Found: 6
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Understanding the life experience of Barth syndrome from the perspective of adults: a qualitative one-on-one interview study.
- Published in:
- 2019
- By:
- Publication type:
- journal article
Pozelimab for CHAPLE disease: results from in-trial interviews and clinical outcome assessments.
- Published in:
- Orphanet Journal of Rare Diseases, 2024, v. 19, n. 1, p. 1, doi. 10.1186/s13023-024-03277-9
- By:
- Publication type:
- Article
Development and content validity of the Barth Syndrome Symptom Assessment (BTHS-SA) for adolescents and adults.
- Published in:
- 2021
- By:
- Publication type:
- journal article
Psychometric performance of the Primary Mitochondrial Myopathy Symptom Assessment (PMMSA) in a randomized, double-blind, placebo-controlled crossover study in subjects with mitochondrial disease.
- Published in:
- Journal of Patient-Reported Outcomes, 2022, v. 6, n. 1, p. 1, doi. 10.1186/s41687-022-00534-y
- By:
- Publication type:
- Article
Content Validity and Psychometric Evaluation of the Functional Assessment of Chronic Illness Therapy–Fatigue (FACIT–Fatigue) in Patients with Crohn's Disease and Ulcerative Colitis.
- Published in:
- PharmacoEconomics - Open, 2023, v. 7, n. 5, p. 823, doi. 10.1007/s41669-023-00419-w
- By:
- Publication type:
- Article
Content Validity and Psychometric Evaluation of the Crohn's Symptom Severity (CSS) Questionnaire in Patients with Moderately to Severely Active Crohn's Disease.
- Published in:
- Advances in Therapy, 2024, v. 41, n. 9, p. 3678, doi. 10.1007/s12325-024-02923-9
- By:
- Publication type:
- Article