Works matching IS 15250016 AND DT 2013 AND VI 21 AND IP 10

Results: 23

TALENs Targeting HBV: Designer Endonuclease Therapies for Viral Infections.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1819, doi. 10.1038/mt.2013.208

By:

Weber, Nicholas D;
Stone, Daniel;
Jerome, Keith R

Publication type:

Article

Adeno-associated Virus 9 Mediated FKRP Gene Therapy Restores Functional Glycosylation of α-dystroglycan and Improves Muscle Functions.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1832, doi. 10.1038/mt.2013.156

By:

Xu, Lei;
Lu, Pei Juan;
Wang, Chi-Hsien;
Keramaris, Elizabeth;
Qiao, Chunping;
Xiao, Bin;
Blake, Derek J;
Xiao, Xiao;
Lu, Qi Long

Publication type:

Article

NADH-dehydrogenase Type-2 Suppresses Irreversible Visual Loss and Neurodegeneration in the EAE Animal Model of MS.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1876, doi. 10.1038/mt.2013.104

By:

Talla, Venu;
Yu, Hong;
Chou, Tsung-Han;
Porciatti, Vittorio;
Chiodo, Vince;
Boye, Sanford L;
Hauswirth, William W;
Lewin, Alfred S;
Guy, John

Publication type:

Article

Sonia Skarlatos: A Colleague and a Shepherd of Gene Therapy.

Published in:: Molecular Therapy, 2013, v. 21, n. 10, p. 1807, doi. 10.1038/mt.2013.202
Publication type:: Article

Inactivation of Hepatitis B Virus Replication in Cultured Cells and In Vivo with Engineered Transcription Activator-Like Effector Nucleases.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1889, doi. 10.1038/mt.2013.170

By:

Bloom, Kristie;
Ely, Abdullah;
Mussolino, Claudio;
Cathomen, Toni;
Arbuthnot, Patrick

Publication type:

Article

Silencing Mutant ATXN3 Expression Resolves Molecular Phenotypes in SCA3 Transgenic Mice.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1909, doi. 10.1038/mt.2013.152

By:

Rodríguez-Lebrón, Edgardo;
Costa, Maria doCarmo;
Luna-Cancalon, Katiuska;
Peron, Therese M;
Fischer, Svetlana;
Boudreau, Ryan L;
Davidson, Beverly L;
Paulson, Henry L

Publication type:

Article

Removing the Immune Response From Muscular Dystrophy Research.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1821, doi. 10.1038/mt.2013.209

By:

Chamberlain, Jeffrey S

Publication type:

Article

DLK1: A Novel Target for Immunotherapeutic Remodeling of the Tumor Blood Vasculature.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1958, doi. 10.1038/mt.2013.133

By:

Chi Sabins, Nina;
Taylor, Jennifer L;
Fabian, Kellsye PL;
Appleman, Leonard J;
Maranchie, Jodi K;
Stolz, Donna Beer;
Storkus, Walter J

Publication type:

Article

Intravenous Delivery of siRNA Targeting CD47 Effectively Inhibits Melanoma Tumor Growth and Lung Metastasis.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1919, doi. 10.1038/mt.2013.135

By:

Wang, Yuhua;
Xu, Zhenghong;
Guo, Shutao;
Zhang, Lu;
Sharma, Arati;
Robertson, Gavin P;
Huang, Leaf

Publication type:

Article

Toward RNAi Therapy for the Polyglutamine Disease Machado-Joseph Disease.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1898, doi. 10.1038/mt.2013.144

By:

do Carmo Costa, Maria;
Luna-Cancalon, Katiuska;
Fischer, Svetlana;
Ashraf, Naila S;
Ouyang, Michelle;
Dharia, Rahil M;
Martin-Fishman, Lucas;
Yang, Yemen;
Shakkottai, Vikram G;
Davidson, Beverly L;
Rodríguez-Lebrón, Edgardo;
Paulson, Henry L

