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Immunogenicity of Current and New Therapies for Hemophilia A.
- Published in:
- Pharmaceuticals (14248247), 2022, v. 15, n. 8, p. 911, doi. 10.3390/ph15080911
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- Publication type:
- Article
Key issues in inhibitor management in patients with haemophilia.
- Published in:
- Blood Transfusion (17232007), 2014, v. 12, p. s319, doi. 10.2450/2013.0246-12
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- Publication type:
- Article
Thalidomide for the treatment of gastrointestinal bleeding due to angiodysplasia in a patient with Glanzmann's thrombasthenia.
- Published in:
- Hematology Reports, 2017, v. 9, n. 2, p. 53, doi. 10.4081/hr.2017.6961
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- Publication type:
- Article
CORRIGENDUM: Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response.
- Published in:
- 2006
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- Publication type:
- Correction Notice
Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response.
- Published in:
- Nature Medicine, 2006, v. 12, n. 3, p. 342, doi. 10.1038/nm1358
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- Publication type:
- Article
Longitudinal sequencing of RUNX1 familial platelet disorder: new insights into genetic mechanisms of transformation to myeloid malignancies.
- Published in:
- British Journal of Haematology, 2019, v. 186, n. 5, p. 724, doi. 10.1111/bjh.15990
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- Publication type:
- Article
Long-acting recombinant factor IX Fc fusion protein ( rFIXFc) for perioperative management of subjects with haemophilia B in the phase 3 B-LONG study.
- Published in:
- British Journal of Haematology, 2015, v. 168, n. 1, p. 124, doi. 10.1111/bjh.13112
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- Publication type:
- Article
Switching to recombinant factor IX Fc fusion protein prophylaxis results in fewer infusions, decreased factor IX consumption and lower bleeding rates.
- Published in:
- British Journal of Haematology, 2015, v. 168, n. 1, p. 113, doi. 10.1111/bjh.13109
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- Publication type:
- Article
An inherited mutation leading to production of only the short isoform of GATA-1 is associated with impaired erythropoiesis.
- Published in:
- Nature Genetics, 2006, v. 38, n. 7, p. 807, doi. 10.1038/ng1825
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- Publication type:
- Article
Safety and efficacy of cryoprecipitate-poor plasma as a replacement fluid for therapeutic plasma exchange in thrombotic thrombocytopenic purpura: A single center retrospective evaluation.
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- Journal of Clinical Apheresis, 2014, v. 29, n. 6, p. 311, doi. 10.1002/jca.21336
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- Publication type:
- Article
Pharmacoeconomic studies of bypassing agents in mild-tomoderate bleeding episodes in patients with hemophilia and inhibitors: a critical appraisal.
- Published in:
- Journal of Coagulation Disorders, 2010, v. 2, n. 2, p. 93
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- Publication type:
- Article
Pharmacoeconomic studies of bypassing agents in mild-tomoderate bleeding episodes in patients with hemophilia and inhibitors: a critical appraisal.
- Published in:
- Journal of Coagulation Disorders, 2009, v. 1, n. 1, p. 93
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- Publication type:
- Article
Comparative transcriptomic analysis of circulating endothelial cells in sickle cell stroke.
- Published in:
- Annals of Hematology, 2024, v. 103, n. 4, p. 1167, doi. 10.1007/s00277-024-05655-6
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- Publication type:
- Article
Real-World Rates of Bleeding, Factor VIII Use, and Quality of Life in Individuals with Severe Haemophilia A Receiving Prophylaxis in a Prospective, Noninterventional Study.
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- Journal of Clinical Medicine, 2021, v. 10, n. 24, p. 5959, doi. 10.3390/jcm10245959
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- Publication type:
- Article
International consensus recommendations on the management of people with haemophilia B.
- Published in:
- Therapeutic Advances in Hematology, 2022, v. 13, p. 1, doi. 10.1177/20406207221085202
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- Publication type:
- Article
Updates from guardian<sup>™</sup>: a comprehensive registration programme.
- Published in:
- European Journal of Haematology, 2015, v. 95, p. 22, doi. 10.1111/ejh.12648
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- Publication type:
- Article
Impaired repair properties of endothelial colony‐forming cells in patients with granulomatosis with polyangiitis.
