTERS (2009-2017).

Published in:

2023

By:

Mattera, Raffaele;
Caterina Putti, Maria;
Biffi, Alessandra;
Parasole, Rosanna;
Conter, Valentino;
Rizzari, Carmelo;
Grazia Valsecchi, Maria;
Silvestri, Daniela;
Biondi, Andrea;
Locatelli, Franco;
Barisone, Elena;
Micalizzi, Concetta;
Mina, Tommaso;
Kiren, Valentina

Publication type:

Abstract

Systemic Fusariosis: A Rare Complication in Children with Acute Lymphoblastic Leukemia.

Published in:

Journal of Fungi, 2020, v. 6, n. 4, p. 1, doi. 10.3390/jof6040212

By:

Biddeci, Giada;
Donà, Daniele;
Geranio, Giulia;
Spadini, Silvia;
Petris, Maria Grazia;
Pillon, Marta;
Biffi, Alessandra;
Putti, Maria Caterina

Publication type:

Article

Evaluation of high‐power laser therapy as treatment of chemotherapy‐induced oral mucositis in paediatric patients with oncohematological diseases—Dr Morankar.

Published in:

International Journal of Paediatric Dentistry, 2025, v. 35, n. 1, p. 5, doi. 10.1111/ipd.13280

By:

Ludovichetti, Francesco Saverio;
Costa, Giorgia;
Signoriello, Anna Giulia;
Stellini, Edoardo;
Zerman, Nicoletta;
Biffi, Alessandra;
Mazzoleni, Sergio

Publication type:

Article

Evaluating high power laser therapy (HPLT) as treatment for chemotherapy‐induced oral mucositis in paediatric patients with oncohematological diseases‐ Dr Jin.

Published in:

International Journal of Paediatric Dentistry, 2025, v. 35, n. 1, p. 2, doi. 10.1111/ipd.13281

By:

Ludovichetti, Francesco Saverio;
Costa, Giorgia;
Signoriello, Anna Giulia;
Stellini, Edoardo;
Zerman, Nicoletta;
Biffi, Alessandra;
Mazzoleni, Sergio

Publication type:

Article

Evaluating high power laser therapy (HPLT) as treatment for chemotherapy‐induced oral mucositis in paediatric patients with oncohematological diseases.

Published in:

International Journal of Paediatric Dentistry, 2023, v. 33, n. 3, p. 269, doi. 10.1111/ipd.13050

By:

Ludovichetti, Francesco Saverio;
Costa, Giorgia;
Signoriello, Anna Giulia;
Stellini, Edoardo;
Zerman, Nicoletta;
Biffi, Alessandra;
Mazzoleni, Sergio

Publication type:

Article

Neonatal-Onset Familial Mediterranean Fever in an Infant with Human Parainfluenza Virus-4 Infection.

Published in:

Neonatology (16617800), 2021, v. 118, n. 3, p. 359, doi. 10.1159/000514694

By:

Michev, Alexandre;
Borghesi, Alessandro;
Tretti, Caterina;
Martella, Maddalena;
Di Comite, Amelia;
Biffi, Alessandra;
Marzollo, Antonio;
Bresolin, Silvia

Publication type:

Article

Pain coping strategies in paediatric patients newly diagnosed with leukaemia compared with healthy peers.

Published in:

European Journal of Cancer Care, 2022, v. 31, n. 3, p. 1, doi. 10.1111/ecc.13575

By:

Tremolada, Marta;
Tasso, Giulia;
Bonichini, Sabrina;
Taverna, Livia;
Tumino, Manuela;
Putti, Maria Caterina;
Biffi, Alessandra;
Pillon, Marta

Publication type:

Article

Absence of VOD in paediatric thalassaemic HSCT recipients using defibrotide prophylaxis and intravenous Busulphan.

Published in:

British Journal of Haematology, 2009, v. 147, n. 4, p. 554, doi. 10.1111/j.1365-2141.2009.07871.x

By:

Cappelli, Barbara;
Chiesa, Robert;
Evangelio, Costanza;
Biffi, Alessandra;
Roccia, Tito;
Frugnoli, Ilaria;
Biral, Erika;
No, Anna;
Fossati, Marco;
Finizio, Valentina;
Miniero, Roberto;
Napolitano, Sara;
Ferrua, Francesca;
Soliman, Clara;
Ciceri, Fabio;
Roncarolo, Maria G.;
Marktel, Sarah

Publication type:

Article

A Multi-Omics Approach Reveals Enrichment in Metabolites Involved in the Regulation of the Glutathione Pathway in LIN28B-Dependent Cancer Cells.

