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Diabetes drugs activate neuroprotective pathways in models of neonatal hypoxic-ischemic encephalopathy.
- Published in:
- EMBO Molecular Medicine, 2024, v. 16, n. 6, p. 1284, doi. 10.1038/s44321-024-00079-1
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- Publication type:
- Article
Gene therapy for global brain diseases: one small step for mice, one giant leap for humans.
- Published in:
- 2020
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- Publication type:
- journal article
Neuroprotective exendin-4 enhances hypothermia therapy in a model of hypoxic-ischaemic encephalopathy.
- Published in:
- 2018
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- Publication type:
- journal article
Delineating pathological pathways in a chemically induced mouse model of Gaucher disease.
- Published in:
- Journal of Pathology, 2016, v. 239, n. 4, p. 496, doi. 10.1002/path.4751
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- Publication type:
- Article
Clinical and Molecular Features of Early Infantile Niemann Pick Type C Disease.
- Published in:
- International Journal of Molecular Sciences, 2020, v. 21, n. 14, p. 5059, doi. 10.3390/ijms21145059
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- Publication type:
- Article
Inhibition of Mitochondrial Complex I Impairs Release of α-Galactosidase by Jurkat Cells.
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- International Journal of Molecular Sciences, 2019, v. 20, n. 18, p. 4349, doi. 10.3390/ijms20184349
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- Publication type:
- Article
Evidence for Contribution of CD4+CD25+ Regulatory T Cells in Maintaining Immune Tolerance to Human Factor IX following Perinatal Adenovirus Vector Delivery.
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- Journal of Immunology Research, 2015, v. 2015, p. 1, doi. 10.1155/2015/397879
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- Publication type:
- Article
Evidence for contribution of CD4+ CD25+ regulatory T cells in maintaining immune tolerance to human factor IX following perinatal adenovirus vector delivery.
- Published in:
- 2015
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- Publication type:
- journal article
New possibilities for neuroprotection in neonatal hypoxic-ischemic encephalopathy.
- Published in:
- European Journal of Pediatrics, 2022, v. 181, n. 3, p. 875, doi. 10.1007/s00431-021-04320-8
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- Publication type:
- Article
Immediate Remote Ischemic Postconditioning Reduces Brain Nitrotyrosine Formation in a Piglet Asphyxia Model.
- Published in:
- Oxidative Medicine & Cellular Longevity, 2016, p. 1, doi. 10.1155/2016/5763743
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- Publication type:
- Article
Gene Therapy for Lysosomal Storage Disorders: Ongoing Studies and Clinical Development.
- Published in:
- Biomolecules (2218-273X), 2021, v. 11, n. 4, p. 611, doi. 10.3390/biom11040611
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- Publication type:
- Article
Generation of light-producing somatic-transgenic mice using adeno-associated virus vectors.
- Published in:
- Scientific Reports, 2020, v. 10, n. 1, p. 1, doi. 10.1038/s41598-020-59075-3
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- Publication type:
- Article
Systemic gene delivery following intravenous administration of AAV9 to fetal and neonatal mice and late-gestation nonhuman primates.
- Published in:
- FASEB Journal, 2015, v. 29, n. 9, p. 3876, doi. 10.1096/fj.14-269092
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- Publication type:
- Article
Intravenous administration of AAV2/9 to the fetal and neonatal mouse leads to differential targeting of CNS cell types and extensive transduction of the nervous system.
- Published in:
- FASEB Journal, 2011, v. 25, n. 10, p. 3505, doi. 10.1096/fj.11-182311
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- Publication type:
- Article
Comparison of different promoters to improve AAV vector-mediated gene therapy for neuronopathic Gaucher disease.
- Published in:
- Human Molecular Genetics, 2024, v. 33, n. 17, p. 1467, doi. 10.1093/hmg/ddae081
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- Publication type:
- Article
Fetal gene therapy.
- Published in:
- Journal of Inherited Metabolic Disease, 2024, v. 47, n. 1, p. 192, doi. 10.1002/jimd.12659
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- Publication type:
- Article
Erratum to: Increased glucocerebrosidase (GBA) 2 activity in GBA1 deficient mice brains and in Gaucher leucocytes.
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- 2013
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- Publication type:
- Correction Notice
Increased glucocerebrosidase (GBA) 2 activity in GBA1 deficient mice brains and in Gaucher leucocytes.
- Published in:
- Journal of Inherited Metabolic Disease, 2013, v. 36, n. 5, p. 869, doi. 10.1007/s10545-012-9561-3
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- Publication type:
- Article
Systemic AAV9 gene therapy using the synapsin I promoter rescues a mouse model of neuronopathic Gaucher disease but with limited cross-correction potential to astrocytes.
