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- Title
Design, baseline characteristics, and early findings of the MPS VI (mucopolysaccharidosis VI) Clinical Surveillance Program (CSP).
- Authors
Hendriksz, Christian J; Giugliani, Roberto; Harmatz, Paul; Lampe, Christina; Martins, Ana Maria; Pastores, Gregory M; Steiner, Robert D; Leão Teles, Elisa; Valayannopoulos, Vassili; CSP Study Group
- Abstract
To outline the design, baseline data, and 5-year follow-up data of patients with mucopolysaccharidosis (MPS) VI enrolled in the Clinical Surveillance Program (CSP), a voluntary, multinational, observational program.
- Publication
Journal of inherited metabolic disease, 2013, Vol 36, Issue 2, p373
- ISSN
1573-2665
- Publication type
Journal Article
- DOI
10.1007/s10545-011-9410-9