Published in:

International Journal of Molecular Sciences, 2024, v. 25, n. 3, p. 1602, doi. 10.3390/ijms25031602

By:

Stocchero, Matteo;
Corallo, Diana;
Bresolin, Silvia;
Pantile, Marcella;
Pirillo, Paola;
Bortolozzi, Roberta;
Menegazzo, Sara;
Boso, Daniele;
Viola, Giampietro;
Baraldi, Eugenio;
Biffi, Alessandra;
Giordano, Giuseppe;
Aveic, Sanja

Publication type:

Article

Exploring the Role of Fibroblasts in Promoting Neuroblastoma Cell Migration and Invasion.

Published in:

Journal of Nanotheranostics, 2024, v. 5, n. 4, p. 212, doi. 10.3390/jnt5040013

By:

Corallo, Diana;
Nardelli, Cristina;
Pantile, Marcella;
Menegazzo, Sara;
Biffi, Alessandra;
Aveic, Sanja

Publication type:

Article

CD72 is a pan‐tumor antigen associated to pediatric acute leukemia.

Published in:

Cytometry. Part A, 2023, v. 103, n. 12, p. 1004, doi. 10.1002/cyto.a.24790

By:

Buldini, Barbara;
Faggin, Giovanni;
Porcù, Elena;
Scarparo, Pamela;
Polato, Katia;
Tregnago, Claudia;
Varotto, Elena;
Rizzardi, Paolo;
Rizzari, Carmelo;
Locatelli, Franco;
Biffi, Alessandra;
Pigazzi, Martina

Publication type:

Article

Dlg1, Sec8, and Mtmr2 Regulate Membrane Homeostasis in Schwann Cell Myelination.

Published in:

Journal of Neuroscience, 2009, v. 29, n. 27, p. 8858, doi. 10.1523/JNEUROSCI.1423-09.2009

By:

Bolis, Annalisa;
Coviello, Silvia;
Visigalli, Ilaria;
Taveggia, Carla;
Bachi, Angela;
Chishti, Athar H.;
Hanada, Toshihiko;
Quattrini, Angelo;
Previtali, Stefano Carlo;
Biffi, Alessandra;
Bolino, Alessandra

Publication type:

Article

Healthcare migration in Italian paediatric haematology-oncology centres belonging to AIEOP.

Published in:

Italian Journal of Pediatrics, 2024, v. 50, n. 1, p. 1, doi. 10.1186/s13052-024-01620-1

By:

Rondelli, Roberto;
Belotti, Tamara;
Masetti, Riccardo;
Locatelli, Franco;
Massimino, Maura;
Biffi, Alessandra;
Dufour, Carlo;
Fagioli, Franca;
Menna, Giuseppe;
Biondi, Andrea;
Favre, Claudio;
Zecca, Marco;
Santoro, Nicola;
Russo, Giovanna;
Perrotta, Silverio;
Pession, Andrea;
Prete, Arcangelo

Publication type:

Article

Psychological Well-Being, Cognitive Functioning, and Quality of Life in 205 Adolescent and Young Adult Childhood Cancer Survivors Compared to Healthy Peers.

Published in:

Frontiers in Psychology, 2022, p. 1, doi. 10.3389/fpsyg.2022.860729

By:

Tremolada, Marta;
Taverna, Livia;
Bonichini, Sabrina;
Pillon, Marta;
Biffi, Alessandra

Publication type:

Article

Novel Compounds Synergize With Venetoclax to Target KMT2A-Rearranged Pediatric Acute Myeloid Leukemia.

Published in:

Frontiers in Pharmacology, 2022, v. 13, p. 1, doi. 10.3389/fphar.2021.820191

By:

Tregnago, Claudia;
Benetton, Maddalena;
Da Ros, Ambra;
Borella, Giulia;
Longo, Giorgia;
Polato, Katia;
Francescato, Samuela;
Biffi, Alessandra;
Pigazzi, Martina

Publication type:

Article

RNY4 in Circulating Exosomes of Patients With Pediatric Anaplastic Large Cell Lymphoma: An Active Player?