Publication type:

Article

Panorama From the Oncolytic Virotherapy Summit.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1814, doi. 10.1038/mt.2013.207

By:

Pol, Jonathan G;
Marguerie, Monique;
Arulanandam, Rozanne;
Bell, John C;
Lichty, Brian D

Publication type:

Article

Hydrodynamic Delivery of mIL10 Gene Protects Mice From High-fat Diet-induced Obesity and Glucose Intolerance.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1852, doi. 10.1038/mt.2013.125

By:

Gao, Mingming;
Zhang, Chunbo;
Ma, Yongjie;
Bu, Le;
Yan, Linna;
Liu, Dexi

Publication type:

Article

Amalgamating Oncolytic Viruses to Enhance Their Safety, Consolidate Their Killing Mechanisms, and Accelerate Their Spread.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1930, doi. 10.1038/mt.2013.164

By:

Ayala-Breton, Camilo;
Suksanpaisan, Lukkana;
Mader, Emily K;
Russell, Stephen J;
Peng, Kah-Whye

Publication type:

Article

Research Highlights.

Published in:: Molecular Therapy, 2013, v. 21, n. 10, p. 1809, doi. 10.1038/mt.2013.204
Publication type:: Article

On the Mechanism and Benefit of siRNA-mediated Targeting of CD47 in Cancer.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1811, doi. 10.1038/mt.2013.205

By:

Zhao, Xiwen;
Matlung, Hanke;
Kuijpers, Taco W;
van den Berg, Timo K

Publication type:

Article

Transcriptional Profiling of Hmgb1-Induced Myocardial Repair Identifies a Key Role for Notch Signaling.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1841, doi. 10.1038/mt.2013.137

By:

Limana, Federica;
Esposito, Grazia;
Fasanaro, Pasquale;
Foglio, Eleonora;
Arcelli, Diego;
Voellenkle, Christine;
Di Carlo, Anna;
Avitabile, Daniele;
Martelli, Fabio;
Antonio Russo, Matteo;
Pompilio, Giulio;
Germani, Antonia;
C Capogrossi, Maurizio

Publication type:

Article

Corrigendum to 'Topical Application of Recombinant Type VII Collagen Incorporates Into the Dermal-Epidermal Junction and Promotes Wound Closure'.

Published in:: Molecular Therapy, 2013, v. 21, n. 10, p. 1969, doi. 10.1038/mt.2013.213
Publication type:: Article

Myeloid/Microglial Driven Autologous Hematopoietic Stem Cell Gene Therapy Corrects a Neuronopathic Lysosomal Disease.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1938, doi. 10.1038/mt.2013.141

By:

Sergijenko, Ana;
Langford-Smith, Alexander;
Liao, Ai Y;
Pickford, Claire E;
McDermott, John;
Nowinski, Gabriel;
Langford-Smith, Kia J;
Merry, Catherine LR;
Jones, Simon A;
Wraith, J Edmond;
Wynn, Robert F;
Wilkinson, Fiona L;
Bigger, Brian W

Publication type:

Article

Dose-dependent Neuroprotection of VEGF165 in Huntington's Disease Striatum.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1862, doi. 10.1038/mt.2013.132

By:

Ellison, Stuart M;
Trabalza, Antonio;
Tisato, Veronica;
Pazarentzos, Evangelos;
Lee, Shirley;
Papadaki, Vasiliki;
Goniotaki, Despoina;
Morgan, Sarah;
Mirzaei, Nazanin;
Mazarakis, Nicholas D

Publication type:

Article

Adeno-associated Virus-mediated Rescue of Neonatal Lethality in Argininosuccinate Synthetase-deficient Mice.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1823, doi. 10.1038/mt.2013.139

By:

Kok, Cindy Y;
Cunningham, Sharon C;
Carpenter, Kevin H;
Dane, Allison P;
Siew, Susan M;
Logan, Grant J;
Kuchel, Philip W;
Alexander, Ian E

Publication type:

Article

In This Issue.

