Works matching AU Mall, Marcus A.

Results: 187

Progress of personalized medicine of cystic fibrosis in the times of efficient CFTR modulators.

Published in:

Molecular & Cellular Pediatrics, 2025, v. 12, n. 1, p. 1, doi. 10.1186/s40348-025-00194-0

By:

Tümmler, Burkhard;
Pallenberg, Sophia Theres;
Dittrich, Anna-Maria;
Graeber, Simon Y.;
Naehrlich, Lutz;
Sommerburg, Olaf;
Mall, Marcus A.

Publication type:

Article

Räumlich aufgelöste Analyse der Aktivität der Neutrophilenelastase mit ratiometrischen Fluoreszenzsonden.

Published in:

Angewandte Chemie, 2012, v. 124, n. 25, p. 6363, doi. 10.1002/ange.201109226

By:

Gehrig, Stefanie;
Mall, Marcus A.;
Schultz, Carsten

Publication type:

Article

Reply to Martin and Grasemann: Is There a Role for Lumacaftor/Ivacaftor in Young Children with Cystic Fibrosis?

Published in:

Annals of the American Thoracic Society, 2025, v. 22, n. 3, p. 469, doi. 10.1513/AnnalsATS.202411-1237LE

By:

Stahl, Mirjam;
Röhmel, Jobst;
Wielpütz, Mark O.;
Mall, Marcus A.

Publication type:

Article

Longitudinal Magnetic Resonance Imaging of Changes in Lung Morphology and Perfusion in Children with Cystic Fibrosis from Infancy through Adolescence.

Published in:

Annals of the American Thoracic Society, 2025, v. 22, n. 1, p. 93, doi. 10.1513/AnnalsATS.202404-396OC

By:

Wielpütz, Mark O.;
Stahl, Mirjam;
Triphan, Simon M. F.;
Wucherpfennig, Lena;
Leutz-Schmidt, Patricia;
Gestewitz, Sonja;
Steinke, Eva;
Graeber, Simon Y.;
Kauczor, Hans-Ulrich;
Eichinger, Monika;
Puderbach, Michael U.;
Alrajab, Abdulsattar;
Schenk, Jens-Peter;
Sommerburg, Olaf;
Mall, Marcus A.

Publication type:

Article

Long-Term Impact of Lumacaftor/Ivacaftor Treatment on Cystic Fibrosis Disease Progression in Children 2–5 Years of Age Homozygous for F508del-CFTR : A Phase 2, Open-Label Clinical Trial.

Published in:

Annals of the American Thoracic Society, 2024, v. 21, n. 11, p. 1550, doi. 10.1513/AnnalsATS.202402-201OC

By:

Stahl, Mirjam;
Roehmel, Jobst;
Eichinger, Monika;
Doellinger, Felix;
Naehrlich, Lutz;
Kopp, Matthias V.;
Dittrich, Anna-Maria;
Sommerburg, Olaf;
Ray, Partha;
Maniktala, Anita;
Xu, Tu;
Conner, Sarah;
Joshi, Aniket;
Mascia, Molly;
Wielpütz, Mark O.;
Mall, Marcus A.

Publication type:

Article

Magnetic Resonance Imaging of Pulmonary and Paranasal Sinus Abnormalities in Children with Primary Ciliary Dyskinesia Compared to Children with Cystic Fibrosis.

Published in:

Annals of the American Thoracic Society, 2024, v. 21, n. 3, p. 438, doi. 10.1513/AnnalsATS.202305-453OC

By:

Wucherpfennig, Lena;
Wuennemann, Felix;
Eichinger, Monika;
Schmitt, Niclas;
Seitz, Angelika;
Baumann, Ingo;
Roehmel, Jobst F.;
Stahl, Mirjam;
Hämmerling, Susanne;
Chung, Jaehi;
Schenk, Jens-Peter;
Alrajab, Abdulsattar;
Kauczor, Hans-Ulrich;
Mall, Marcus A.;
Wielpütz, Mark O.;
Sommerburg, Olaf

Publication type:

Article

Elexacaftor/Tezacaftor/Ivacaftor Improves Bronchial Artery Dilatation Detected by Magnetic Resonance Imaging in Patients with Cystic Fibrosis.

