Works matching Gene therapy

Results: 5000

Gene and Cell Therapy for Sarcomas: A Review.

Published in:

Cancers, 2025, v. 17, n. 7, p. 1125, doi. 10.3390/cancers17071125

By:

Chawla, Sant P.;
Pang, Skyler S.;
Jain, Darshit;
Jeffrey, Samantha;
Chawla, Neal S.;
Song, Paul Y.;
Hall, Frederick L.;
Gordon, Erlinda M.

Publication type:

Article

Analysis of Processing, Post-Maturation, and By-Products of shRNA in Gene and Cell Therapy Applications.

Published in:

Methods & Protocols, 2025, v. 8, n. 2, p. 38, doi. 10.3390/mps8020038

By:

Hong, Zhenyi;
Tesic, Nikola;
Bofill-De Ros, Xavier

Publication type:

Article

Predictive factors of final visual outcome in patients with leber hereditary optic neuropathy treated with lenadogene nolparvovec gene therapy.

Published in:

2025

By:

Barboni, Piero;
Newman, Nancy;
Biousse, Valérie;
Yu‐Wai‐Man, Patrick;
Carelli, Valerio;
Vignal‐Clermont, Catherine;
Josse, Constant;
Taiel, Magali;
Sahel, José‐Alain;
Sergott, Robert

Publication type:

Abstract

Predictive factors of final visual outcome in patients with leber hereditary optic neuropathy treated with lenadogene nolparvovec gene therapy.

Published in:

2025

By:

Barboni, Piero;
Newman, Nancy;
Biousse, Valérie;
Yu‐Wai‐Man, Patrick;
Carelli, Valerio;
Vignal‐Clermont, Catherine;
Josse, Constant;
Taiel, Magali;
Sahel, José‐Alain;
Sergott, Robert

Publication type:

Abstract

Efficacy and safety of lenadogene nolparvovec gene therapy for leber hereditary optic neuropathy in the real‐life setting.

Published in:

Acta Ophthalmologica (1755375X), 2025, v. 103, p. N.PAG, doi. 10.1111/aos.16931

By:

Yu‐Wai‐Man, Patrick;
Vignal‐Clermont, Catherine;
Carelli, Valerio;
La Morgia, Chiara;
Moster, Mark;
Sergott, Robert;
Donahue, Sean;
Dollfus, Hélène;
Klopstock, Thomas;
Priglinger, Claudia;
Hage, Rabih;
Smirnov, Vasily;
Cochard, Catherine;
Rougier, Marie‐Benedicte;
Tournaire‐Marques, Emilie;
Lebranchu, Pierre;
Froment, Caroline;
Pollet‐Villard, Frederic;
Laville, Marie‐Alice;
Prospero‐Ponce, Claudia

Publication type:

Article

Gene therapy – can we do better?

Published in:

Acta Ophthalmologica (1755375X), 2025, v. 103, p. N.PAG, doi. 10.1111/aos.16818

By:

Yu‐Wai‐Man, Patrick

Publication type:

Article

Long‐term results of unilateral or bilateral injection of lenadogene nolparvovec gene therapy for leber hereditary optic neuropathy.

Published in:

2025

By:

Biousse, Valérie;
Yu‐Wai‐Man, Patrick;
Newman, Nancy;
Subramanian, Prem;
Moster, Mark;
Wang, An‐Guor;
Donahue, Sean;
Leroy, Bart;
Carelli, Valerio;
Vignal‐Clermont, Catherine;
Sadun, Alfredo;
Sergott, Robert;
Fernández, Gema Rebolleda;
Chwalisz, Bart;
Banik, Rudrani;
Taiel, Magali;
Sahel, José‐Alain

Publication type:

Abstract

Long‐term results of unilateral or bilateral injection of lenadogene nolparvovec gene therapy for leber hereditary optic neuropathy.

Published in:

2025

By:

Biousse, Valérie;
Yu‐Wai‐Man, Patrick;
Newman, Nancy;
Subramanian, Prem;
Moster, Mark;
Wang, An‐Guor;
Donahue, Sean;
Leroy, Bart;
Carelli, Valerio;
Vignal‐Clermont, Catherine;
Sadun, Alfredo;
Sergott, Robert;
Fernández, Gema Rebolleda;
Chwalisz, Bart;
Banik, Rudrani;
Taiel, Magali;
Sahel, José‐Alain

Publication type:

Abstract

组织工程血管化基因治疗的研究进展.

