Works matching AU Gao, Guangping

Results: 130

Overcoming innate immune barriers that impede AAV gene therapy vectors.

Published in:

2021

By:

Muhuri, Manish;
Yukiko Maeda;
Hong Ma;
Ram, Sanjay;
Fitzgerald, Katherine A.;
Tai, Phillip W. L.;
Guangping Gao;
Maeda, Yukiko;
Ma, Hong;
Tai, Phillip Wl;
Gao, Guangping

Publication type:

journal article

GFP-on mouse model for interrogation of in vivo gene editing.

Published in:

Nature Communications, 2025, v. 16, n. 1, p. 1, doi. 10.1038/s41467-025-61449-y

By:

Dib, Carla;
Queenan, Jack A.;
Swartzrock, Leah;
Willner, Hana;
Denis, Morgane;
Ahmed, Nouraiz;
Moulana Zada, Fareha;
Borges, Beltran;
Charlesworth, Carsten T.;
Lum, Tony;
Yates, Bradley P.;
Kwon, Caleb Y.;
Scorzo, Augustino V.;
Davis, Scott C.;
Davis, Jessie R.;
He, Ran;
Xie, Jun;
Gao, Guangping;
MacKenzie, Tippi C.;
Liu, David R.

Publication type:

Article

Directed evolution of adeno-associated virus for glioma cell transduction.

Published in:

Journal of Neuro-Oncology, 2010, v. 96, n. 3, p. 337, doi. 10.1007/s11060-009-9972-7

By:

Maguire, Casey A.;
Gianni, Davide;
Meijer, Dimphna H.;
Shaket, Lev A.;
Wakimoto, Hiroaki;
Rabkin, Samuel D.;
Guangping Gao;
Sena-Esteves, Miguel

Publication type:

Article

The Sodium Channel β4 Auxiliary Subunit Selectively Controls Long-Term Depression in Core Nucleus Accumbens Medium Spiny Neurons.

Published in:

Frontiers in Cellular Neuroscience, 2017, v. 11, p. 1, doi. 10.3389/fncel.2017.00017

By:

Xincai Ji;
Saha, Sucharita;
Guangping Gao;
Lasek, Amy W.;
Homanics, Gregg E.;
Guildford, Melissa;
Tapper, Andrew R.;
Martin, Gilles E.

Publication type:

Article

Recombinant Adeno-Associated Virus Serotype 6 (rAAV6) Potently and Preferentially Transduces Rat Astrocytes In vitro and In vivo.

Published in:

Frontiers in Cellular Neuroscience, 2016, v. 10, p. 1, doi. 10.3389/fncel.2016.00262

By:

Schober, Alexandra L.;
Gagarkin, Dmitriy A.;
Ying Chen;
Guangping Gao;
Jacobson, Lauren;
Mongin, Alexander A.

Publication type:

Article

Characterization of adenoviral transduction profile in prostate cancer cells and normal prostate tissue.

Published in:

Prostate, 2017, v. 77, n. 12, p. 1265, doi. 10.1002/pros.23386

By:

Ai, Jianzhong;
Tai, Phillip W.L.;
Lu, Yi;
Li, Jia;
Ma, Hong;
Su, Qin;
Wei, Qiang;
Li, Hong;
Gao, Guangping

Publication type:

Article

Isolation and Identification of Pathogenic Bacteria Causing Bovine Subclinical Mastitis in Eastern Hebei Province.

Published in:

Animal Husbandry & Feed Science, 2018, v. 10, n. 1, p. 65, doi. 10.19578/j.cnki.ahfs.2018.01.014

By:

Gao Guisheng;
Wu Tonglei;
Zhang Zhiqiang;
Yang Zongze;
Fu Zhixin;
Zou Fengping;
Gao Guangping;
An Jiwei;
Yao Weiping;
Shi Qiumei

Publication type:

Article

Adeno-associated virus serotype rh.10 displays strong muscle tropism following intraperitoneal delivery.

Published in:

Scientific Reports, 2017, p. 40336, doi. 10.1038/srep40336

By:

Ai, Jianzhong;
Li, Jia;
Gessler, Dominic J.;
Su, Qin;
Wei, Qiang;
Li, Hong;
Gao, Guangping

Publication type:

Article

RNA activation of haploinsufficient Foxg1 gene in murine neocortex.

Published in:

Scientific Reports, 2016, p. 39311, doi. 10.1038/srep39311

By:

Fimiani, Cristina;
Goina, Elisa;
Su, Qin;
Gao, Guangping;
Mallamaci, Antonello

Publication type:

Article

Editorial: "AAV Gene Therapy: Immunology and Immunotherapeutics".

