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Title
Agalsidase-beta therapy for advanced Fabry disease: a randomized trial.
Authors
Banikazemi, Maryam; Bultas, Jan; Waldek, Stephen; Wilcox, William R; Whitley, Chester B; McDonald, Marie; Finkel, Richard; Packman, Seymour; Bichet, Daniel G; Warnock, David G; Desnick, Robert J; Fabry Disease Clinical Trial Study Group
Abstract
Fabry disease (alpha-galactosidase A deficiency) is a rare, X-linked lysosomal storage disorder that can cause early death from renal, cardiac, and cerebrovascular involvement.
Publication
Annals of internal medicine, 2007, Vol 146, Issue 2, p77