Works matching AU Ali, Robin R

Results: 64
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    Retinal dystrophies and gene therapy.

    Published in:
    2012
    By:
    • Sundaram V;
    • Moore AT;
    • Ali RR;
    • Bainbridge JW;
    • Sundaram, Venki;
    • Moore, Anthony T;
    • Ali, Robin R;
    • Bainbridge, James W
    Publication type:
    journal article
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    Comprehensive genomic access to vector integration in clinical gene therapy.

    Published in:
    Nature Medicine, 2009, v. 15, n. 12, p. 1431, doi. 10.1038/nm.2057
    By:
    • Gabriel, Richard;
    • Eckenberg, Ralph;
    • Paruzynski, Anna;
    • Bartholomae, Cynthia C.;
    • Nowrouzi, Ali;
    • Arens, Anne;
    • Howe, Steven J.;
    • Recchia, Alessandra;
    • Cattoglio, Claudia;
    • Wei Wang;
    • Faber, Katrin;
    • Schwarzwaelder, Kerstin;
    • Kirsten, Romy;
    • Deichmann, Annette;
    • Ball, Claudia R.;
    • Balaggan, Kamaljit S.;
    • Yáñez-Muñoz, Rafael J.;
    • Ali, Robin R.;
    • Gaspar, H. Bobby;
    • Biasco, Luca
    Publication type:
    Article
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    Effective gene therapy with nonintegrating lentiviral vectors.

    Published in:
    Nature Medicine, 2006, v. 12, n. 3, p. 348, doi. 10.1038/nm1365
    By:
    • Yáñez-Muñoz, Rafael J.;
    • Balaggan, Kamaljit S.;
    • MacNeil, Angus;
    • Howe, Steven J.;
    • Schmidt, Manfred;
    • Smith, Alexander J.;
    • Buch, Prateek;
    • MacLaren, Robert E.;
    • Anderson, Patrick N.;
    • Barker, Susie E.;
    • Duran, Yanai;
    • Bartholomae, Cynthia;
    • von Kalle, Christof;
    • Heckenlively, John R.;
    • Kinnon, Christine;
    • Ali, Robin R.;
    • Thrasher, Adrian J.
    Publication type:
    Article
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    Leber Congenital Amaurosis Associated with AIPL1: Challenges in Ascribing Disease Causation, Clinical Findings, and Implications for Gene Therapy.

    Published in:
    PLoS ONE, 2012, v. 7, n. 3, p. 1, doi. 10.1371/journal.pone.0032330
    By:
    • Mei Hong Tan;
    • Mackay, Donna S.;
    • Jill Cowing;
    • Tran, Hoai Viet;
    • Smith, Alexander J.;
    • Wright, Genevieve A.;
    • Dev-Borman, Arundhati;
    • Henderson, Robert H.;
    • Moradi, Phillip;
    • Russell-Eggitt, Isabelle;
    • MacLaren, Robert E.;
    • Robson, Anthony G.;
    • Cheetham, Michael E.;
    • Thompson, Dorothy A.;
    • Webster, Andrew R.;
    • Michaelides, Michel;
    • Ali, Robin R.;
    • Moore, Anthony T.
    Publication type:
    Article
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    AAV-mediated ERdj5 overexpression protects against P23H rhodopsin toxicity.

    Published in:
    Human Molecular Genetics, 2020, v. 29, n. 8, p. 1310, doi. 10.1093/hmg/ddaa049
    By:
    • Aguilà, Monica;
    • Bellingham, James;
    • Athanasiou, Dimitra;
    • Bevilacqua, Dalila;
    • Duran, Yanai;
    • Maswood, Ryea;
    • Parfitt, David A;
    • Iwawaki, Takao;
    • Spyrou, Giannis;
    • Smith, Alexander J;
    • Ali, Robin R;
    • Cheetham, Michael E
    Publication type:
    Article
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    Rescue of mutant rhodopsin traffic by metformin-induced AMPK activation accelerates photoreceptor degeneration.

    Published in:
    Human Molecular Genetics, 2017, v. 26, n. 2, p. 305, doi. 10.1093/hmg/ddw387
    By:
    • Athanasiou, Dimitra;
    • Aguila, Monica;
    • Opefi, Chikwado A.;
    • South, Kieron;
    • Bellingham, James;
    • Bevilacqua, Dalila;
    • Munro, Peter M.;
    • Kanuga, Naheed;
    • Mackenzie, Francesca E.;
    • Dubis, Adam M.;
    • Georgiadis, Anastasios;
    • Graca, Anna B.;
    • Pearson, Rachael A.;
    • Ali, Robin R.;
    • Sakami, Sanae;
    • Palczewski, Krzysztof;
    • Sherman, Michael Y.;
    • Reeves, Philip J.;
    • Cheetham, Michael E.
    Publication type:
    Article
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    Hsp90 inhibition protects against inherited retinal degeneration.