Published in:

Annals of the American Thoracic Society, 2023, v. 20, n. 11, p. 1595, doi. 10.1513/AnnalsATS.202302-168OC

By:

Wucherpfennig, Lena;
Triphan, Simon M. F.;
Wege, Sabine;
Kauczor, Hans-Ulrich;
Heussel, Claus P.;
Sommerburg, Olaf;
Stahl, Mirjam;
Mall, Marcus A.;
Eichinger, Monika;
Wielpütz, Mark O.

Publication type:

Article

Effects of Lumacaftor/Ivacaftor on Cystic Fibrosis Disease Progression in Children 2 through 5 Years of Age Homozygous for F508del-CFTR: A Phase 2 Placebo-controlled Clinical Trial.

Published in:

Annals of the American Thoracic Society, 2023, v. 20, n. 8, p. 1144, doi. 10.1513/AnnalsATS.202208-684OC

By:

Stahl, Mirjam;
Roehmel, Jobst;
Eichinger, Monika;
Doellinger, Felix;
Naehrlich, Lutz;
Kopp, Matthias V.;
Dittrich, Anna-Maria;
Lee, Christopher;
Sommerburg, Olaf;
Simon Tian;
Tu Xu;
Pan Wu;
Joshi, Aniket;
Ray, Partha;
Duncan, Margaret E.;
Wielputz, Mark O.;
Mall, Marcus A.

Publication type:

Article

Longitudinal Magnetic Resonance Imaging Detects Onset and Progression of Chronic Rhinosinusitis from Infancy to School Age in Cystic Fibrosis.

Published in:

Annals of the American Thoracic Society, 2023, v. 20, n. 5, p. 687, doi. 10.1513/AnnalsATS.202209-763OC

By:

Wucherpfennig, Lena;
Wuennemann, Felix;
Eichinger, Monika;
Schmitt, Niclas;
Seitz, Angelika;
Baumann, Ingo;
Stahl, Mirjam;
Graeber, Simon Y.;
Jaehi Chung;
Schenk, Jens-Peter;
Alrajab, Abdulsattar;
Kauczor, Hans-Ulrich;
Mall, Marcus A.;
Sommerburg, Olaf;
Wielpütz, Mark O.

Publication type:

Article

Effects of Lumacaftor-Ivacaftor on Lung Clearance Index, Magnetic Resonance Imaging, and Airway Microbiome in Phe508del Homozygous Patients with Cystic Fibrosis.

Published in:

2021

By:

Graeber, Simon Y.;
Boutin, Sébastien;
Wielpütz, Mark O.;
Joachim, Cornelia;
Frey, Dario L.;
Wege, Sabine;
Sommerburg, Olaf;
Kauczor, Hans-Ulrich;
Stahl, Mirjam;
Dalpke, Alexander H.;
Mall, Marcus A.

Publication type:

journal article

Magnetic Resonance Imaging Detects Chronic Rhinosinusitis in Infants and Preschool Children with Cystic Fibrosis.

Published in:

2020

By:

Sommerburg, Olaf;
Wielpütz, Mark O.;
Trame, Jan-Philipp;
Wuennemann, Felix;
Opdazaite, Elzbieta;
Stahl, Mirjam;
Puderbach, Michael U.;
Kopp-Schneider, Annette;
Fritzsching, Eva;
Kauczor, Hans-Ulrich;
Baumann, Ingo;
Mall, Marcus A.;
Eichinger, Monika

Publication type:

journal article

Emerging Concepts and Therapies for Mucoobstructive Lung Disease.

Published in:

2018

By:

Mall, Marcus A;
Danahay, Henry;
Boucher, Richard C

Publication type:

journal article

Unplugging Mucus in Cystic Fibrosis and Chronic Obstructive Pulmonary Disease.

Published in:

2016

By:

Mall, Marcus A.

Publication type:

journal article

Effects of lumacaftor--ivacaftor therapy on cystic fibrosis transmembrane conductance regulator function in F508del homozygous patients with cystic fibrosis aged 2-11 years.

Published in:

Frontiers in Pharmacology, 2023, p. 1, doi. 10.3389/fphar.2023.1188051

By:

Berges, Julian;
Graeber, Simon Y.;
Hämmerling, Susanne;
Yin Yu;
Krümpelmann, Arne;
Stahl, Mirjam;
Hirtz, Stephanie;
Scheuermann, Heike;
Mall, Marcus A.;
Sommerburg, Olaf

Publication type:

Article

Effects of elexacaftor/tezacaftor/ ivacaftor therapy on mental health of patients with cystic fibrosis.