Published in:

2021

By:

Martinez-Navio, José M.;
Paulk, Nicole K.;
Gao, Guangping

Publication type:

Editorial

Vectored Immunotherapeutics for Infectious Diseases: Can rAAVs Be The Game Changers for Fighting Transmissible Pathogens?

Published in:

Frontiers in Immunology, 2021, v. 11, p. N.PAG, doi. 10.3389/fimmu.2021.673699

By:

Zhan, Wei;
Muhuri, Manish;
Tai, Phillip W. L.;
Gao, Guangping

Publication type:

Article

Novel Combinatorial MicroRNA-Binding Sites in AAV Vectors Synergistically Diminish Antigen Presentation and Transgene Immunity for Efficient and Stable Transduction.

Published in:

Frontiers in Immunology, 2021, v. 11, p. N.PAG, doi. 10.3389/fimmu.2021.674242

By:

Muhuri, Manish;
Zhan, Wei;
Maeda, Yukiko;
Li, Jia;
Lotun, Anoushka;
Chen, Jennifer;
Sylvia, Katelyn;
Dasgupta, Ishani;
Arjomandnejad, Motahareh;
Nixon, Thomas;
Keeler, Allison M.;
Manokaran, Sangeetha;
He, Ran;
Su, Qin;
Tai, Phillip W. L.;
Gao, Guangping

Publication type:

Article

Domain-inlaid Nme2Cas9 adenine base editors with improved activity and targeting scope.

Published in:

Nature Communications, 2024, v. 15, n. 1, p. 1, doi. 10.1038/s41467-024-45763-5

By:

Bamidele, Nathan;
Zhang, Han;
Dong, Xiaolong;
Cheng, Haoyang;
Gaston, Nicholas;
Feinzig, Hailey;
Cao, Hanbing;
Kelly, Karen;
Watts, Jonathan K.;
Xie, Jun;
Gao, Guangping;
Sontheimer, Erik J.

Publication type:

Article

Durable contraception in the female domestic cat using viral-vectored delivery of a feline anti-Müllerian hormone transgene.

Published in:

Nature Communications, 2023, v. 14, n. 1, p. 1, doi. 10.1038/s41467-023-38721-0

By:

Vansandt, Lindsey M.;
Meinsohn, Marie-Charlotte;
Godin, Philippe;
Nagykery, Nicholas;
Sicher, Natalie;
Kano, Motohiro;
Kashiwagi, Aki;
Chauvin, Maeva;
Saatcioglu, Hatice D.;
Barnes, Julie L.;
Miller, Amy G.;
Thompson, Amy K.;
Bateman, Helen L.;
Donelan, Elizabeth M.;
González, Raquel;
Newsom, Jackie;
Gao, Guangping;
Donahoe, Patricia K.;
Wang, Dan;
Swanson, William F.

Publication type:

Article

Combinatorial design of nanoparticles for pulmonary mRNA delivery and genome editing.

Published in:

Nature Biotechnology, 2023, v. 41, n. 10, p. 1410, doi. 10.1038/s41587-023-01679-x

By:

Li, Bowen;
Manan, Rajith Singh;
Liang, Shun-Qing;
Gordon, Akiva;
Jiang, Allen;
Varley, Andrew;
Gao, Guangping;
Langer, Robert;
Xue, Wen;
Anderson, Daniel

Publication type:

Article

Drag-and-drop genome insertion of large sequences without double-strand DNA cleavage using CRISPR-directed integrases.

Published in:

Nature Biotechnology, 2023, v. 41, n. 4, p. 500, doi. 10.1038/s41587-022-01527-4

By:

Yarnall, Matthew T. N.;
Ioannidi, Eleonora I.;
Schmitt-Ulms, Cian;
Krajeski, Rohan N.;
Lim, Justin;
Villiger, Lukas;
Zhou, Wenyuan;
Jiang, Kaiyi;
Garushyants, Sofya K.;
Roberts, Nathaniel;
Zhang, Liyang;
Vakulskas, Christopher A.;
Walker II, John A.;
Kadina, Anastasia P.;
Zepeda, Adrianna E.;
Holden, Kevin;
Ma, Hong;
Xie, Jun;
Gao, Guangping;
Foquet, Lander

Publication type:

Article

Cas9-mediated allelic exchange repairs compound heterozygous recessive mutations in mice.