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- Journal of Cellular & Molecular Medicine, 2022, v. 26, n. 19, p. 5044, doi. 10.1111/jcmm.17531
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- Publication type:
- Article
Intermittent low platelet counts hampering diagnosis of X-linked thrombocytopenia in children: report of two unrelated cases and a novel mutation in the gene coding for the Wiskott-Aldrich syndrome protein.
- Published in:
- 2017
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- Publication type:
- journal article
Use of recombinant factor VIIa in the management of severe bleeding episodes in patients with Bernard–Soulier syndrome.
- Published in:
- Annals of Hematology, 2005, v. 84, n. 12, p. 816, doi. 10.1007/s00277-005-1080-y
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- Publication type:
- Article
Use of recombinant factor VIIa in the management of severe bleeding episodes in patients with Bernard-Soulier syndrome.
- Published in:
- 2005
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- Publication type:
- journal article
Knee radiosynovectomy with 153Sm-hydroxyapatite compared to 90Y-hydroxyapatite: initial results of a prospective trial.
- Published in:
- Annals of Nuclear Medicine, 2021, v. 35, n. 2, p. 232, doi. 10.1007/s12149-020-01557-5
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- Publication type:
- Article
Angiogenesis-Related Genes in Endothelial Progenitor Cells May Be Involved in Sickle Cell Stroke.
- Published in:
- 2020
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- Publication type:
- journal article
Correction to: Routine clinical care data for population pharmacokinetic modeling: the case for Fanhdi/Alphanate in hemophilia A patients.
- Published in:
- 2019
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- Publication type:
- Correction Notice
Routine clinical care data for population pharmacokinetic modeling: the case for Fanhdi/Alphanate in hemophilia A patients.
- Published in:
- Journal of Pharmacokinetics & Pharmacodynamics, 2019, v. 46, n. 5, p. 427, doi. 10.1007/s10928-019-09637-4
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- Publication type:
- Article
Genetic variability of platelet glycoprotein Ibα gene.
- Published in:
- American Journal of Hematology, 2004, v. 77, n. 2, p. 107, doi. 10.1002/ajh.20148
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- Publication type:
- Article
A MicroRNA-regulated and GP64-pseudotyped Lentiviral Vector Mediates Stable Expression of FVIII in a Murine Model of Hemophilia A.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 4, p. 723, doi. 10.1038/mt.2010.290
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- Publication type:
- Article
Evidence of Multiyear Factor IX Expression by AAV-Mediated Gene Transfer to Skeletal Muscle in an Individual with Severe Hemophilia B.
- Published in:
- Molecular Therapy, 2006, v. 14, n. 3, p. 452, doi. 10.1016/j.ymthe.2006.05.004
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- Publication type:
- Article
The molecular mechanism responsible for HbSC retinopathy may depend on the action of the angiogenesis-related genes ROBO1 and SLC38A5.
- Published in:
- Experimental Biology & Medicine, 2024, p. 1, doi. 10.3389/ebm.2024.10070
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- Publication type:
- Article
Comparative transcriptome analysis of endothelial progenitor cells of HbSS patients with and without proliferative retinopathy.
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- Experimental Biology & Medicine, 2023, v. 248, n. 8, p. 677, doi. 10.1177/15353702231157927
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- Publication type:
- Article
Gene therapy for hemophilia: looking beyond factor expression.
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- Experimental Biology & Medicine, 2022, v. 247, n. 24, p. 2223, doi. 10.1177/15353702221147565
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- Publication type:
- Article
Promoting pain coping skills in haemophilia: A remote intervention integrating exercise and pain education.
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- Haemophilia, 2024, v. 30, n. 3, p. 800, doi. 10.1111/hae.14991
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- Publication type:
- Article
Current and emerging gene therapies for haemophilia A and B.
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- Haemophilia, 2024, v. 30, p. 12, doi. 10.1111/hae.14984
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- Publication type:
- Article
Chronic pain in patients with hemophilia: Influence of kinesiophobia and catastrophizing thoughts.
