Works matching AU Naldini, Luigi


Results: 133
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    Editing T cell specificity towards leukemia by zinc finger nucleases and lentiviral gene transfer.

    Published in:
    Nature Medicine, 2012, v. 18, n. 5, p. 807, doi. 10.1038/nm.2700
    By:
    • Provasi, Elena;
    • Genovese, Pietro;
    • Lombardo, Angelo;
    • Magnani, Zulma;
    • Liu, Pei-Qi;
    • Reik, Andreas;
    • Chu, Victoria;
    • Paschon, David E;
    • Zhang, Lei;
    • Kuball, Jurgen;
    • Camisa, Barbara;
    • Bondanza, Attilio;
    • Casorati, Giulia;
    • Ponzoni, Maurilio;
    • Ciceri, Fabio;
    • Bordignon, Claudio;
    • Greenberg, Philip D;
    • Holmes, Michael C;
    • Gregory, Philip D;
    • Naldini, Luigi
    Publication type:
    Article
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    TIM-3, LAG-3, or 2B4 gene disruptions increase the anti-tumor response of engineered T cells.

    Published in:
    Frontiers in Immunology, 2024, p. 1, doi. 10.3389/fimmu.2024.1315283
    By:
    • Cianciotti, Beatrice Claudia;
    • Magnani, Zulma Irene;
    • Ugolini, Alessia;
    • Camisa, Barbara;
    • Merelli, Ivan;
    • Vavassori, Valentina;
    • Potenza, Alessia;
    • Imparato, Antonio;
    • Manfredi, Francesco;
    • Abbati, Danilo;
    • Perani, Laura;
    • Spinelli, Antonello;
    • Shifrut, Eric;
    • Ciceri, Fabio;
    • Vago, Luca;
    • Di Micco, Raffaella;
    • Naldini, Luigi;
    • Genovese, Pietro;
    • Ruggiero, Eliana;
    • Bonini, Chiara
    Publication type:
    Article
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    Liver-directed lentiviral gene therapy corrects hemophilia A mice and achieves normal-range factor VIII activity in non-human primates.

    Published in:
    Nature Communications, 2022, v. 13, n. 1, p. 1, doi. 10.1038/s41467-022-30102-3
    By:
    • Milani, Michela;
    • Canepari, Cesare;
    • Liu, Tongyao;
    • Biffi, Mauro;
    • Russo, Fabio;
    • Plati, Tiziana;
    • Curto, Rosalia;
    • Patarroyo-White, Susannah;
    • Drager, Douglas;
    • Visigalli, Ilaria;
    • Brombin, Chiara;
    • Albertini, Paola;
    • Follenzi, Antonia;
    • Ayuso, Eduard;
    • Mueller, Christian;
    • Annoni, Andrea;
    • Naldini, Luigi;
    • Cantore, Alessio
    Publication type:
    Article
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    Unbiased assessment of genome integrity and purging of adverse outcomes at the target locus upon editing of CD4<sup>+</sup> T‐cells for the treatment of Hyper IgM1.

    Published in:
    EMBO Journal, 2023, v. 42, n. 23, p. 1, doi. 10.15252/embj.2023114188
    By:
    • Canarutto, Daniele;
    • Asperti, Claudia;
    • Vavassori, Valentina;
    • Porcellini, Simona;
    • Rovelli, Elisabetta;
    • Paulis, Marianna;
    • Ferrari, Samuele;
    • Varesi, Angelica;
    • Fiumara, Martina;
    • Jacob, Aurelien;
    • Sergi Sergi, Lucia;
    • Visigalli, Ilaria;
    • Ferrua, Francesca;
    • González‐Granado, Luis Ignacio;
    • Lougaris, Vassilios;
    • Finocchi, Andrea;
    • Villa, Anna;
    • Radrizzani, Marina;
    • Naldini, Luigi
    Publication type:
    Article
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    Gene Modification and Three‐Dimensional Scaffolds as Novel Tools to Allow the Use of Postnatal Thymic Epithelial Cells for Thymus Regeneration Approaches.

    Published in:
    Stem Cells Translational Medicine, 2019, v. 8, n. 10, p. 1107, doi. 10.1002/sctm.18-0218
    By:
    • Bortolomai, Ileana;
    • Sandri, Monica;
    • Draghici, Elena;
    • Fontana, Elena;
    • Campodoni, Elisabetta;
    • Marcovecchio, Genni Enza;
    • Ferrua, Francesca;
    • Perani, Laura;
    • Spinelli, Antonello;
    • Canu, Tamara;
    • Catucci, Marco;
    • Di Tomaso, Tiziano;
    • Sergi Sergi, Lucia;
    • Esposito, Antonio;
    • Lombardo, Angelo;
    • Naldini, Luigi;
    • Tampieri, Anna;
    • Hollander, Georg A.;
    • Villa, Anna;
    • Bosticardo, Marita
    Publication type:
    Article
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    Constitutive IL-1RA production by modified immune cells protects against IL-1–mediated inflammatory disorders.