Published in:

Chinese Journal of Tissue Engineering Research / Zhongguo Zuzhi Gongcheng Yanjiu, 2022, v. 26, n. 28, p. 4569, doi. 10.12307/2022.315

By:

李光照;
陈锐;
贾洪林;
任利玲

Publication type:

Article

基因治疗骨关节炎的概念、机制及问题.

Published in:

Chinese Journal of Tissue Engineering Research / Zhongguo Zuzhi Gongcheng Yanjiu, 2020, v. 24, n. 27, p. 4356, doi. 10.3969/j.issn.2095-4344.2717

By:

胡中岭;
李彬彬;
崔逸爽;
王茜;
张辉;
李琪佳;
王志强

Publication type:

Article

National guidelines for gene therapy product (2019): A road-map to gene therapy products development and clinical trials.

Published in:

Perspectives in Clinical Research, 2021, v. 12, n. 3, p. 118, doi. 10.4103/picr.PICR_189_20

By:

Sivagourounadin, Kiruthika;
Ravichandran, Mirunalini;
Rajendran, Priyadharsini

Publication type:

Article

FGF-4 Gene Therapy GENERX - Collateral Therapeutics: Ad5FGF4, Fibroblast Growth Factor-4 Gene Therapy GENERX - Collateral Therapeutics, GENERX.

Published in:: BioDrugs, 2002, v. 16, n. 1, p. 75, doi. 10.2165/00063030-200216010-00010
Publication type:: Article

多发性骨髓瘤的免疫基因治疗.

Published in:

Journal of Kunming Medical University / Kunming Yike Daxue Xuebao, 2016, v. 37, n. 6, p. 1

By:

秋玉珍;
张铀

Publication type:

Article

ТЕРАПЕВТИЧНА ЕФИКАСНОСТ И ЕФЕКТИВНОСТ НА РАЗХОДИТЕ НА ГЕННОЗАМЕСТИТЕЛНА ТЕРАПИЯ ЗА ЛЕЧЕНИЕ НА ПАЦИЕНТИ СЪС СПИНАЛНА МУСКУЛНА АТРОФИЯ ТИП 1

Published in:

Neurology & Psychiatry, 2020, v. 51, n. 2, p. 3

By:

Веков, Т.;
Велева, Н.;
Драганова, М.

Publication type:

Article

Oncolytic virus-based suicide gene therapy for cancer treatment: a perspective of the clinical trials conducted at Henry Ford Health.

Published in:

Translational Medicine Communications, 2023, v. 8, n. 1, p. 1, doi. 10.1186/s41231-023-00144-w

By:

Thoidingjam, Shivani;
Sriramulu, Sushmitha;
Freytag, Svend;
Brown, Stephen L.;
Kim, Jae Ho;
Chetty, Indrin J.;
Siddiqui, Farzan;
Movsas, Benjamin;
Nyati, Shyam

Publication type:

Article

HEMATOPOIETIC STEM CELL GENE THERAPY FOR INHERITED MONOGENIC DISEASES AND ITS IMPLICATIONS FOR FUTURE GENE THERAPY TRIALS IN TURKEY.

Published in:

Trakya University Journal of Natural Sciences, 2019, v. 20, p. S17, doi. 10.23902/trkjnat.483402

By:

GÜNEY ESKEN, Gülen;
EROL, Özgür Doğuş;
AERTS-KAYA, Fatima

Publication type:

Article

脑胶质瘤的基因治疗与病毒治疗研究进展.

Published in:

Journal of Clinical Neurosurgery / Linchuang Shenjingwaike Zazhi, 2021, v. 18, n. 2, p. 237, doi. 10.3969/j.issn.1672-7770.2021.02.026

By:

张国栋;
鞠海涛;
黄平;
岳鹏;
万方;
窦长武

Publication type:

Article

Radioresponsive tumor necrosis factor-related apoptosis-inducing ligand (TRAIL) gene therapy for malignant brain tumors.