Published in:

Frontiers in Pharmacology, 2023, p. 1, doi. 10.3389/fphar.2023.1179208

By:

Piehler, Linus;
Thalemann, Ralf;
Lehmann, Christine;
Thee, Stephanie;
Röhmel, Jobst;
Syunyaeva, Zulfiya;
Stahl, Mirjam;
Mall, Marcus A.;
Graeber, Simon Y.

Publication type:

Article

Long-term effects of lumacaftor/ivacaftor on paranasal sinus abnormalities in children with cystic fibrosis detected with magnetic resonance imaging.

Published in:

Frontiers in Pharmacology, 2023, v. 14, p. 1, doi. 10.3389/fphar.2023.1161891

By:

Wucherpfennig, Lena;
Wuennemann, Felix;
Eichinger, Monika;
Seitz, Angelika;
Baumann, Ingo;
Stahl, Mirjam;
Graeber, Simon Y.;
Shengkai Zhao;
Jaehi Chung;
Schenk, Jens-Peter;
Alrajab, Abdulsattar;
Kauczor, Hans-Ulrich;
Mall, Marcus A.;
Sommerburg, Olaf;
Wielpütz, Mark O.

Publication type:

Article

Changes in Microbiome Dominance Are Associated With Declining Lung Function and Fluctuating Inflammation in People With Cystic Fibrosis.

Published in:

Frontiers in Microbiology, 2022, v. 13, p. 1, doi. 10.3389/fmicb.2022.885822

By:

Frey, Dario L.;
Bridson, Calum;
Dittrich, Susanne;
Graeber, Simon Y.;
Stahl, Mirjam;
Wege, Sabine;
Herth, Felix;
Sommerburg, Olaf;
Schultz, Carsten;
Dalpke, Alexander;
Mall, Marcus A.;
Boutin, Sébastien

Publication type:

Article

Homozygous CFTR mutation M348K in a boy with respiratory symptoms and failure to thrive. Disease-causing mutation or benign alteration?

Published in:

European Journal of Pediatrics, 2012, v. 171, n. 7, p. 1039, doi. 10.1007/s00431-012-1672-1

By:

Hentschel, Julia;
Riesener, Gabriele;
Nelle, Heike;
Stuhrmann, Manfred;
Schöner, Anja;
Sommerburg, Olaf;
Fritzsching, Eva;
Mall, Marcus;
Eggeling, Ferdinand;
Mainz, Jochen

Publication type:

Article

Ion mobility-tandem mass spectrometry of mucin-type O-glycans.

Published in:

Nature Communications, 2024, v. 15, n. 1, p. 1, doi. 10.1038/s41467-024-46825-4

By:

Bechtella, Leïla;
Jin Chunsheng;
Fentker, Kerstin;
Ertürk, Güney R.;
Safferthal, Marc;
Polewski, Łukasz;
Götze, Michael;
Graeber, Simon Y.;
Vos, Gaël M.;
Struwe, Weston B.;
Mall, Marcus A.;
Mertins, Philipp;
Karlsson, Niclas G.;
Pagel, Kevin

Publication type:

Article

Ductal Mucus Obstruction and Reduced Fluid Secretion Are Early Defects in Chronic Pancreatitis.

Published in:

Frontiers in Physiology, 2018, p. 1, doi. 10.3389/fphys.2018.00632

By:

Balázs, Anita;
Balla, Zsolt;
Kui, Balázs;
Maléth, József;
Rakonczay Jr., Zoltán;
Duerr, Julia;
Zhou-Suckow, Zhe;
Schatterny, Jolanthe;
Sendler, Matthias;
Mayerle, Julia;
Kühn, Jens-P.;
Tiszlavicz, László;
Mall, Marcus A.;
Hegyi, Peter

Publication type:

Article

Health-related quality of life and impact of socioeconomic status among primary and secondary school students after the third COVID-19 wave in Berlin, Germany.

Published in:

PLoS ONE, 2024, v. 19, n. 5, p. 1, doi. 10.1371/journal.pone.0302995

By:

Kern, Mascha;
Glatz, Toivo;
Mall, Marcus A.;
Seybold, Joachim;
Kurth, Tobias;
Mockenhaupt, Frank P.;
Theuring, Stefanie

Publication type:

Article

Therapeutic Inhibition of Cathepsin S Reduces Inflammation and Mucus Plugging in Adult βENaC-Tg Mice.