Published in:

Nature Biotechnology, 2018, v. 36, n. 10, p. 839, doi. 10.1038/nbt.4219

By:

Wang, Dan;
Li, Jia;
Song, Chun-Qing;
Tran, Karen;
Mou, Haiwei;
Wu, Pei-Hsuan;
Tai, Phillip W L;
Mendonca, Craig A;
Ren, Lingzhi;
Wang, Blake Y;
Su, Qin;
Gessler, Dominic J;
Zamore, Phillip D;
Xue, Wen;
Gao, Guangping

Publication type:

Article

Cas9-mediated allelic exchange repairs compound heterozygous recessive mutations in mice.

Published in:

Nature Biotechnology, 2018, v. 36, n. 9, p. 839, doi. 10.1038/nbt.4219

By:

Wang, Dan;
Li, Jia;
Song, Chun-Qing;
Tran, Karen;
Mou, Haiwei;
Wu, Pei-Hsuan;
Tai, Phillip W L;
Mendonca, Craig A;
Ren, Lingzhi;
Wang, Blake Y;
Su, Qin;
Gessler, Dominic J;
Zamore, Phillip D;
Xue, Wen;
Gao, Guangping

Publication type:

Article

Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo.

Published in:

Nature Biotechnology, 2016, v. 34, n. 3, p. 328, doi. 10.1038/nbt.3471

By:

Yin, Hao;
Song, Chun-Qing;
Dorkin, Joseph R;
Zhu, Lihua J;
Li, Yingxiang;
Wu, Qiongqiong;
Park, Angela;
Yang, Junghoon;
Suresh, Sneha;
Bizhanova, Aizhan;
Gupta, Ankit;
Bolukbasi, Mehmet F;
Walsh, Stephen;
Bogorad, Roman L;
Gao, Guangping;
Weng, Zhiping;
Dong, Yizhou;
Koteliansky, Victor;
Wolfe, Scot A;
Langer, Robert

Publication type:

Article

Functional Upregulation of α4* Nicotinic Acetylcholine Receptors in VTA GABAergic Neurons Increases Sensitivity to Nicotine Reward.

Published in:

Journal of Neuroscience, 2015, v. 35, n. 22, p. 8570, doi. 10.1523/JNEUROSCI.4453-14.2015

By:

Ngolab, Jennifer;
Liwang Liu;
Zhao-Shea, Rubing;
Guangping Gao;
Gardner, Paul D.;
Tapper, Andrew R.

Publication type:

Article

Graphene quantum dots rescue angiogenic retinopathy via blocking STAT3/Periostin/ERK signaling.

Published in:

Journal of Nanobiotechnology, 2022, v. 20, n. 1, p. 1, doi. 10.1186/s12951-022-01362-4

By:

Zhao, Na;
Gui, Xiao;
Fang, Qian;
Zhang, Rui;
Zhu, Weiye;
Zhang, Haorui;
Li, Qing;
Zhou, Yukun;
Zhao, Jiawei;
Cui, Xiao;
Gao, Guangping;
Tang, Huipeng;
Shen, Ni;
Chen, Taoyong;
Song, Hongyuan;
Shen, Wei

Publication type:

Article

Effect of Echinacea Polysaccharide on Secretion of IL-lα mRNA by IEC-6 Injured by LPS.

Published in:

Agricultural Biotechnology (2164-4993), 2016, v. 5, n. 6, p. 35

By:

Yanying ZHANG;
Qhimei SHI;
Qinghui JIA;
Guisheng GAO;
Guangping GAO;
Xinhua SHAO

Publication type:

Article

Antibiotic Sensitivity Test and Detection of Sulfonamide Resistance Gene Sul2 in Escherichia coli Isolates from Swine.

Published in:

Agricultural Biotechnology (2164-4993), 2016, v. 5, n. 2, p. 40

By:

Yanying ZHANG;
Fang XIANG;
Rui GUO;
Zhaoxing ZHANG;
Qiumei SHI;
Yuqin LIU;
Cairan YANG;
Zongze YANG;
Guangping GAO;
Guisheng GAO;
Zhi PENG;
Xun SUO

Publication type:

Article

Histopathological Observation of Cynoglossus semilaevis Gunther with Abdominal Dropsy in Industrial Aquaculture.

