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Correction to: Hepatobiliary disease in XLMTM: a common comorbidity with potential impact on treatment strategies.
Published in:
2022
By:
- D'Amico, Adele;
- Longo, Antonella;
- Fattori, Fabiana;
- Tosi, Michele;
- Bosco, Luca;
- Testa, Maria Beatrice Chiarini;
- Paglietti, Maria Giovanna;
- Cherchi, Claudio;
- Carlesi, Adelina;
- Mizzoni, Irene;
- Bertini, Enrico
Publication type:
corrected article
Hepatobiliary disease in XLMTM: a common comorbidity with potential impact on treatment strategies.
Published in:
2021
By:
- D'Amico, Adele;
- Longo, Antonella;
- Fattori, Fabiana;
- Tosi, Michele;
- Bosco, Luca;
- Chiarini Testa, Maria Beatrice;
- Paglietti, Giovanna;
- Cherchi, Claudio;
- Carlesi, Adelina;
- Mizzoni, Irene;
- Bertini, Enrico;
- Paglietti, Maria Giovanna
Publication type:
journal article
Nusinersen in pediatric and adult patients with type III spinal muscular atrophy.
Published in:
Annals of Clinical & Translational Neurology, 2021, v. 8, n. 8, p. 1622, doi. 10.1002/acn3.51411
By:
- Pera, Maria Carmela;
- Coratti, Giorgia;
- Bovis, Francesca;
- Pane, Marika;
- Pasternak, Amy;
- Montes, Jacqueline;
- Sansone, Valeria A.;
- Dunaway Young, Sally;
- Duong, Tina;
- Messina, Sonia;
- Mizzoni, Irene;
- D'Amico, Adele;
- Civitello, Matthew;
- Glanzman, Allan M.;
- Bruno, Claudio;
- Salmin, Francesca;
- Morando, Simone;
- De Sanctis, Roberto;
- Sframeli, Maria;
- Antonaci, Laura
Publication type:
Article
Switching therapies: safety profile of Onasemnogene abeparvovec-xioi in a SMA1 patient previously treated with Risdiplam.
Published in:
Acta Myologica, 2022, v. 41, n. 3, p. 117
By:
- Tosi, Michele;
- Catteruccia, Michela;
- Cherchi, Claudio;
- Mizzoni, Irene;
- D'Amico, Adele
Publication type:
Article
Determining minimal clinically important differences in the Hammersmith Functional Motor Scale Expanded for untreated spinal muscular atrophy patients: An international study.
Published in:
European Journal of Neurology, 2024, v. 31, n. 8, p. 1, doi. 10.1111/ene.16309
By:
- Coratti, Giorgia;
- Bovis, Francesca;
- Pera, Maria Carmela;
- Scoto, Mariacristina;
- Montes, Jacqueline;
- Pasternak, Amy;
- Mayhew, Anna;
- Muni‐Lofra, Robert;
- Duong, Tina;
- Rohwer, Annemarie;
- Dunaway Young, Sally;
- Civitello, Matthew;
- Salmin, Francesca;
- Mizzoni, Irene;
- Morando, Simone;
- Pane, Marika;
- Albamonte, Emilio;
- D'Amico, Adele;
- Brolatti, Noemi;
- Sframeli, Maria
Publication type:
Article
Type I spinal muscular atrophy patients treated with nusinersen: 4‐year follow‐up of motor, respiratory and bulbar function.
Published in:
European Journal of Neurology, 2023, v. 30, n. 6, p. 1755, doi. 10.1111/ene.15768
By:
- Pane, Marika;
- Coratti, Giorgia;
- Sansone, Valeria A.;
- Messina, Sonia;
- Catteruccia, Michela;
- Bruno, Claudio;
- Sframeli, Maria;
- Albamonte, Emilio;
- Pedemonte, Marina;
- Brolatti, Noemi;
- Mizzoni, Irene;
- D'Amico, Adele;
- Bravetti, Chiara;
- Berti, Beatrice;
- Palermo, Concetta;
- Leone, Daniela;
- Salmin, Francesca;
- De Sanctis, Roberto;
- Pera, Maria Carmela;
- Piastra, Marco
Publication type:
Article

Found: 6

Correction to: Hepatobiliary disease in XLMTM: a common comorbidity with potential impact on treatment strategies.

Hepatobiliary disease in XLMTM: a common comorbidity with potential impact on treatment strategies.

Nusinersen in pediatric and adult patients with type III spinal muscular atrophy.

Switching therapies: safety profile of Onasemnogene abeparvovec-xioi in a SMA1 patient previously treated with Risdiplam.

Determining minimal clinically important differences in the Hammersmith Functional Motor Scale Expanded for untreated spinal muscular atrophy patients: An international study.

Type I spinal muscular atrophy patients treated with nusinersen: 4‐year follow‐up of motor, respiratory and bulbar function.