Published in:

Mediators of Inflammation, 2021, p. 1, doi. 10.1155/2021/6682657

By:

Brown, Ryan;
Small, Donna M.;
Doherty, Declan F.;
Holsinger, Leslie;
Booth, Robert;
Williams, Richard;
Ingram, Rebecca J.;
Elborn, J. Stuart;
Mall, Marcus A.;
Taggart, Clifford C.;
Weldon, Sinéad

Publication type:

Article

Initial evaluation of a biochemical cystic fibrosis newborn screening by sequential analysis of immunoreactive trypsinogen and pancreatitis-associated protein (IRT/PAP) as a strategy that does not involve DNA testing in a Northern European population.

Published in:

Journal of Inherited Metabolic Disease, 2010, v. 33, p. 263, doi. 10.1007/s10545-010-9174-7

By:

Sommerburg, Olaf;
Lindner, Martin;
Muckenthaler, Martina;
Kohlmueller, Dirk;
Leible, Svenja;
Feneberg, Reinhard;
Kulozik, Andreas;
Mall, Marcus;
Hoffmann, Georg

Publication type:

Article

Pleuropneumonia caused by Nocardia cyriacigeorgica in a 14‐year‐old girl with primary ciliary dyskinesia.

Published in:

Pediatric Pulmonology, 2023, v. 58, n. 9, p. 2656, doi. 10.1002/ppul.26536

By:

Urbantat, Ruth M.;
Pioch, Charlotte O.;
Ziegahn, Niklas;
Stegemann, Miriam S.;
Stahl, Mirjam;
Mall, Marcus A.;
Roehmel, Jobst F.

Publication type:

Article

Mucus obstruction and inflammation in early cystic fibrosis lung disease: Emerging role of the IL‐1 signaling pathway.

Published in:

Pediatric Pulmonology, 2019, v. 54, p. S5, doi. 10.1002/ppul.24462

By:

Balázs, Anita;
Mall, Marcus A.

Publication type:

Article

Rare cause for hemoptysis in an adolescent: Bronchial capillary hemangioma.

Published in:

Pediatric Pulmonology, 2017, v. 52, n. 7, p. E40, doi. 10.1002/ppul.23673

By:

Hämmerling, Susanne;
Becker, Sebastian;
Mall, Marcus A.

Publication type:

Article

Five years of experience with biochemical cystic fibrosis newborn screening based on IRT/PAP in Germany.

Published in:

Pediatric Pulmonology, 2015, v. 50, n. 7, p. 655, doi. 10.1002/ppul.23190

By:

Sommerburg, Olaf;
Hammermann, Jutta;
Lindner, Martin;
Stahl, Mirjam;
Muckenthaler, Martina;
Kohlmueller, Dirk;
Happich, Margit;
Kulozik, Andreas E.;
Stopsack, Marina;
Gahr, Manfred;
Hoffmann, Georg F.;
Mall, Marcus A.

Publication type:

Article

Ten years of chest MRI for patients with cystic fibrosis: Translation from the bench to clinical routine.

Published in:

Der Radiologe, 2019, v. 59, p. 10, doi. 10.1007/s00117-019-0553-2

By:

Leutz-Schmidt, Patricia;
Eichinger, Monika;
Stahl, Mirjam;
Sommerburg, Olaf;
Biederer, Jürgen;
Kauczor, Hans-Ulrich;
Puderbach, Michael U.;
Mall, Marcus A.;
Wielpütz, Mark O.

Publication type:

Article

Incidence and outcomes of SARS-CoV-2-associated PIMS in Germany: a nationwide analysis.

Published in:

2022

By:

Karagiannidis, Christian;
Sander, Leif-Erik;
Mall, Marcus A.;
Busse, Reinhard

Publication type:

Letter

Studying the pathophysiology of coronavirus disease 2019: a protocol for the Berlin prospective COVID-19 patient cohort (Pa-COVID-19).

