- Title
Selection-free precise gene repair using high-capacity adenovector delivery of advanced prime editing systems rescues dystrophin synthesis in DMD muscle cells.
- Authors
Wang, Qian; Capelletti, Sabrina; Liu, Jin; Janssen, Josephine M; Gonçalves, Manuel A F V
- Publication
Nucleic Acids Research, 2024, Vol 52, Issue 5, p2740
- ISSN
0305-1048
- Publication type
Academic Journal
- DOI
10.1093/nar/gkae057