Found: 19
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Enzyme replacement in the CSF to treat metachromatic leukodystrophy in mouse model using single intracerebroventricular injection of self-complementary AAV1 vector.
- Published in:
- Scientific Reports, 2015, p. 13104, doi. 10.1038/srep13104
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- Publication type:
- Article
Targeted gene transfer into ependymal cells through intraventricular injection of AAV1 vector and long-term enzyme replacement via the CSF.
- Published in:
- Scientific Reports, 2014, p. 1, doi. 10.1038/srep05506
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- Publication type:
- Article
Intrathecal AAV Serotype 9-mediated Delivery of shRNA Against TRPV1 Attenuates Thermal Hyperalgesia in a Mouse Model of Peripheral Nerve Injury.
- Published in:
- Molecular Therapy, 2014, v. 22, n. 2, p. 409, doi. 10.1038/mt.2013.247
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- Publication type:
- Article
Corrective effect on Fabry mice of yeast recombinant human α-galactosidase with N-linked sugar chains suitable for lysosomal delivery.
- Published in:
- Journal of Human Genetics, 2006, v. 51, n. 4, p. 341, doi. 10.1007/s10038-006-0369-6
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- Publication type:
- Article
In Vivo Gene Delivery by Pancreatic Direct Injection of rAAV8 Vector Is Efficient Exclusively to the Injured Islets.
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- Diabetes, 2007, v. 56, p. A419
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- Publication type:
- Article
Therapeutic Application of Extracellular Vesicles-Capsulated Adeno-Associated Virus Vector via nSMase2/Smpd3 , Satellite, and Immune Cells in Duchenne Muscular Dystrophy.
- Published in:
- International Journal of Molecular Sciences, 2022, v. 23, n. 3, p. 1551, doi. 10.3390/ijms23031551
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- Publication type:
- Article
High-Level Expression of Alkaline Phosphatase by Adeno-Associated Virus Vector Ameliorates Pathological Bone Structure in a Hypophosphatasia Mouse Model.
- Published in:
- 2020
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- Publication type:
- journal article
Tyrosine triple mutated AAV2-BDNF gene therapy in a rat model of transient IOP elevation.
- Published in:
- Molecular Vision, 2016, v. 22, p. 1
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- Publication type:
- Article
Systemic Cancer Gene Therapy Using Adeno-associated Virus Type 1 Vector Expressing MDA-7/IL24.
- Published in:
- Molecular Therapy, 2007, v. 15, n. 10, p. 1805, doi. 10.1038/sj.mt.6300225
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- Publication type:
- Article
AAV1 Mediated Co-expression of Formylglycine-Generating Enzyme and Arylsulfatase A Efficiently Corrects Sulfatide Storage in a Mouse Model of Metachromatic Leukodystrophy.
- Published in:
- Molecular Therapy, 2007, v. 15, n. 1, p. 38, doi. 10.1038/sj.mt.6300012
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- Publication type:
- Article
996. Direct Comparison of Adeno-Associated Virus (AAV) Serotypes for Muscle Expression of Soluble Anti-Angiogenic Proteins.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S384, doi. 10.1016/j.ymthe.2006.08.1089
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- Publication type:
- Article
48. Adeno-Associated Viral (AAV) Vector- Mediated Systemic Delivery of mda-7/IL24 Inhibits Tumor Growth by Antitumor Bystander Effect.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S20, doi. 10.1016/j.ymthe.2006.08.062
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- Publication type:
- Article
407. A Single Unilateral Injection of AAV1-ASA and AAV1-FGE Vectors into the Hippocampus Results in Bilateral Expression and Widespread Distribution of ASA and Prevention of Sulfatide Storage in the Whole Brain of MLD Model Mice.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S156, doi. 10.1016/j.ymthe.2006.08.470
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- Publication type:
- Article
1071. Potential Utility of Adipose-Derived Stromal Cells (ASCs) as a Carrier for Ex Vivo Gene Therapy–Gene Transfer Efficiency of ASCs
- Published in:
- 2005
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- Publication type:
- Abstract
242. The Use of AAV Serotype 1 Vector for Expression of α-Galactosidase A in Fabry Knockout Mice
- Published in:
- 2005
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- Publication type:
- Abstract
Intraperitoneal administration of AAV9-shRNA inhibits target gene expression in the dorsal root ganglia of neonatal mice.
- Published in:
- Molecular Pain, 2013, v. 9, n. 1, p. 1, doi. 10.1186/1744-8069-9-36
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- Publication type:
- Article
Non-human primate model of amyotrophic lateral sclerosis with cytoplasmic mislocalization of TDP-43.
- Published in:
- Brain: A Journal of Neurology, 2012, v. 135, n. 3, p. 833, doi. 10.1093/brain/awr348
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- Publication type:
- Article
Serotype-independent Method of Recombinant Adeno-associated Virus (AAV) Vector Production and Purification Koichi Miyake, Noriko Miyake, Yoshiyuki Yamazaki, Takashi Shimada and Yukihiko Hirai Department of.
- Published in:
- Journal of Nippon Medical School, 2012, v. 79, n. 6, p. 394, doi. 10.1272/jnms.79.394
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- Publication type:
- Article
Microstructure and Thermal Cycle Reliability of Sn-Ag-Cu-In-Sb Solder Joint.
- Published in:
- Materials Transactions, 2022, v. 63, n. 7, p. 1021, doi. 10.2320/matertrans.MT-MC2022013
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- Publication type:
- Article