    Published in:
    Human Molecular Genetics, 2014, v. 23, n. 8, p. 2164
    By:
    • Aguilà, Mònica;
    • Bevilacqua, Dalila;
    • McCulley, Caroline;
    • Schwarz, Nele;
    • Athanasiou, Dimitra;
    • Kanuga, Naheed;
    • Novoselov, Sergey S.;
    • Lange, Clemens A.K.;
    • Ali, Robin R.;
    • Bainbridge, James W.;
    • Gias, Carlos;
    • Coffey, Peter J.;
    • Garriga, Pere;
    • Cheetham, Michael E.
    Publication type:
    Article
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    Gene transfer in ophthalmology.

    Published in:
    Der Ophthalmologe, 1999, v. 96, n. 9, p. 570, doi. 10.1007/s003470050454
    By:
    • Reichel, Martin B.;
    • Hudde, Tobias;
    • Ali, Robin R.;
    • Wiedemann, Peter
    Publication type:
    Article
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    Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors.

    Published in:
    Human Molecular Genetics, 2009, v. 18, n. 12, p. 2099, doi. 10.1093/hmg/ddp133
    By:
    • Tan, Mei Hong;
    • Smith, Alexander J.;
    • Pawlyk, Basil;
    • Xu, Xiaoyun;
    • Liu, Xiaoqing;
    • Bainbridge, James B.;
    • Basche, Mark;
    • McIntosh, Jenny;
    • Tran, Hoai Viet;
    • Nathwani, Amit;
    • Li, Tiansen;
    • Ali, Robin R.
    Publication type:
    Article
    31

    Letter to the Editor.

    Published in:
    2006
    By:
    • Ali, Robin R.;
    • Winkfield, Karen M.;
    • Galanos, Anthony N.;
    • Miller, Karl E.;
    • Adams, Stephen M.;
    • Miller, Martha M.
    Publication type:
    Letter
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    Lentiviral Vector Integration Profiles Differ in Rodent Postmitotic Tissues.

    Published in:
    Molecular Therapy, 2011, v. 19, n. 4, p. 703, doi. 10.1038/mt.2011.19
    By:
    • Bartholomae, Cynthia C.;
    • Arens, Anne;
    • Balaggan, Kamaljit S.;
    • Yáñez-Muñoz, Rafael J.;
    • Montini, Eugenio;
    • Howe, Steven J.;
    • Paruzynski, Anna;
    • Korn, Bernhard;
    • Appelt, Jens Uwe;
    • MacNeil, Angus;
    • Cesana, Daniela;
    • Abel, Ulrich;
    • Glimm, Hanno;
    • Naldini, Luigi;
    • Ali, Robin R.;
    • Thrasher, Adrian J.;
    • von Kalle, Christof;
    • Schmidt, Manfred
    Publication type:
    Article
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    Corrigendum to “Local Administration of an Adeno-Associated Viral Vector Expressing IL-10 Reduces Monocyte Infiltration and Subsequent Photoreceptor Damage During Experimental Autoimmune Uveitis”.

    Published in:
    Molecular Therapy, 2006, v. 13, n. 4, p. 829, doi. 10.1016/j.ymthe.2005.09.013
    By:
    • Broderick, Cathryn A.;
    • Smith, Alexander J.;
    • Balaggan, Kam S.;
    • Georgiadis, Anastasios;
    • Buch, Prateek K.;
    • Trittibach, Peter C.;
    • Barker, Susie E.;
    • Sarra, Gian-Marco;
    • Thrasher, Adrian J.;
    • Dick, Andrew D.;
    • Ali, Robin R.
    Publication type:
    Article
    38

    Inhibition of Ocular Neovascularization by Hedgehog Blockade.

    Published in:
    Molecular Therapy, 2006, v. 13, n. 3, p. 573, doi. 10.1016/j.ymthe.2005.10.010
    By:
    • Surace, Enrico M.;
    • Balaggan, Kamaljit S.;
    • Tessitore, Alessandra;
    • Mussolino, Claudio;
    • Cotugno, Gabriella;
    • Bonetti, Ciro;
    • Vitale, Aniello;
    • Ali, Robin R.;
    • Auricchio, Alberto
    Publication type:
    Article
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    LRG1 Alters Pericyte Phenotype and Compromises Vascular Maturation.

    Published in:
    Cells (2073-4409), 2025, v. 14, n. 8, p. 593, doi. 10.3390/cells14080593
    By:
    • Hoeh, Alexandra E.;
    • Chang, Jui-Hsien;
    • Mueller, Ronja S.;
    • Basche, Mark;
    • Fantin, Alessandro;
    • Sepetis, Anastasios;
    • De Rossi, Giulia;
    • Dritsoula, Athina;
    • Ali, Robin R.;
    • Turowski, Patric;
    • Moss, Stephen E.;
    • Greenwood, John
    Publication type:
    Article