Published in:

Infection, 2020, v. 48, n. 4, p. 619, doi. 10.1007/s15010-020-01464-x

By:

Kurth, Florian;
Roennefarth, Maria;
Thibeault, Charlotte;
Corman, Victor M.;
Müller-Redetzky, Holger;
Mittermaier, Mirja;
Ruwwe-Glösenkamp, Christoph;
Heim, Katrin M.;
Krannich, Alexander;
Zvorc, Saskia;
Schmidt, Sein;
Kretzler, Lucie;
Dang-Heine, Chantip;
Rose, Matthias;
Hummel, Michael;
Hocke, Andreas;
Hübner, Ralf H.;
Opitz, Bastian;
Mall, Marcus A.;
Röhmel, Jobst

Publication type:

Article

Mukoviszidose im Kindes- und im Erwachsenenalter.

Published in:

Innere Medizin (2731-7080), 2024, v. 65, n. 6, p. 538, doi. 10.1007/s00108-024-01717-z

By:

Syunyaeva, Zulfiya;
Mall, Marcus A.;
Stahl, Mirjam

Publication type:

Article

Immune-mediated inflammatory diseases (IMIDs) in children: key research questions and some answers.

Published in:

Molecular & Cellular Pediatrics, 2024, v. 11, n. 1, p. 1, doi. 10.1186/s40348-024-00177-7

By:

Kallinich, Tilmann;
Mall, Marcus A.

Publication type:

Article

DMBT1 is upregulated in cystic fibrosis, affects ciliary motility, and is reduced by acetylcysteine.

Published in:

Molecular & Cellular Pediatrics, 2022, v. 9, n. 1, p. 1, doi. 10.1186/s40348-022-00136-0

By:

Kiefer, Alexander;
Plattner, Erika;
Ruppel, Renate;
Weiss, Christel;
Zhou-Suckow, Zhe;
Mall, Marcus;
Renner, Marcus;
Müller, Hanna

Publication type:

Article

DMBT1 is upregulated in cystic fibrosis, affects ciliary motility, and is reduced by acetylcysteine.

Published in:

Molecular & Cellular Pediatrics, 2022, v. 9, n. 1, p. 1, doi. 10.1186/s40348-022-00136-0

By:

Kiefer, Alexander;
Plattner, Erika;
Ruppel, Renate;
Weiss, Christel;
Zhou-Suckow, Zhe;
Mall, Marcus;
Renner, Marcus;
Müller, Hanna

Publication type:

Article

Post-infection symptoms up to 24 months after COVID-19: a matched cohort study in Berlin, Germany.

Published in:

Frontiers in Public Health, 2025, p. 1, doi. 10.3389/fpubh.2025.1513664

By:

Meierkord, Anne;
Schulze, Daniel;
Gertler, Maximilian;
Seybold, Joachim;
Mall, Marcus A.;
Kurth, Tobias;
Mockenhaupt, Frank P.;
Theuring, Stefanie

Publication type:

Article

Potential of Intestinal Current Measurement for Personalized Treatment of Patients with Cystic Fibrosis.

Published in:

Journal of Personalized Medicine, 2021, v. 11, n. 5, p. 384, doi. 10.3390/jpm11050384

By:

Graeber, Simon Y.;
Vitzthum, Constanze;
Mall, Marcus A.;
van der Ent, Cornelis K.;
Heijerman, Harry G. M.

Publication type:

Article

Dextromethorphan inhibits collagen and collagen-like cargo secretion to ameliorate lung fibrosis.

Published in:

Science Translational Medicine, 2024, v. 16, n. 778, p. 1, doi. 10.1126/scitranslmed.adj3087

By:

Khan, Muzamil M.;
Galea, George;
Jung, Juan;
Zukowska, Joanna;
Lauer, David;
Tuechler, Nadine;
Halavatyi, Aliaksandr;
Tischer, Christian;
Haberkant, Per;
Stein, Frank;
Jung, Ferris;
Landry, Jonathan J. M.;
Khan, Arif M.;
Oorschot, Viola;
Becher, Isabelle;
Neumann, Beate;
Muley, Thomas;
Winter, Hauke;
Duerr, Julia;
Mall, Marcus A

Publication type:

Article

Gene signature driving invasive mucinous adenocarcinoma of the lung.