Published in:

Frontiers in Oncology, 2020, v. 10, p. 1, doi. 10.3389/fonc.2020.00238

By:

Lovisa, Federica;
Di Battista, Piero;
Gaffo, Enrico;
Damanti, Carlotta C.;
Garbin, Anna;
Gallingani, Ilaria;
Carraro, Elisa;
Pillon, Marta;
Biffi, Alessandra;
Bortoluzzi, Stefania;
Mussolin, Lara

Publication type:

Article

Oncological Children and Well-Being: Occupational Performance and HRQOL Change after Fine Motor Skills Stimulation Activities.

Published in:

Pediatric Reports, 2021, v. 13, n. 3, p. 383, doi. 10.3390/pediatric13030046

By:

Taverna, Livia;
Bellavere, Martina;
Tremolada, Marta;
Santinelli, Lietta;
Rudelli, Nicola;
Mainardi, Michele;
Onder, Graziano;
Putti, Maria Caterina;
Biffi, Alessandra;
Tosetto, Barbara

Publication type:

Article

An innovative hematopoietic stem cell gene therapy approach benefits CLN1 disease in the mouse model.

Published in:

EMBO Molecular Medicine, 2023, v. 15, n. 4, p. 1, doi. 10.15252/emmm.202215968

By:

Peviani, Marco;
Das, Sabyasachi;
Patel, Janki;
Jno‐Charles, Odella;
Kumar, Rajesh;
Zguro, Ana;
Mathews, Tyler D;
Cabras, Paolo;
Milazzo, Rita;
Cavalca, Eleonora;
Poletti, Valentina;
Biffi, Alessandra

Publication type:

Article

Application of the Weighted-Incidence Syndromic Combination Antibiogram (WISCA) to guide the empiric antibiotic treatment of febrile neutropenia in oncological paediatric patients: experience from two paediatric hospitals in Northern Italy.

Published in:

Annals of Clinical Microbiology & Antimicrobials, 2024, v. 23, n. 1, p. 1, doi. 10.1186/s12941-024-00673-8

By:

Liberati, Cecilia;
Donà, Daniele;
Maestri, Linda;
Petris, Maria Grazia;
Barbieri, Elisa;
Gallo, Elisa;
Gallocchio, Jacopo;
Pierobon, Marta;
Calore, Elisabetta;
Zin, Annachiara;
Brigadoi, Giulia;
Mariani, Marcello;
Mesini, Alessio;
Saffioti, Carolina;
Ugolotti, Elisabetta;
Gregori, Dario;
Giaquinto, Carlo;
Castagnola, Elio;
Biffi, Alessandra

Publication type:

Article

Characterization of new arylsulfatase A gene mutations reinforces genotype-phenotype correlation in metachromatic leukodystrophy.

Published in:

Human Mutation, 2009, v. 30, n. 10, p. E936, doi. 10.1002/humu.21093

By:

Cesani, Martina;
Capotondo, Alessia;
Plati, Tiziana;
Sergi, Lucia Sergi;
Fumagalli, Francesca;
Roncarolo, Maria Grazia;
Naldini, Luigi;
Comi, Giancarlo;
Sessa, Maria;
Biffi, Alessandra

Publication type:

Article

Development of Communication and Language Skills in Children with Hematological–Oncological Disorders: Challenges and Perspectives.

Published in:

Children, 2025, v. 12, n. 5, p. 574, doi. 10.3390/children12050574

By:

Melcarne, Giusy;
Marangon, Giulia;
Incardona, Roberta Maria;
Agostinelli, Anna;
Montino, Silvia;
Sorbara, Silvia;
Biffi, Alessandra;
Tremolada, Marta

Publication type:

Article

Preclinical Safety and Efficacy of Human CD34<sup>+</sup> Cells Transduced With Lentiviral Vector for the Treatment of Wiskott-Aldrich Syndrome.

Published in:

Molecular Therapy, 2013, v. 21, n. 1, p. 175, doi. 10.1038/mt.2012.23

By:

Scaramuzza, Samantha;
Biasco, Luca;
Ripamonti, Anna;
Castiello, Maria C;
Loperfido, Mariana;
Draghici, Elena;
Hernandez, Raisa J;
Benedicenti, Fabrizio;
Radrizzani, Marina;
Salomoni, Monica;
Ranzani, Marco;
Bartholomae, Cynthia C;
Vicenzi, Elisa;
Finocchi, Andrea;
Bredius, Robbert;
Bosticardo, Marita;
Schmidt, Manfred;
von Kalle, Christof;
Montini, Eugenio;
Biffi, Alessandra

Publication type:

Article

864. Characterization of Transgenic Mice Over-Expressing Arylsulfatase A: Implications for Gene Therapy and Sulfatases Activation Mechanisms.

