Found: 14
Select item for more details and to access through your institution.
Combination Antisense Treatment for Destructive Exon Skipping of Myostatin and Open Reading Frame Rescue of Dystrophin in Neonatal mdx Mice.
- Published in:
- Molecular Therapy, 2015, v. 23, n. 8, p. 1341, doi. 10.1038/mt.2015.88
- By:
- Publication type:
- Article
Microdystrophin Gene Addition Significantly Improves Muscle Functionality and Diaphragm Muscle Histopathology in a Fibrotic Mouse Model of Duchenne Muscular Dystrophy.
- Published in:
- International Journal of Molecular Sciences, 2023, v. 24, n. 9, p. 8174, doi. 10.3390/ijms24098174
- By:
- Publication type:
- Article
Targeted Antisense Oligonucleotide-Mediated Skipping of Murine Postn Exon 17 Partially Addresses Fibrosis in D2. mdx Mice.
- Published in:
- International Journal of Molecular Sciences, 2024, v. 25, n. 11, p. 6113, doi. 10.3390/ijms25116113
- By:
- Publication type:
- Article
Myostatin inhibition in combination with antisense oligonucleotide therapy improves outcomes in spinal muscular atrophy.
- Published in:
- Journal of Cachexia, Sarcopenia & Muscle, 2020, v. 11, n. 3, p. 768, doi. 10.1002/jcsm.12542
- By:
- Publication type:
- Article
Inhibition of myostatin improves muscle atrophy in oculopharyngeal muscular dystrophy (OPMD).
- Published in:
- Journal of Cachexia, Sarcopenia & Muscle, 2019, v. 10, n. 5, p. 1016, doi. 10.1002/jcsm.12438
- By:
- Publication type:
- Article
G-quadruplex ligands mediate downregulation of DUX4 expression.
- Published in:
- Nucleic Acids Research, 2020, v. 48, n. 8, p. 4179, doi. 10.1093/nar/gkaa146
- By:
- Publication type:
- Article
Expression of the Pro-Fibrotic Marker Periostin in a Mouse Model of Duchenne Muscular Dystrophy.
- Published in:
- Biomedicines, 2024, v. 12, n. 1, p. 216, doi. 10.3390/biomedicines12010216
- By:
- Publication type:
- Article
An Induced Pluripotent Stem Cell-Derived Human Blood–Brain Barrier (BBB) Model to Test the Crossing by Adeno-Associated Virus (AAV) Vectors and Antisense Oligonucleotides.
- Published in:
- Biomedicines, 2023, v. 11, n. 10, p. 2700, doi. 10.3390/biomedicines11102700
- By:
- Publication type:
- Article
Long-Term Systemic Treatment of a Mouse Model Displaying Chronic FSHD-like Pathology with Antisense Therapeutics That Inhibit DUX4 Expression.
- Published in:
- Biomedicines, 2022, v. 10, n. 7, p. N.PAG, doi. 10.3390/biomedicines10071623
- By:
- Publication type:
- Article
Targeting TGFβ Signaling to Address Fibrosis Using Antisense Oligonucleotides.
- Published in:
- Biomedicines, 2018, v. 6, n. 3, p. 74, doi. 10.3390/biomedicines6030074
- By:
- Publication type:
- Article
Systemic antisense therapeutics inhibiting DUX4 expression ameliorates FSHD-like pathology in an FSHD mouse model.
- Published in:
- Human Molecular Genetics, 2021, v. 30, n. 15, p. 1398, doi. 10.1093/hmg/ddab136
- By:
- Publication type:
- Article
Established PABPN1 intranuclear inclusions in OPMD muscle can be efficiently reversed by AAV-mediated knockdown and replacement of mutant expanded PABPN1.
- Published in:
- Human Molecular Genetics, 2019, v. 28, n. 19, p. 3301, doi. 10.1093/hmg/ddz167
- By:
- Publication type:
- Article
Functional muscle recovery following dystrophin and myostatin exon splice modulation in aged mdx mice.
- Published in:
- Human Molecular Genetics, 2019, v. 28, n. 18, p. 3091, doi. 10.1093/hmg/ddz125
- By:
- Publication type:
- Article
Pharmacological modulation of the ER stress response ameliorates oculopharyngeal muscular dystrophy.
- Published in:
- Human Molecular Genetics, 2019, v. 28, n. 10, p. 1694, doi. 10.1093/hmg/ddz007
- By:
- Publication type:
- Article