Found: 16
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Impact of next-generation sequencing error on analysis of barcoded plasmid libraries of known complexity and sequence.
- Published in:
- Nucleic Acids Research, 2014, v. 42, n. 16, p. e129, doi. 10.1093/nar/gku607
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- Publication type:
- Article
Gene therapy: Progress in childhood disease.
- Published in:
- Journal of Paediatrics & Child Health, 2012, v. 48, n. 6, p. 466, doi. 10.1111/j.1440-1754.2011.02204.x
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- Publication type:
- Article
Treatment of an infant with X-linked severe combined immunodeficiency (SCID-X1) by gene therapy in Australia.
- Published in:
- 2005
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- Publication type:
- journal article
Treatment of an infant with X‐linked severe combined immunodeficiency (SCID‐X1) by gene therapy in Australia.
- Published in:
- Medical Journal of Australia, 2005, v. 182, n. 9, p. 458, doi. 10.5694/j.1326-5377.2005.tb06785.x
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- Publication type:
- Article
Gene therapy clinical trials worldwide to 2023—an update.
- Published in:
- Journal of Gene Medicine, 2024, v. 26, n. 8, p. 1, doi. 10.1002/jgm.3721
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- Publication type:
- Article
Gene therapy clinical trials worldwide to 2017: An update.
- Published in:
- Journal of Gene Medicine, 2018, v. 20, n. 5, p. 1, doi. 10.1002/jgm.3015
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- Publication type:
- Article
Gene therapy clinical trials worldwide to 2012 - an update.
- Published in:
- Journal of Gene Medicine, 2013, v. 15, n. 2, p. 65, doi. 10.1002/jgm.2698
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- Publication type:
- Article
Lentivirus vector-mediated gene transfer to the developing bronchiolar airway epithelium in the fetal lamb.
- Published in:
- Journal of Gene Medicine, 2007, v. 9, n. 6, p. 429, doi. 10.1002/jgm.1039
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- Publication type:
- Article
Thymocyte self-renewal and oncogenic risk in immunodeficient mouse models: relevance for human gene therapy clinical trials targeting haematopoietic stem cell populations?
- Published in:
- Mammalian Genome, 2018, v. 29, n. 11/12, p. 771, doi. 10.1007/s00335-018-9780-5
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- Publication type:
- Article
Lymphomagenesis in SCID-X1 Mice Following Lentivirus-mediated Phenotype Correction Independent of Insertional Mutagenesis and γc Overexpression.
- Published in:
- Molecular Therapy, 2010, v. 18, n. 5, p. 965, doi. 10.1038/mt.2010.50
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- Publication type:
- Article
839. Lentiviral Vectors Encoding Connexin43 Mutants Reduce Gap Junction Function: Toward Molecular Ablation of Re-Entrant Cardiac Arrhythmias
- Published in:
- 2005
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- Publication type:
- Abstract
Bone Marrow Transplantation for Treatment of the Col1a2<sup>+/G610C</sup> Osteogenesis Imperfecta Mouse Model.
- Published in:
- 2019
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- Publication type:
- journal article
Restoring the natural tropism of AAV2 vectors for human liver.
- Published in:
- Science Translational Medicine, 2020, v. 12, n. 560, p. 1, doi. 10.1126/scitranslmed.aba3312
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- Publication type:
- Article
Curative Cell and Gene Therapy for Osteogenesis Imperfecta.
- Published in:
- Journal of Bone & Mineral Research, 2022, v. 37, n. 5, p. 826, doi. 10.1002/jbmr.4549
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- Publication type:
- Article
Myoblast sensitivity and fibroblast insensitivity to osteogenic conversion by BMP-2 correlates with the expression of Bmpr-1a.
- Published in:
- BMC Musculoskeletal Disorders, 2009, v. 10, p. 1, doi. 10.1186/1471-2474-10-51
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- Publication type:
- Article
A novel splice-site mutation in the common gamma chain (γc) gene IL2RG results in X-linked severe combined immunodeficiency with an atypical NK<sup>+</sup> phenotype.
- Published in:
- Human Mutation, 2004, v. 23, n. 5, p. 522, doi. 10.1002/humu.9235
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- Publication type:
- Article