Published in:

Cancer Gene Therapy, 2007, v. 14, n. 8, p. 706, doi. 10.1038/sj.cgt.7701065

By:

Tsurushima, H.;
Yuan, X.;
Dillehay, L. E.;
Leong, K. W.

Publication type:

Article

International Society for Cell and Gene Therapy of Cancer: 2005 meeting in Shenzhen, China.

Published in:

Cancer Gene Therapy, 2007, v. 14, n. 2, p. 128, doi. 10.1038/sj.cgt.7700996

By:

Guinn, B. A.;
Norris, J. S.;
Farzaneh, F.;
Deisseroth, A. B.

Publication type:

Article

Gene therapy for carcinoma of the breast.

Published in:

Cancer Gene Therapy, 2006, v. 13, n. 7, p. 633, doi. 10.1038/sj.cgt.7700929

By:

Stoff-Khalili, M. A.;
Dall, P.;
Curiel, D. T.

Publication type:

Article

The insulinoma-associated 1: a novel promoter for targeted cancer gene therapy for small-cell lung cancer.

Published in:

Cancer Gene Therapy, 2006, v. 13, n. 4, p. 375, doi. 10.1038/sj.cgt.7700887

By:

Pedersen, N.;
Pedersen, M. W.;
Lan, M. S.;
Breslin, M. B.;
Poulsen, H. S.

Publication type:

Article

In suicide gene therapy, the site of subcellular localization of the activating enzyme is more important than the rate at which it activates prodrug.

Published in:

Cancer Gene Therapy, 2000, v. 7, n. 10, p. 1348, doi. 10.1038/sj.cgt.0238

By:

Spooner, Robert A;
Martin, Janet;
Friedlos, Frank;
Marais, Richard;
Springer, Caroline J

Publication type:

Article

Генная терапия, или допинг будущего.

Published in:

Science in Olympic Sports, 2019, n. 4, p. 24

By:

Стурбос, Хавьер;
Мейер, Эдди;
Шамаш, Патрик;
Куммиски, Йозеф;
Де Мерод, Принц Александр

Publication type:

Article

ИКОНОМИЧЕСКИ АСПЕКТИ НА ФАРМАКОГЕНОМИКАТА И ГЕННИТЕ ТЕРАПИИ

Published in:

Medical Review / Meditsinski Pregled, 2024, v. 60, n. 2, p. 42

By:

Веков, Т.;
Петрова, Г.;
Бечева-Крайчир, Е.;
Колев, Ж.

Publication type:

Article

RESPUESTA INMUNE Y TERAPIA GÉNICA CON VECTORES VIRALES ADENOASOCIADOS.

Published in:

Medicina (Buenos Aires), 2019, v. 79, n. 6, p. 493

By:

SIERRA-DELGADO, JULIETH A.;
BAUTISTA-NINO, PAULA K.;
VARGAS-CASTELLANOS, CLARA I.;
SERRANO DIAZ, NORMA C.;
RINCON, MELVIN Y.

Publication type:

Article

Hemophilia A gene therapy via intraosseous delivery of factor VIII-lentiviral vectors.

Published in:

Thrombosis Journal, 2016, v. 14, p. 93, doi. 10.1186/s12959-016-0105-1

By:

Miao, Carol H.

Publication type:

Article

The Current State of Cancer Gene Therapy and Its Application in Esophageal Carcinoma.

Published in:

Digestive Surgery, 2005, v. 22, n. 4, p. 222, doi. 10.1159/000088052

By:

Buskens, Christianne J.;
Marsman, Willem A.;
Bosma, Piter J.;
Van Lanschot, J. Jan V.

Publication type:

Article

遗传性耳聋基因治疗专家共识（2023，上海）.

Published in:

Chinese Journal of Ophthalmology & Otorhinolaryngology, 2024, v. 24, n. 1, p. 1, doi. 10.14166/j.issn.1671-2420.2024.01.001

By:

舒易来;
范新泰;
高子雯;
王大奇;
程晓婷;
吕俊;
胡纯纯;
徐秀;
周旭娇;
郭荦;
马竞;
张剑宁;
陶永;
孙珊;
杨美琴;
胡炯炯;
蔡宇伽;
李大力;
李耕林;
杨军

Publication type:

Article

Gene therapy - Principles and Applications.