Published in:

Agricultural Biotechnology (2164-4993), 2016, v. 5, n. 1, p. 37

By:

Guangping GAO;
Guisheng GAO;
Yanying ZHANG;
Zhixin JI;
Qinghui JIA;
Ting SU;
Qiumei SHI;
Hongsheng HAN;
Qingchun Song;
Jianxin ZHU

Publication type:

Article

Antibacterial Effects of Chinese Herbal Medicines against Streptococcus iniae in Oreochrornis niloticus.

Published in:

Agricultural Biotechnology (2164-4993), 2016, v. 5, n. 1, p. 33

By:

Guisheng GAO;
Yanying ZHANG;
Yongmei SU;
Qiumei SHI;
Guangping GAO;
Yating BAI;
Hongsheng HAN;
Jianxin ZHU;
Qingchun SONG;
Guanglian REN

Publication type:

Article

PCR Detection of Streptococcus agalactiae in Dairy Cows Suffering from Mastitis.

Published in:

Agricultural Biotechnology (2164-4993), 2013, v. 2, n. 5, p. 22

By:

Yanying ZHANG;
Guisheng GAO;
Zhengben LI;
Guangping GAO;
Qiumei SHI;
Xinhua SHAO;
Yinju LIANG;
Huiran LIU

Publication type:

Article

Histopathological Observation of Classical Swine Fever in Newborn Piglets.

Published in:

Agricultural Biotechnology (2164-4993), 2013, v. 2, n. 5, p. 45

By:

Ping SHEN;
Guisheng GAO;
Yanying ZHANG;
Qiumei SHI;
Guangping GAO;
Zhipeng LI

Publication type:

Article

Histopathological Observation of Goose Escherichia coli Disease.

Published in:

Agricultural Biotechnology (2164-4993), 2013, v. 2, n. 5, p. 28

By:

Ping SHEN;
Guangping GAO;
Guisheng GAO;
Yanying ZHANG;
Qiumei SHI;
Xinhua SHAO;
Lining HE;
Wenwen SU

Publication type:

Article

Screening of Chinese Herbal Medicines against Avian Infectious Laryngotracheitis Virus and Escherichia coli.

Published in:

Agricultural Biotechnology (2164-4993), 2013, v. 2, n. 5, p. 25

By:

Yanying ZHANG;
Qiumei SHI;
Guisheng GAO;
Guangping GAO;
Ping SHEN

Publication type:

Article

Effects of Two Drugs on Small Intestinal Epithelial Lymphocytes of Experimental Piglets with Spleen Deficiency.

Published in:

Agricultural Biotechnology (2164-4993), 2013, v. 2, n. 4, p. 34

By:

SHEN, Ping;
ZHANG, Yanying;
GAO, Guisheng;
SHI, Qiumei;
GAO, Guangping;
SHAO, Xinhua

Publication type:

Article

Correction: Single-dose immunogenicity and protective efficacy of simian adenoviral vectors against Plasmodium berghei.

Published in:

European Journal of Immunology, 2011, v. 41, n. 5, p. 1501, doi. 10.1002/eji.201190031

By:

Reyes-Sandoval, Arturo;
Sridhar, Saranya;
Berthoud, Tamara;
Moore, Anne C.;
Harty, John T.;
Gilbert, Sarah C.;
Gao, Guangping;
Ertl, Hildegund C. J.;
Wilson, James C.;
Hill, Adrian V. S.

Publication type:

Article

Single-dose immunogenicity and protective efficacy of simian adenoviral vectors against Plasmodium berghei.

Published in:

European Journal of Immunology, 2008, v. 38, n. 3, p. 732, doi. 10.1002/eji.200737672

By:

Reyes-Sandoval, Arturo;
Sridhar, Saranya;
Berthoud, Tamara;
Moore, Anne C.;
Harty, John T.;
Gilbert, Sarah C.;
Gao, Guangping;
Ertl, Hildegund C. J.;
Wilson, James C.;
Hill, Adrian V. S.

Publication type:

Article

Streamlined ex vivo and in vivo genome editing in mouse embryos using recombinant adenoassociated viruses.

Published in:

Nature Communications, 2018, v. 9, n. 1, p. 1, doi. 10.1038/s41467-017-02706-7

By:

Yeonsoo Yoon;
Dan Wang;
Tai, Phillip W. L.;
Riley, Joy;
Guangping Gao;
Rivera-Pérez, Jaime A.

Publication type:

Article

Regulation of RIPK1 activation by TAK1-mediated phosphorylation dictates apoptosis and necroptosis.