    Published in:
    Science Translational Medicine, 2023, v. 15, n. 698, p. 1, doi. 10.1126/scitranslmed.ade3856
    By:
    • Colantuoni, Mariasilvia;
    • Jofra Hernandez, Raisa;
    • Pettinato, Emanuela;
    • Basso-Ricci, Luca;
    • Magnani, Laura;
    • Andolfi, Grazia;
    • Rigamonti, Chiara;
    • Finardi, Annamaria;
    • Romeo, Valentina;
    • Soldi, Monica;
    • Sergi Sergi, Lucia;
    • Rocchi, Martina;
    • Scala, Serena;
    • Hoffman, Hal M.;
    • Gregori, Silvia;
    • Kajaste-Rudnitski, Anna;
    • Sanvito, Francesca;
    • Muzio, Luca;
    • Naldini, Luigi;
    • Aiuti, Alessandro
    Publication type:
    Article
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    Targeted inducible delivery of immunoactivating cytokines reprograms glioblastoma microenvironment and inhibits growth in mouse models.

    Published in:
    Science Translational Medicine, 2022, v. 14, n. 653, p. 1, doi. 10.1126/scitranslmed.abl4106
    By:
    • Birocchi, Filippo;
    • Cusimano, Melania;
    • Rossari, Federico;
    • Beretta, Stefano;
    • Rancoita, Paola M. V.;
    • Ranghetti, Anna;
    • Colombo, Stefano;
    • Costa, Barbara;
    • Angel, Peter;
    • Sanvito, Francesca;
    • Callea, Marcella;
    • Norata, Rossana;
    • Chaabane, Linda;
    • Canu, Tamara;
    • Spinelli, Antonello;
    • Genua, Marco;
    • Ostuni, Renato;
    • Merelli, Ivan;
    • Coltella, Nadia;
    • Naldini, Luigi
    Publication type:
    Article
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    A Set of Cell Lines Derived from a Genetic Murine Glioblastoma Model Recapitulates Molecular and Morphological Characteristics of Human Tumors.

    Published in:
    Cancers, 2021, v. 13, n. 2, p. 230, doi. 10.3390/cancers13020230
    By:
    • Costa, Barbara;
    • Fletcher, Michael N. C.;
    • Boskovic, Pavle;
    • Ivanova, Ekaterina L.;
    • Eisemann, Tanja;
    • Lohr, Sabrina;
    • Bunse, Lukas;
    • Löwer, Martin;
    • Burchard, Stefanie;
    • Korshunov, Andrey;
    • Coltella, Nadia;
    • Cusimano, Melania;
    • Naldini, Luigi;
    • Liu, Hai-Kun;
    • Platten, Michael;
    • Radlwimmer, Bernhard;
    • Angel, Peter;
    • Peterziel, Heike
    Publication type:
    Article
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    Dual-regulated Lentiviral Vector for Gene Therapy of X-linked Chronic Granulomatosis.

    Published in:
    Molecular Therapy, 2014, v. 22, n. 8, p. 1472, doi. 10.1038/mt.2014.87
    By:
    • Chiriaco, Maria;
    • Farinelli, Giada;
    • Capo, Valentina;
    • Zonari, Erika;
    • Scaramuzza, Samantha;
    • Di Matteo, Gigliola;
    • Sergi, Lucia Sergi;
    • Migliavacca, Maddalena;
    • Hernandez, Raisa Jofra;
    • Bombelli, Ferdinando;
    • Giorda, Ezio;
    • Kajaste-Rudnitski, Anna;
    • Trono, Didier;
    • Grez, Manuel;
    • Rossi, Paolo;
    • Finocchi, Andrea;
    • Naldini, Luigi;
    • Gentner, Bernhard;
    • Aiuti, Alessandro
    Publication type:
    Article
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    Charting a Clear Path: The ASGCT Standardized Pathways Conference.

    Published in:
    Molecular Therapy, 2014, v. 22, n. 7, p. 1235, doi. 10.1038/mt.2014.95
    By:
    • Kiem, Hans-Peter;
    • Baum, Christopher;
    • Bushman, Frederic D;
    • Byrne, Barry J;
    • Carter, Barrie J;
    • Cavagnaro, Joy;
    • Malech, Harry L;
    • Mendell, Jerry R;
    • Naldini, Luigi M;
    • Sorrentino, Brian P;
    • Williams, David A;
    • Flotte, Terence R
    Publication type:
    Article
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    Uncovering and Dissecting the Genotoxicity of Self-inactivating Lentiviral Vectors In Vivo.

    Published in:
    Molecular Therapy, 2014, v. 22, n. 4, p. 774, doi. 10.1038/mt.2014.3
    By:
    • Cesana, Daniela;
    • Ranzani, Marco;
    • Volpin, Monica;
    • Bartholomae, Cynthia;
    • Duros, Caroline;
    • Artus, Alexandre;
    • Merella, Stefania;
    • Benedicenti, Fabrizio;
    • Sergi Sergi, Lucia;
    • Sanvito, Francesca;
    • Brombin, Chiara;
    • Nonis, Alessandro;
    • Serio, Clelia Di;
    • Doglioni, Claudio;
    • von Kalle, Christof;
    • Schmidt, Manfred;
    • Cohen-Haguenauer, Odile;
    • Naldini, Luigi;
    • Montini, Eugenio
    Publication type:
    Article
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