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- Haemophilia, 2023, v. 29, n. 1, p. 386, doi. 10.1111/hae.14708
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- Publication type:
- Article
Haemophilia gene therapy—Update on new country initiatives.
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- Haemophilia, 2022, v. 28, p. 61, doi. 10.1111/hae.14512
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- Publication type:
- Article
Haemophilia gene therapy—Update on new country initiatives.
- Published in:
- Haemophilia, 2022, v. 28, p. 61, doi. 10.1111/hae.14512
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- Publication type:
- Article
Aquatic exercise in patients with haemophilia: Electromyographic and functional results from a prospective cohort study.
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- Haemophilia, 2021, v. 27, n. 2, p. e221, doi. 10.1111/hae.14275
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- Publication type:
- Article
Long‐term safety and sustained efficacy for up to 5 years of treatment with recombinant factor IX Fc fusion protein in subjects with haemophilia B: Results from the B‐YOND extension study.
- Published in:
- Haemophilia, 2020, v. 26, n. 6, p. e262, doi. 10.1111/hae.14036
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- Publication type:
- Article
An international survey to inform priorities for new guidelines on von Willebrand disease.
- Published in:
- Haemophilia, 2020, v. 26, n. 1, p. 106, doi. 10.1111/hae.13881
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- Publication type:
- Article
Haemophilia Experiences, Results and Opportunities (HERO study) in Brazil: Assessment of the psychosocial effects of haemophilia in patients and caregivers.
- Published in:
- Haemophilia, 2019, v. 25, n. 4, p. 640, doi. 10.1111/hae.13774
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- Publication type:
- Article
The 1st WFH Gene Therapy Round Table: Understanding the landscape and challenges of gene therapy for haemophilia around the world.
- Published in:
- Haemophilia, 2019, v. 25, n. 2, p. 189, doi. 10.1111/hae.13673
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- Publication type:
- Article
Long‐term safety and efficacy of turoctocog alfa in prophylaxis and treatment of bleeding episodes in severe haemophilia A: Final results from the guardian 2 extension trial.
- Published in:
- Haemophilia, 2018, v. 24, n. 6, p. e391, doi. 10.1111/hae.13617
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- Publication type:
- Article
Haemophilia care in Latin America: Assessment and perspectives.
- Published in:
- Haemophilia, 2018, v. 24, n. 6, p. e395, doi. 10.1111/hae.13607
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- Publication type:
- Article
Evaluation of the utility of the ISTH- BAT in haemophilia carriers: a multinational study.
- Published in:
- Haemophilia, 2016, v. 22, n. 6, p. 912, doi. 10.1111/hae.13089
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- Publication type:
- Article
Meeting the challenges of haemophilia care and patient support in China and Brazil.
- Published in:
- Haemophilia, 2012, v. 18, p. 33, doi. 10.1111/j.1365-2516.2012.02890.x
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- Publication type:
- Article
Cost of hemophilia A in Brazil: a microcosting study.
- Published in:
- Health Economics Review, 2024, v. 14, n. 1, p. 1, doi. 10.1186/s13561-024-00539-x
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- Publication type:
- Article
The translational gap for gene therapies in low- and middle-income countries.
- Published in:
- Science Translational Medicine, 2024, v. 16, n. 746, p. 1, doi. 10.1126/scitranslmed.adn1902
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- Publication type:
- Article
Possible Association between Cytomegalovirus Infection and Gastrointestinal Bleeding in Hemophiliac Patients.
- Published in:
- Acta Haematologica, 2000, v. 103, n. 2, p. 73, doi. 10.1159/000041023
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- Publication type:
- Article
Comparative Effectiveness of Valoctocogene Roxaparvovec and Prophylactic Factor VIII Replacement in Severe Hemophilia A.
- Published in:
- Advances in Therapy, 2024, v. 41, n. 6, p. 2267, doi. 10.1007/s12325-024-02834-9
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- Publication type:
- Article
Systematic Analysis of Bleeding Phenotype in PT-VWD Compared to Type 2B VWD Using an Electronic Bleeding Questionnaire.
- Published in:
- Clinical & Applied Thrombosis/Hemostasis, 2014, v. 20, n. 8, p. 765, doi. 10.1177/1076029614543825
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- Publication type:
- Article