Published in:

EMBO Molecular Medicine, 2017, v. 9, n. 4, p. 462, doi. 10.15252/emmm.201606711

By:

Guo, Minzhe;
Tomoshige, Koichi;
Meister, Michael;
Muley, Thomas;
Fukazawa, Takuya;
Tsuchiya, Tomoshi;
Karns, Rebekah;
Warth, Arne;
Fink‐Baldauf, Iris M;
Nagayasu, Takeshi;
Naomoto, Yoshio;
Xu, Yan;
Mall, Marcus A;
Maeda, Yutaka

Publication type:

Article

SARS-CoV-2 infection and transmission in school settings during the second COVID-19 wave: a cross-sectional study, Berlin, Germany, November 2020.

Published in:

Eurosurveillance (15607917), 2021, v. 26, n. 34, p. 1, doi. 10.2807/1560-7917.ES.2021.26.34.2100184

By:

Theuring, Stefanie;
Thielecke, Marlene;
van Loon, Welmoed;
Homme, Franziska;
Hülso, Claudia;
von der Haar, Annkathrin;
Körner, Jennifer;
Schmidt, Michael;
Böhringer, Falko;
Mall, Marcus A.;
Rosen, Alexander;
von Kalle, Christof;
Kirchberger, Valerie;
Kurth, Tobias;
Seybold, Joachim;
Mockenhaupt, Frank P.

Publication type:

Article

Generalized anxiety disorder in Berlin school children after the third COVID-19 wave in Germany: a cohort study between June and September 2021.

Published in:

Child & Adolescent Psychiatry & Mental Health, 2023, v. 17, n. 1, p. 1, doi. 10.1186/s13034-022-00552-0

By:

Theuring, Stefanie;
Kern, Mascha;
Hommes, Franziska;
Mall, Marcus A.;
Seybold, Joachim;
Mockenhaupt, Frank P.;
Glatz, Toivo;
Kurth, Tobias

Publication type:

Article

Compromised DNA repair is responsible for diabetes‐associated fibrosis.

Published in:

EMBO Journal, 2020, v. 39, n. 11, p. 1, doi. 10.15252/embj.2019103477

By:

Kumar, Varun;
Agrawal, Raman;
Pandey, Aparamita;
Kopf, Stefan;
Hoeffgen, Manuel;
Kaymak, Serap;
Bandapalli, Obul Reddy;
Gorbunova, Vera;
Seluanov, Andrei;
Mall, Marcus A;
Herzig, Stephan;
Nawroth, Peter P

Publication type:

Article

Control of ion transport in mammalian airways by protease activated receptors type 2 (PAR-2).

Published in:

FASEB Journal, 2005, v. 19, n. 8, p. 969, doi. 10.1096/fj.04-2469fje

By:

Kunzelmann, Karl;
Sun, Jane;
Markovich, Daniel;
König, Jens;
Mürle, Bettina;
Mall, Marcus;
Schreiber, Rainer

Publication type:

Article

Depression Symptoms in Patients with Cystic Fibrosis Fluctuate at Baseline and Improve with Elexacaftor/Tezacaftor/Ivacaftor Therapy.

Published in:

2024

By:

Piehler, Linus;
Thalemann, Ralf;
Lehmann, Christine;
Stahl, Mirjam;
Mall, Marcus A.;
Graeber, Simon Y.

Publication type:

Letter to the Editor

Pharmacological Improvement of Cystic Fibrosis Transmembrane Conductance Regulator Function Rescues Airway Epithelial Homeostasis and Host Defense in Children with Cystic Fibrosis.

Published in:

American Journal of Respiratory & Critical Care Medicine, 2024, v. 209, n. 11, p. 1338, doi. 10.1164/rccm.202310-1836OC

By:

Loske, Jennifer;
Völler, Mirjam;
Lukassen, Sören;
Stahl, Mirjam;
Thürmann, Loreen;
Seegebarth, Anke;
Röhmel, Jobst;
Wisniewski, Sebastian;
Messingschlager, Marey;
Lorenz, Stephan;
Klages, Sven;
Eils, Roland;
Lehmann, Irina;
Mall, Marcus A.;
Graeber, Simon Y.;
Trump, Saskia

Publication type:

Article

Elexacaftor/Tezacaftor/Ivacaftor Treatment and Depression-related Events.

Published in:

American Journal of Respiratory & Critical Care Medicine, 2024, v. 209, n. 3, p. 299, doi. 10.1164/rccm.202308-1525OC

By:

Ramsey, Bonnie;
Correll, Christoph U.;
DeMaso, David R.;
McKone, Edward;
Tullis, Elizabeth;
Taylor-Cousar, Jennifer L.;
Chu, Chenghao;
Volkova, Nataliya;
Ahluwalia, Neil;
Waltz, David;
Tian, Simon;
Mall, Marcus A.

