Works matching IS 19466234 AND DT 2025 AND VI 17 AND IP 785


Results: 6
    1

    Antisense oligonucleotide–mediated MSH3 suppression reduces somatic CAG repeat expansion in Huntington's disease iPSC–derived striatal neurons.

    Published in:
    Science Translational Medicine, 2025, v. 17, n. 785, p. 1, doi. 10.1126/scitranslmed.adn4600
    By:
    • Bunting, Emma L.;
    • Donaldson, Jasmine;
    • Cumming, Sarah A.;
    • Olive, Jessica;
    • Broom, Elizabeth;
    • Miclăuș, Mihai;
    • Hamilton, Joseph;
    • Tegtmeyer, Matthew;
    • Zhao, Hien T.;
    • Brenton, Jonathan;
    • Lee, Won-Seok;
    • Handsaker, Robert E.;
    • Li, Susan;
    • Ford, Brittany;
    • Ryten, Mina;
    • McCarroll, Steven A.;
    • Kordasiewicz, Holly B.;
    • Monckton, Darren G.;
    • Balmus, Gabriel;
    • Flower, Michael
    Publication type:
    Article
    2

    Early detection of pancreatic cancer by a high-throughput protease-activated nanosensor assay.

    Published in:
    Science Translational Medicine, 2025, v. 17, n. 785, p. 1, doi. 10.1126/scitranslmed.adq3110
    By:
    • Montoya Mira, Jose L.;
    • Quentel, Arnaud;
    • Patel, Ranish K.;
    • Keith, Dove;
    • Sousa, Megan;
    • Minnier, Jessica;
    • Kingston, Benjamin R.;
    • David, Larry;
    • Esener, Sadik C.;
    • Sears, Rosalie C.;
    • Lopez, Charles D.;
    • Sheppard, Brett C.;
    • Demirci, Utkan;
    • Wong, Melissa H.;
    • Fischer, Jared M.
    Publication type:
    Article
    3
    4
    5

    In vivo expansion of gene-targeted hepatocytes through transient inhibition of an essential gene.

    Published in:
    Science Translational Medicine, 2025, v. 17, n. 785, p. 1, doi. 10.1126/scitranslmed.adk3920
    By:
    • De Giorgi, Marco;
    • Park, So Hyun;
    • Castoreno, Adam;
    • Cao, Mingming;
    • Hurley, Ayrea;
    • Saxena, Lavanya;
    • Chuecos, Marcel A.;
    • Walkey, Christopher J.;
    • Doerfler, Alexandria M.;
    • Furgurson, Mia N.;
    • Ljungberg, M. Cecilia;
    • Patel, Kalyani R.;
    • Hyde, Sarah;
    • Chickering, Tyler;
    • Lefebvre, Stephanie;
    • Wassarman, Kelly;
    • Miller, Patrick;
    • Qin, June;
    • Schlegel, Mark K.;
    • Zlatev, Ivan
    Publication type:
    Article
    6