Works matching IS 15250016 AND DT 2011 AND VI 19 AND IP 2
Results: 30
Sustained Enzymatic Correction by rAAV-Mediated Liver Gene Therapy Protects Against Induced Motor Neuropathy in Acute Porphyria Mice.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 2, p. 243, doi. 10.1038/mt.2010.210
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- Publication type:
- Article
The FGF-2-Derived Peptide FREG Inhibits Melanoma Growth In Vitro and In Vivo.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 266, doi. 10.1038/mt.2010.211
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- Publication type:
- Article
Neuroprotection by Gene Therapy Targeting Mutant SOD1 in Individual Pools of Motor Neurons Does not Translate Into Therapeutic Benefit in fALS Mice.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 274, doi. 10.1038/mt.2010.260
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- Publication type:
- Article
AAV6-Mediated Gene Silencing fALS Short.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 231, doi. 10.1038/mt.2010.306
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- Publication type:
- Article
Lentiviral Vector Platform for Production of Bioengineered Recombinant Coagulation Factor VIII.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 302, doi. 10.1038/mt.2010.239
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- Publication type:
- Article
Ex-vivo Gene Therapy Restores LEKTI Activity and Corrects the Architecture of Netherton Syndrome-derived Skin Grafts.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 408, doi. 10.1038/mt.2010.201
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- Publication type:
- Article
CNS-targeted Viral Delivery of G-CSF in an Animal Model for ALS: Improved Efficacy and Preservation of the Neuromuscular Unit.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 284, doi. 10.1038/mt.2010.271
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- Publication type:
- Article
Is Human Cell Therapy Research Caught in a Mousetrap?
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- Molecular Therapy, 2011, v. 19, n. 2, p. 224, doi. 10.1038/mt.2010.304
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- Publication type:
- Article
Elimination Pathways of Systemically Delivered siRNA.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 381, doi. 10.1038/mt.2010.266
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- Publication type:
- Article
Inhibition of Choroidal Neovascularization in a Nonhuman Primate Model by Intravitreal Administration of an AAV2 Vector Expressing a Novel Anti-VEGF Molecule.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 260, doi. 10.1038/mt.2010.230
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- Publication type:
- Article
Surface Characteristics of Nanoparticles Determine Their Intracellular Fate in and Processing by Human Blood-Brain Barrier Endothelial Cells In Vitro.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 318, doi. 10.1038/mt.2010.236
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- Publication type:
- Article
Microvesicle-mediated RNA Molecule Delivery System Using Monocytes/Macrophages.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 395, doi. 10.1038/mt.2010.254
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- Publication type:
- Article
Efficient Generation of Hepatoblasts From Human ES Cells and iPS Cells by Transient Overexpression of Homeobox Gene HEX.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 400, doi. 10.1038/mt.2010.241
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- Publication type:
- Article
Application of Phi29 Motor pRNA for Targeted Therapeutic Delivery of siRNA Silencing Metallothionein-IIA and Survivin in Ovarian Cancers.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 386, doi. 10.1038/mt.2010.243
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- Publication type:
- Article
Direct Conversion of Skin Cells into Blood: Alchemy or Science?
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- Molecular Therapy, 2011, v. 19, n. 2, p. 227, doi. 10.1038/mt.2010.291
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- Publication type:
- Article
Vaccine-induced T cells Provide Partial Protection Against High-dose Rectal SIVmac239 Challenge of Rhesus Macaques.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 417, doi. 10.1038/mt.2010.238
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- Publication type:
- Article
Preclinical Safety Evaluation of AAV2-sFLT01- A Gene Therapy for Age-related Macular Degeneration.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 326, doi. 10.1038/mt.2010.258
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- Publication type:
- Article
MITF-siRNA Formulation Is a Safe and Effective Therapy for Human Melasma.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 362, doi. 10.1038/mt.2010.263
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- Publication type:
- Article
Antifibrotic Effect of MMP13-encoding Plasmid DNA Delivered Using Polyethylenimine Shielded With Hyaluronic Acid.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 2, p. 355, doi. 10.1038/mt.2010.262
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- Publication type:
- Article
Gene Therapy Moves Forward in 2010.
- Published in:
- 2011
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- Publication type:
- Conference Paper/Materials
Safe, Efficient, and Reproducible Gene Therapy of the Brain in the Dog Models of Sanfilippo and Hurler Syndromes.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 2, p. 251, doi. 10.1038/mt.2010.265
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- Publication type:
- Article
Poly(oligo-D-arginine) With Internal Disulfide Linkages as a Cytoplasm-sensitive Carrier for siRNA Delivery.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 372, doi. 10.1038/mt.2010.242
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- Publication type:
- Article
In This Issue.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 2, p. 222, doi. 10.1038/mt.2010.309
- Publication type:
- Article
Long-term Retinal Function and Structure Rescue Using Capsid Mutant AAV8 Vector in the rd10 Mouse, a Model of Recessive Retinitis Pigmentosa.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 2, p. 234, doi. 10.1038/mt.2010.273
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- Publication type:
- Article
Research Highlights.
- Published in:
- 2011
- Publication type:
- Abstract
Adaptive Antiviral Immunity Is a Determinant of the Therapeutic Success of Oncolytic Virotherapy.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 2, p. 335, doi. 10.1038/mt.2010.264
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- Publication type:
- Article
Solving the Problem of γ-Retroviral Vectors Containing Long Terminal Repeats.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 229, doi. 10.1038/mt.2010.305
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- Publication type:
- Article
Chronic Systemic Therapy With Low-dose Morpholino Oligomers Ameliorates the Pathology and Normalizes Locomotor Behavior in mdx Mice.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 345, doi. 10.1038/mt.2010.261
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- Publication type:
- Article
Novel Properties of Tyrosine-mutant AAV2 Vectors in the Mouse Retina.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 2, p. 293, doi. 10.1038/mt.2010.234
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- Publication type:
- Article
Prevention of Diabetic Neuropathy by Regulatable Expression of HSV-Mediated Erythropoietin.
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- Molecular Therapy, 2011, v. 19, n. 2, p. 310, doi. 10.1038/mt.2010.215
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- Publication type:
- Article