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- Human Molecular Genetics, 2020, v. 29, n. 12, p. 1933, doi. 10.1093/hmg/ddz317
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- Publication type:
- Article
Neonatal brain-directed gene therapy rescues a mouse model of neurodegenerative CLN6 Batten disease.
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- Human Molecular Genetics, 2019, v. 28, n. 23, p. 3867, doi. 10.1093/hmg/ddz210
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- Publication type:
- Article
Targeted retroviral gene delivery using ultrasound.
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- Journal of Gene Medicine, 2007, v. 9, n. 2, p. 77, doi. 10.1002/jgm.1003
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- Publication type:
- Article
Spatial and acoustic pressure dependence of microbubble-mediated gene delivery targeted using focused ultrasound.
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- Journal of Gene Medicine, 2006, v. 8, n. 11, p. 1347, doi. 10.1002/jgm.962
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- Publication type:
- Article
Influence of Coagulation Factor X on In Vitro and In Vivo Gene Delivery by Adenovirus (Ad) 5, Ad35, and Chimeric Ad5/Ad35 Vectors.
- Published in:
- Molecular Therapy, 2009, v. 17, n. 10, p. 1683, doi. 10.1038/mt.2009.152
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- Publication type:
- Article
546. Targeted Non-Viral Gene Delivery Using Microbubbles and Focused Ultrasound.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S210, doi. 10.1016/j.ymthe.2006.08.618
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- Publication type:
- Article
Corrigendum to “Oncogenesis Following Delivery of a Nonprimate Lentiviral Gene Therapy Vector to Fetal and Neonatal Mice”.
- Published in:
- Molecular Therapy, 2006, v. 13, n. 4, p. 830, doi. 10.1016/j.ymthe.2005.10.003
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- Publication type:
- Article
Oncogenesis Following Delivery of a Nonprimate Lentiviral Gene Therapy Vector to Fetal and Neonatal Mice
- Published in:
- Molecular Therapy, 2005, v. 12, n. 4, p. 763, doi. 10.1016/j.ymthe.2005.07.358
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- Publication type:
- Article
484. Ultrasound-Mediated Microbubble Destruction and Retroviral Gene Delivery
- Published in:
- 2005
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- Publication type:
- Abstract
209. Nuclear Localization Mediated by the Adenoviral-Core Peptide Mu Enhances Phage φC31-Integrase Activity in Mammalian Cells
- Published in:
- 2005
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- Publication type:
- Abstract
In vivo bioimaging with tissue-specific transcription factor activated luciferase reporters.
- Published in:
- Scientific Reports, 2015, p. 11842, doi. 10.1038/srep11842
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- Publication type:
- Article
A Novel Small NPC1 Promoter Enhances AAV-Mediated Gene Therapy in Mouse Models of Niemann–Pick Type C1 Disease.
- Published in:
- Cells (2073-4409), 2023, v. 12, n. 12, p. 1619, doi. 10.3390/cells12121619
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- Publication type:
- Article
Argininosuccinic aciduria fosters neuronal nitrosative stress reversed by Asl gene transfer.
- Published in:
- Nature Communications, 2018, v. 9, n. 1, p. 1, doi. 10.1038/s41467-018-05972-1
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- Publication type:
- Article
Using Stem Cells to Grow Artificial Tissue for Peripheral Nerve Repair.
- Published in:
- Stem Cells International, 2016, p. 1, doi. 10.1155/2016/7502178
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- Publication type:
- Article
Epilepsy Gene Therapy Using an Engineered Potassium Channel.
- Published in:
- Journal of Neuroscience, 2019, v. 39, n. 16, p. 3159, doi. 10.1523/JNEUROSCI.1143-18.2019
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- Publication type:
- Article
Neuroprotective Effects of Diabetes Drugs for the Treatment of Neonatal Hypoxia-Ischemia Encephalopathy.
- Published in:
- Frontiers in Cellular Neuroscience, 2020, v. 14, p. 1, doi. 10.3389/fncel.2020.00112
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- Publication type:
- Article
Perinatal systemic gene delivery using adeno-associated viral vectors.
- Published in:
- Frontiers in Molecular Neuroscience, 2014, v. 7, p. 1, doi. 10.3389/fnmol.2014.00089
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- Publication type:
- Article
Nuclear Localisation Sequence Templated Nonviral Gene Delivery Vectors: Investigation of Intracellular Trafficking Events of LMD and LD Vector Systems ( LMD=liposome:mu peptide:DNA; LD=liposome:plasmid DNA).
- Published in:
- ChemBioChem, 2003, v. 4, n. 4, p. 286, doi. 10.1002/cbic.200390049
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- Publication type:
- Article