Published in:

Nature Communications, 2017, v. 8, n. 1, p. 1, doi. 10.1038/s41467-017-00406-w

By:

Jiefei Geng;
Yasushi Ito;
Linyu Shi;
Palak Amin;
Jiachen Chu;
Ouchida, Amanda Tomie;
Mookhtiar, Adnan Kasim;
Heng Zhao;
Daichao Xu;
Shan, Bing;
Najafov, Ayaz;
Guangping Gao;
Akira, Shizuo;
Junying Yuan

Publication type:

Article

Global CNS Transduction of Adult Mice by Intravenously Delivered rAAVrh.8 and rAAVrh.10 and Nonhuman Primates by rAAVrh.10.

Published in:

Molecular Therapy, 2014, v. 22, n. 7, p. 1299, doi. 10.1038/mt.2014.68

By:

Yang, Bin;
Li, Shaoyong;
Wang, Hongyan;
Guo, Yansu;
Gessler, Dominic J;
Cao, Chunyan;
Su, Qin;
Kramer, Joshua;
Zhong, Li;
Ahmed, Seemin Seher;
Zhang, Hongwei;
He, Ran;
Desrosiers, Ronald C;
Brown, Robert;
Xu, Zuoshang;
Gao, Guangping

Publication type:

Article

A Single Intravenous rAAV Injection as Late as P20 Achieves Efficacious and Sustained CNS Gene Therapy in Canavan Mice.

Published in:

Molecular Therapy, 2013, v. 21, n. 12, p. 2136, doi. 10.1038/mt.2013.138

By:

Ahmed, Seemin Seher;
Li, Huapeng;
Cao, Chunyan;
Sikoglu, Elif M;
Denninger, Andrew R;
Su, Qin;
Eaton, Samuel;
Liso Navarro, Ana A;
Xie, Jun;
Szucs, Sylvia;
Zhang, Hongwei;
Moore, Constance;
Kirschner, Daniel A;
Seyfried, Thomas N;
Flotte, Terence R;
Matalon, Reuben;
Gao, Guangping

Publication type:

Article

Gene Therapy for Canavan's Disease Takes a Step Forward.

Published in:

Molecular Therapy, 2013, v. 21, n. 3, p. 505, doi. 10.1038/mt.2013.25

By:

Ahmed, Seemin S;
Gao, Guangping

Publication type:

Article

A deep learning model trained on expressed transcripts across different tissue types reveals cell-type codon-optimization preferences Open Access.

Published in:

Nucleic Acids Research, 2025, v. 53, n. 6, p. 1, doi. 10.1093/nar/gkaf233

By:

Ravi, Sandhiya;
Sharma, Tapan;
Yip, Mitchell;
Yang, Huiya;
Xie, Jun;
Gao, Guangping;
Tai, Phillip W L

Publication type:

Article

Self-delivering, chemically modified CRISPR RNAs for AAV co-delivery and genome editing in vivo.

Published in:

Nucleic Acids Research, 2024, v. 52, n. 2, p. 977, doi. 10.1093/nar/gkad1125

By:

Zhang, Han;
Kelly, Karen;
Lee, Jonathan;
Echeverria, Dimas;
Cooper, David;
Panwala, Rebecca;
Amrani, Nadia;
Chen, Zexiang;
Gaston, Nicholas;
Wagh, Atish;
Newby, Gregory A;
Xie, Jun;
Liu, David R;
Gao, Guangping;
Wolfe, Scot A;
Khvorova, Anastasia;
Watts, Jonathan K;
Sontheimer, Erik J

Publication type:

Article

Querying Recombination Junctions of Replication-Competent Adeno-Associated Viruses in Gene Therapy Vector Preparations with Single Molecule, Real-Time Sequencing.

Published in:

Viruses (1999-4915), 2023, v. 15, n. 6, p. 1228, doi. 10.3390/v15061228

By:

Yip, Mitchell;
Chen, Jing;
Zhi, Yan;
Tran, Ngoc Tam;
Namkung, Suk;
Pastor, Eric;
Gao, Guangping;
Tai, Phillip W. L.

Publication type:

Article

An optimized protocol for detection of E. coli β-galactosidase in lung tissue following gene transfer.

Published in:

Histochemistry & Cell Biology, 2005, v. 124, n. 1, p. 79, doi. 10.1007/s00418-005-0793-2

By:

Bell, Peter;
Limberis, Maria;
Guangping Gao;
Di Wu;
Bove, Mark S.;
Sanmiguel, Julio C.;
Wilson, James M.

Publication type:

Article

AAV-Mediated Targeting of the Activin A-ACVR1 R206H Signaling in Fibrodysplasia Ossificans Progressiva.