Publication type:

Article

Phase 3 Open-Label Clinical Trial of Elexacaftor/Tezacaftor/Ivacaftor in Children Aged 2–5 Years with Cystic Fibrosis and at Least One F508del Allele.

Published in:

American Journal of Respiratory & Critical Care Medicine, 2023, v. 208, n. 1, p. 59, doi. 10.1164/rccm.202301-0084OC

By:

Goralski, Jennifer L.;
Hoppe, Jordana E.;
Mall, Marcus A.;
McColley, Susanna A.;
McKone, Edward;
Ramsey, Bonnie;
Rayment, Jonathan H.;
Robinson, Phil;
Stehling, Florian;
Taylor-Cousar, Jennifer L.;
Tullis, Elizabeth;
Ahluwalia, Neil;
Anna Chin;
Chenghao Chu;
Mengdi Lu;
Tao Niu;
Weinstock, Tanya;
Ratjen, Felix;
Rosenfeld, Margaret

Publication type:

Article

Efficacy and Safety of Elexacaftor/Tezacaftor/Ivacaftor in Children 6 Through 11 Years of Age with Cystic Fibrosis Heterozygous for and a Minimal Function Mutation: A Phase 3b, Randomized, Placebo-controlled Study.

Published in:

American Journal of Respiratory & Critical Care Medicine, 2022, v. 206, n. 11, p. 1361, doi. 10.1164/rccm.202202-0392OC

By:

Mall, Marcus A.;
Brugha, Rossa;
Gartner, Silvia;
Legg, Julian;
Moeller, Alexander;
Mondejar-Lopez, Pedro;
Prais, Dario;
Pressler, Tacjana;
Ratjen, Felix;
Reix, Philippe;
Robinson, Paul D.;
Selvadurai, Hiran;
Stehling, Florian;
Ahluwalia, Neil;
Arteaga-Solis, Emilio;
Bruinsma, Bote G.;
Jennings, Mark;
Moskowitz, Samuel M.;
Noel, Sabrina;
Tian, Simon

Publication type:

Article

Effects of Elexacaftor/Tezacaftor/Ivacaftor Therapy on CFTR Function in Patients with Cystic Fibrosis and One or Two Alleles.

Published in:

2022

By:

Graeber, Simon Y.;
Vitzthum, Constanze;
Pallenberg, Sophia T.;
Naehrlich, Lutz;
Stahl, Mirjam;
Rohrbach, Alexander;
Drescher, Marika;
Minso, Rebecca;
Ringshausen, Felix C.;
Rueckes-Nilges, Claudia;
Klajda, Jan;
Berges, Julian;
Yin Yu;
Scheuermann, Heike;
Hirtz, Stephanie;
Sommerburg, Olaf;
Dittrich, Anna-Maria;
Tümmler, Burkhard;
Mall, Marcus A.;
Yu, Yin

Publication type:

journal article

Effects of Elexacaftor/Tezacaftor/Ivacaftor Therapy on CFTR Function in Patients with Cystic Fibrosis and One or Two F508del Alleles.

Published in:

American Journal of Respiratory & Critical Care Medicine, 2022, v. 205, n. 5, p. E1, doi. 10.1164/rccm.202110-2249oc

By:

Graeber, Simon Y.;
Vitzthum, Constanze;
Pallenberg, Sophia T.;
Naehrlich, Lutz;
Stahl, Mirjam;
Rohrbach, Alexander;
Drescher, Marika;
Minso, Rebecca;
Ringshausen, Felix C.;
Rueckes-Nilges, Claudia;
Klajda, Jan;
Berges, Julian;
Yin Yu;
Scheuermann, Heike;
Hirtz, Stephanie;
Sommerburg, Olaf;
Dittrich, Anna-Maria;
Tümmler, Burkhard;
Mall, Marcus A.

Publication type:

Article

Reply to Dournes .: Contrast-enhanced Magnetic Resonance Imaging Does Not Detect a Progression in Lung Morphological Score in Preschool Children with Cystic Fibrosis.

Published in:

2022

By:

Stahl, Mirjam;
Steinke, Eva;
Wielpütz, Mark O;
Mall, Marcus A

Publication type:

Letter