Published in:

Global Journal of Transfusion Medicine, 2022, v. 7, n. 1, p. 3, doi. 10.4103/gjtm.gjtm_87_21

By:

Pathak, Sangeeta

Publication type:

Article

Gene therapy breakthroughs in ALS: a beacon of hope for 20% of ALS patients.

Published in:

Translational Neurodegeneration, 2025, v. 14, n. 1, p. 1, doi. 10.1186/s40035-025-00477-6

By:

Xie, Qingjian;
Li, Kezheng;
Chen, Yinuo;
Li, Yaojia;
Jiang, Wenhua;
Cao, Wen;
Yu, Huan;
Fan, Dongsheng;
Deng, Binbin

Publication type:

Article

Biosimilar Gene Therapy: Investigational Assessment of Secukinumab Gene Therapy.

Published in:

Cell Journal (Yakhteh), 2020, v. 21, n. 4, p. 433, doi. 10.22074/cellj.2020.6309

By:

Fallah, Ali;
Estiri, Hajar;
Parrish, Elizabeth;
Soleimani, Mansoureh;
Zeinali, Sirous;
Zadeh-Vakili, Azita

Publication type:

Article

Updates on Current Advances in Gene Therapy.

Published in:

West Indian Medical Journal, 2011, v. 60, n. 2, p. 188

By:

Tani, Jowy;
Sufian, Jomiany Tani

Publication type:

Article

Anti-Scg3 Gene Therapy to Treat Choroidal Neovascularization in Mice.

Published in:

Biomedicines, 2023, v. 11, n. 7, p. 1910, doi. 10.3390/biomedicines11071910

By:

Huang, Chengchi;
Ji, Liyang;
Kaur, Avinash;
Tian, Hong;
Waduge, Prabuddha;
Webster, Keith A.;
Li, Wei

Publication type:

Article

Gene therapy randomised clinical trials in Europe – a review paper of methodology and design.

Published in:

Journal of Market Access & Health Policy, 2020, v. 8, n. 1, p. 1, doi. 10.1080/20016689.2020.1847808

By:

Ilieva, Krassimira;
Borissov, Borislav;
Toumi, Mondher

Publication type:

Article

Various AAV Serotypes and Their Applications in Gene Therapy: An Overview.

Published in:

Cells (2073-4409), 2023, v. 12, n. 5, p. 785, doi. 10.3390/cells12050785

By:

Issa, Shaza S.;
Shaimardanova, Alisa A.;
Solovyeva, Valeriya V.;
Rizvanov, Albert A.

Publication type:

Article

Cellular Vehicles for Cancer Gene Therapy: Current Status and Future Potential.

Published in:

BioDrugs, 2004, v. 18, n. 6, p. 361, doi. 10.2165/00063030-200418060-00003

By:

Pereboeva, Larisa;
Curiel, David T.

Publication type:

Article

INGN 201: Ad-p53, Ad5CMV-p53, Adenoviral p53, INGN 101, p53 gene therapy – Introgen, RPR/INGN 201.

Published in:: BioDrugs, 2003, v. 17, n. 3, p. 216
Publication type:: Article

Perspectives on Gene Therapy for Cystic Fibrosis Airway Disease.

Published in:

BioDrugs, 2001, v. 15, n. 9, p. 615, doi. 10.2165/00063030-200115090-00006

By:

Bigger, B.;
Coutelle, C.

Publication type:

Article

Gene Therapy for Colorectal Cancer: Therapeutic Potential.

Published in:

BioDrugs, 2001, v. 15, n. 6, p. 357, doi. 10.2165/00063030-200115060-00002

By:

Chen, M-J.;
Chung-Faye, G.A.;
Searle, P.F.;
Young, L.S.;
Kerr, D.J.

Publication type:

Article

Current Status of Gene Therapy for Rheumatoid Arthritis.

Published in:

BioDrugs, 1999, v. 11, n. 2, p. 103, doi. 10.2165/00063030-199911020-00004

By:

Reinecke, J.;
Koch, H.;
Meijer, H.;
Granrath, M.;
Schulitz, K-P.;
Wehling, P.

Publication type:

Article

An Overview of Gene Therapy Approaches to Neurological Malignancies.

Published in:

BioDrugs, 1998, v. 9, n. 4, p. 337, doi. 10.2165/00063030-199809040-00006

By:

Izquierdo, M.L.

