Found: 8
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Fetal somatic gene therapy.
- Published in:
- Molecular Human Reproduction, 1996, v. 2, n. 9, p. 633, doi. 10.1093/molehr/2.9.633
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- Publication type:
- Article
Putative X-linked adrenoleukodystrophy gene shares unexpected homology with ABC transporters.
- Published in:
- Nature, 1993, v. 361, n. 6414, p. 726, doi. 10.1038/361726a0
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- Publication type:
- Article
Gene therapy for rheumatoid arthritis.
- Published in:
- Journal of Gene Medicine, 2002, v. 4, n. 6, p. 581, doi. 10.1002/jgm.325
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- Publication type:
- Article
Therapeutic plasma concentrations of human factor IX in mice after gene delivery into the amniotic cavity: a model for the prenatal treatment of haemophilia B.
- Published in:
- Journal of Gene Medicine, 1999, v. 1, n. 6, p. 424, doi. 10.1002/(SICI)1521-2254(199911/12)1:6<424::AID-JGM70>3.0.CO;2-Q
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- Publication type:
- Article
Intravenous Administration of Self-complementary AAV9 Enables Transgene Delivery to Adult Motor Neurons.
- Published in:
- Molecular Therapy, 2009, v. 17, n. 7, p. 1187, doi. 10.1038/mt.2009.71
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- Publication type:
- Article
AAV-mediated intramuscular delivery of myotubularin corrects the myotubular myopathy phenotype in targeted murine muscle and suggests a function in plasma membrane homeostasis.
- Published in:
- Human Molecular Genetics, 2008, v. 17, n. 14, p. 2132, doi. 10.1093/hmg/ddn112
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- Publication type:
- Article
The gene responsible for adrenoleukodystrophy encodes a peroxisomal membrane protein.
- Published in:
- Human Molecular Genetics, 1994, v. 3, n. 2, p. 265
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- Publication type:
- Article
Abnormal messenger RNA expression and a missense mutation in patients with X-linked adrenoleukodystrophy.
- Published in:
- Human Molecular Genetics, 1993, v. 2, n. 11, p. 1949
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- Publication type:
- Article