Published in:

Biomolecules (2218-273X), 2023, v. 13, n. 9, p. 1364, doi. 10.3390/biom13091364

By:

Yang, Yeon-Suk;
Lin, Chujiao;
Ma, Hong;
Xie, Jun;
Kaplan, Frederick S.;
Gao, Guangping;
Shim, Jae-Hyuck

Publication type:

Article

Systemic AAV9 gene transfer in adult GM1 gangliosidosis mice reduces lysosomal storage in CNS and extends lifespan.

Published in:

Human Molecular Genetics, 2015, v. 24, n. 15, p. 4353, doi. 10.1093/hmg/ddv168

By:

Weismann, Cara M.;
Ferreira, Jennifer;
Keeler, Allison M.;
Qin Su;
Linghua Qui;
Shaffer, Scott A.;
Zuoshang Xu;
Guangping Gao;
Sena-Esteves, Miguel

Publication type:

Article

Widespread spinal cord transduction by intrathecal injection of rAAV delivers efficacious RNAi therapy for amyotrophic lateral sclerosis.

Published in:

Human Molecular Genetics, 2014, v. 23, n. 3, p. 668, doi. 10.1093/hmg/ddt454

By:

Wang, Hongyan;
Yang, Bin;
Qiu, Linghua;
Yang, Chunxing;
Kramer, Joshua;
Su, Qin;
Guo, Yansu;
Brown, Robert H.;
Gao, Guangping;
Xu, Zuoshang

Publication type:

Article

Structural characterization of a novel human adeno-associated virus capsid with neurotropic properties.

Published in:

Nature Communications, 2020, v. 11, n. 1, p. 1, doi. 10.1038/s41467-020-17047-1

By:

Hsu, Hung-Lun;
Brown, Alexander;
Loveland, Anna B.;
Lotun, Anoushka;
Xu, Meiyu;
Luo, Li;
Xu, Guangchao;
Li, Jia;
Ren, Lingzhi;
Su, Qin;
Gessler, Dominic J.;
Wei, Yuquan;
Tai, Phillip W. L.;
Korostelev, Andrei A.;
Gao, Guangping

Publication type:

Article

Synergistic Deoxynucleoside and Gene Therapies for Thymidine Kinase 2 Deficiency.

Published in:

Annals of Neurology, 2021, v. 90, n. 4, p. 640, doi. 10.1002/ana.26185

By:

Lopez‐Gomez, Carlos;
Sanchez‐Quintero, Maria J.;
Lee, Eung Jeon;
Kleiner, Gulio;
Tadesse, Saba;
Xie, Jun;
Akman, Hasan Orhan;
Gao, Guangping;
Hirano, Michio

Publication type:

Article

Inhibition or Stimulation of Autophagy Affects Early Formation of Lipofuscin-Like Autofluorescence in the Retinal Pigment Epithelium Cell.

Published in:

International Journal of Molecular Sciences, 2017, v. 18, n. 4, p. 728, doi. 10.3390/ijms18040728

By:

Lei Lei;
Tzekov, Radouil;
Huapeng Li;
McDowell, J. Hugh;
Guangping Gao;
Smith, W. Clay;
Shibo Tang;
Kaushal, Shalesh

Publication type:

Article

Gene replacement therapies for inherited disorders of neurotransmission: Current progress in succinic semialdehyde dehydrogenase deficiency.

Published in:

Journal of Inherited Metabolic Disease, 2024, v. 47, n. 3, p. 476, doi. 10.1002/jimd.12735

By:

Lee, Henry H. C.;
Latzer, Itay Tokatly;
Bertoldi, Mariarita;
Gao, Guangping;
Pearl, Phillip L.;
Sahin, Mustafa;
Rotenberg, Alexander

Publication type:

Article

Adeno-associated virus as a delivery vector for gene therapy of human diseases.

Published in:

Signal Transduction & Targeted Therapy, 2024, v. 9, n. 1, p. 1, doi. 10.1038/s41392-024-01780-w

By:

Wang, Jiang-Hui;
Gessler, Dominic J.;
Zhan, Wei;
Gallagher, Thomas L.;
Gao, Guangping

Publication type:

Article

Rational design of aptazyme riboswitches for efficient control of gene expression in mammalian cells.

Published in:

eLife, 2016, p. 1, doi. 10.7554/eLife.18858

By:

Guocai Zhong;
Haimin Wang;
Bailey, Charles C.;
Guangping Gao;
Farzan, Michael

Publication type:

Article