Publication type:

Article

Effect of suicide gene therapy in combination with immunotherapy on antitumour immune response & tumour regression in a xenograft mouse model for head & neck squamous cell carcinoma.

Published in:

Indian Journal of Medical Research, 2010, v. 132, n. 4, p. 415

By:

Ambade, Aditya V.;
Joshi, Ganesh V.;
Mulherkar, Rita

Publication type:

Article

UKHCDO gene therapy taskforce: Guidance for implementation of haemophilia gene therapy into routine clinical practice for adults.

Published in:

Haemophilia, 2025, v. 31, n. 1, p. 26, doi. 10.1111/hae.15125

By:

Chowdary, Pratima;
Duran, Beatriz;
Batty, Paul;
Lowe, Gillian;
Jones, April;
Pollard, Debra;
Boyce, Sara;
Motwani, Jayashree;
Amirloo, Bahareh;
Musgrave, Kathryn;
Hopper, David;
Classey, Stephen;
Whitaker, Sarah;
Dunn, Nicola;
Bowyer, Annette;
Shapiro, Susan

Publication type:

Article

Towards a global multidisciplinary consensus framework on haemophilia gene therapy: Report of the 2nd World Federation of Haemophilia Gene Therapy Round Table.

Published in:

Haemophilia, 2020, v. 26, n. 3, p. 443, doi. 10.1111/hae.13971

By:

Pierce, Glenn F.;
Pasi, K. John;
Coffin, Donna;
Kaczmarek, Radoslaw;
Lillicrap, David;
Mahlangu, Johnny;
Rottellini, Dawn;
Sannié, Thomas;
Srivastava, Alok;
VandenDriessche, Thierry;
Weill, Alain;
Almeida, Antonio J.;
Baumann, Alain;
Brooker, Mark;
Durante, Luisa;
Naccache, Mayss;
Robinson, Fiona

Publication type:

Article

Clinical advances in gene therapy updates on clinical trials of gene therapy in haemophilia.

Published in:

Haemophilia, 2019, v. 25, n. 5, p. 738, doi. 10.1111/hae.13816

By:

Peyvandi, Flora;
Garagiola, Isabella

Publication type:

Article

The 1st WFH Gene Therapy Round Table: Understanding the landscape and challenges of gene therapy for haemophilia around the world.

Published in:

Haemophilia, 2019, v. 25, n. 2, p. 189, doi. 10.1111/hae.13673

By:

Pierce, Glenn F.;
Coffin, Donna;
Lillicrap, David;
Ozelo, Margareth;
Pasi, John;
Rotellini, Dawn;
Marquez, Safadi;
Sannié, Thomas;
Srivastava, Alok;
Berg, Marijke;
Weill, Alain;
Almeida, Antonio;
Baumann, Alain;
Brooker, Mark;
Durante, Luisa;
Naccache, Mayss;
Robinson, Fiona;
Bagley, Lisa;
Chapin, John;
Diop, Saliou

Publication type:

Article

Gene therapy for renal diseases.

Published in:

Kidney International Supplement, 1997, n. 61, p. S-85, doi. 10.1111/1523-1755.ep17695596

By:

Lien, Yeong-Hau H.;
Li-Wen Lai

Publication type:

Article

Gene therapy and its applications.

Published in:

Journal of Medical Evidence, 2023, v. 4, n. 1, p. 46, doi. 10.4103/JME.JME_65_21

By:

Bansal, Alka;
Prakash, Ravi;
Agarwal, Swati;
Advani, Uma

Publication type:

Article

Secretion of thymidine kinase to increase the effectivity of suicide gene therapy results in the loss of enzymatic activity.

Published in:

Journal of Drug Targeting, 2008, v. 16, n. 1, p. 26, doi. 10.1080/10611860701637768

By:

Beerens, A. M. J.;
Rots, M. G.;
Bermúdez, B.;
de Vries, E. F. J.;
Haisma, H. J.

Publication type:

Article

Gene therapy for cancer and metastatic disease.

Published in:

Expert Reviews in Molecular Medicine, 2003, v. 5, n. 17, p. 1, doi. 10.1017/S1462399403006380

By:

Kesmodel, Susan B.;
Spitz, Francis R.

Publication type:

Article