Published in:: Molecular Therapy, 2013, v. 21, n. 10, p. 1808, doi. 10.1038/mt.2013.203
Publication type:: Article

The Rag2-Il2rb-Dmd- Mouse: a Novel Dystrophic and Immunodeficient Model to Assess Innovating Therapeutic Strategies for Muscular Dystrophies.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1950, doi. 10.1038/mt.2013.186

By:

Vallese, Denis;
Negroni, Elisa;
Duguez, Stéphanie;
Ferry, Arnaud;
Trollet, Capucine;
Aamiri, Ahmed;
Vosshenrich, Christian AJ;
Füchtbauer, Ernst-Martin;
Di Santo, James P;
Vitiello, Libero;
Butler-Browne, Gillian;
Mouly, Vincent

Publication type:

Article

Reply to 'On the Mechanism and Benefit of siRNA-mediated Targeting of CD47 in Cancer'.

Published in:

Molecular Therapy, 2013, v. 21, n. 10, p. 1812, doi. 10.1038/mt.2013.206

By:

Wang, Yuhua;
Xu, Zhenghong;
Huang, Leaf

Publication type:

Article

Works matching IS 15250016 AND DT 2013 AND VI 21 AND IP 10

TALENs Targeting HBV: Designer Endonuclease Therapies for Viral Infections.

Adeno-associated Virus 9 Mediated FKRP Gene Therapy Restores Functional Glycosylation of α-dystroglycan and Improves Muscle Functions.

NADH-dehydrogenase Type-2 Suppresses Irreversible Visual Loss and Neurodegeneration in the EAE Animal Model of MS.

Sonia Skarlatos: A Colleague and a Shepherd of Gene Therapy.

Inactivation of Hepatitis B Virus Replication in Cultured Cells and In Vivo with Engineered Transcription Activator-Like Effector Nucleases.

Silencing Mutant ATXN3 Expression Resolves Molecular Phenotypes in SCA3 Transgenic Mice.

Removing the Immune Response From Muscular Dystrophy Research.

DLK1: A Novel Target for Immunotherapeutic Remodeling of the Tumor Blood Vasculature.

Intravenous Delivery of siRNA Targeting CD47 Effectively Inhibits Melanoma Tumor Growth and Lung Metastasis.

Toward RNAi Therapy for the Polyglutamine Disease Machado-Joseph Disease.

Panorama From the Oncolytic Virotherapy Summit.

Hydrodynamic Delivery of mIL10 Gene Protects Mice From High-fat Diet-induced Obesity and Glucose Intolerance.

Amalgamating Oncolytic Viruses to Enhance Their Safety, Consolidate Their Killing Mechanisms, and Accelerate Their Spread.

Research Highlights.

On the Mechanism and Benefit of siRNA-mediated Targeting of CD47 in Cancer.

Transcriptional Profiling of Hmgb1-Induced Myocardial Repair Identifies a Key Role for Notch Signaling.

Corrigendum to 'Topical Application of Recombinant Type VII Collagen Incorporates Into the Dermal-Epidermal Junction and Promotes Wound Closure'.

Myeloid/Microglial Driven Autologous Hematopoietic Stem Cell Gene Therapy Corrects a Neuronopathic Lysosomal Disease.

Dose-dependent Neuroprotection of VEGF<sub>165</sub> in Huntington's Disease Striatum.

Adeno-associated Virus-mediated Rescue of Neonatal Lethality in Argininosuccinate Synthetase-deficient Mice.

In This Issue.

The Rag2<sup>-</sup>Il2rb<sup>-</sup>Dmd<sup>-</sup> Mouse: a Novel Dystrophic and Immunodeficient Model to Assess Innovating Therapeutic Strategies for Muscular Dystrophies.

Reply to 'On the Mechanism and Benefit of siRNA-mediated Targeting of CD47 in Cancer'.