Published in:

Molecular Therapy, 2006, v. 13, p. S332, doi. 10.1016/j.ymthe.2006.08.950

By:

Capotondo, Alessia;
Venneri, Mary A.;
Cosma, Maria P.;
Pallavicini, Isabella;
Ballabio, Andrea;
Naldini, Luigi;
Biffi, Alessandra

Publication type:

Article

888. Characterization of New Murine Models of Globoid Cell Leukodystrophy: Relevance for Gene Therapy Applications and Studies on Disease Pathogenesis.

Published in:

Molecular Therapy, 2006, v. 13, p. S342, doi. 10.1016/j.ymthe.2006.08.977

By:

Visigalli, Ilaria;
del Carro, Ubaldo;
Politi, Letterio;
Quattrini, Angelo;
Luzi, Paola;
Wenger, David;
Naldini, Luigi;
Biffi, Alessandra

Publication type:

Article

891. Correction of Established Neurologic Disease and Evidences of In Vivo Cross Correction in the Mouse Model of Metachromatic Leukodystrophy.

Published in:

Molecular Therapy, 2006, v. 13, p. S343, doi. 10.1016/j.ymthe.2006.08.980

By:

Biffi, Alessandra;
Capotondo, Alessia;
Fasano, Stefania;
del Carro, Ubaldo;
Marchesini, Sergio;
Azuma, Hisaya;
Brambilla, Riccardo;
Grompe, Markus;
Bordignon, Claudio;
Quattrini, Angelo;
Naldini, Luigi

Publication type:

Article

408. Safety of Lysosomal Enzymes Over-Expression in HSC for Gene Therapy of Storage Disorders.

Published in:

Molecular Therapy, 2006, v. 13, p. S157, doi. 10.1016/j.ymthe.2006.08.471

By:

Biffi, Alessandra;
Visigalli, Ilaria;
Cesani, Martina;
Capotondo, Alessia;
de Sio, Francesca R. Santoni;
Pallavicini, Isabella;
Zingale, Anna;
Naldini, Luigi

Publication type:

Article

442. LV Expressing MR Reporter Genes Allows In Vivo Monitoring of Stem Cell Gene Therapy.

Published in:

Molecular Therapy, 2006, v. 13, p. S170, doi. 10.1016/j.ymthe.2006.08.509

By:

Amendola, Mario;
S. Politi, Letterio;
Cadioli, Marcello;
Galli, Rossella;
Binda, Elena;
Falini, Andrea;
Levi, Sonia;
Scotti, Giuseppe;
Biffi, Alessandra;
Naldini, Luigi

Publication type:

Article

972. HSC-Based Ex Vivo Gene Therapy Prolongs Survival and Improves the Phenotype of Globoid Cell Leukodystrophy Mice

Published in:

2005

By:

Biffi, Alessandra;
Visigalli, Ilaria;
Politi, Letterio S.;
Quattrini, Angelo;
Del Carro, Ubaldo;
Wenger, David;
Bordignon, Claudio;
Naldini, Luigi

Publication type:

Abstract

426. Cure of Established Disease and Direct Evidence of Cellular Cross-Correction in the Nervous System of Metachromatic Leukodystrophy Mice after HSC-Based Gene Therapy

Published in:

2005

By:

Biffi, Alessandra;
Capotondo, Alessia;
Quattrini, Angelo;
Del Carro, Ubaldo;
Brambilla, Riccardo;
Fasano, Stefania;
Marchesini, Sergio;
Bordignon, Claudio;
Naldini, Luigi

Publication type:

Abstract

New Indications for Hematopoietic Stem Cell Gene Therapy in Lysosomal Storage Disorders.

Published in:

Frontiers in Oncology, 2022, v. 12, p. 1, doi. 10.3389/fonc.2022.885639

By:

Rossini, Linda;
Durante, Caterina;
Marzollo, Antonio;
Biffi, Alessandra

Publication type:

Article