Found: 32

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  • Can the CHOP-INTEND be used as An Outcome Measure in the First Months of Age? Implications for Clinical Trials and Real World Data.

    Published in:
    Journal of Neuromuscular Diseases, 2024, v. 11, n. 1, p. 85, doi. 10.3233/JND-221644
    By:
    • Cutrona, Costanza;
    • de Sanctis, Roberto;
    • Coratti, Giorgia;
    • Capasso, Anna;
    • Ricci, Martina;
    • Stanca, Giulia;
    • Carnicella, Sara;
    • Utlulig, Meric;
    • Bersani, Giulia;
    • lazzareschi, Ilaria;
    • Leoni, Chiara;
    • Buonsenso, Danilo;
    • Luciano, Rita;
    • Vento, Giovanni;
    • Finkel, Richard S.;
    • Pane, Marika;
    • Mercuri, Eugenio
    Publication type:
    Article
  • Longitudinal Analysis of PUL 2.0 Domains in Ambulant and Non-Ambulant Duchenne Muscular Dystrophy Patients: How do they Change in Relation to Functional Ability?

    Published in:
    Journal of Neuromuscular Diseases, 2023, v. 10, n. 4, p. 567, doi. 10.3233/JND-221556
    By:
    • Pane, Marika;
    • Coratti, Giorgia;
    • Brogna, Claudia;
    • Bovis, Francesca;
    • D'Amico, Adele;
    • Pegoraro, Elena;
    • Bello, Luca;
    • Sansone, Valeria;
    • Albamonte, Emilio;
    • Ferraroli, Elisabetta;
    • Mazzone, Elena Stacy;
    • Fanelli, Lavinia;
    • Messina, Sonia;
    • Catteruccia, Michela;
    • Cicala, Gianpaolo;
    • Ricci, Martina;
    • Frosini, Silvia;
    • De Luca, Giacomo;
    • Rolle, Enrica;
    • De Sanctis, Roberto
    Publication type:
    Article
  • Oral and Swallowing Abilities Tool (OrSAT) for Type 1 SMA Patients: Development of a New Module.

    Published in:
    Journal of Neuromuscular Diseases, 2021, v. 8, n. 4, p. 589, doi. 10.3233/JND-200614
    By:
    • Berti, Beatrice;
    • Fanelli, Lavinia;
    • de Sanctis, Roberto;
    • Onesimo, Roberta;
    • Palermo, Concetta;
    • Leone, Daniela;
    • Carnicella, Sara;
    • Norcia, Giulia;
    • Forcina, Nicola;
    • Coratti, Giorgia;
    • Giorgio, Valentina;
    • Cerchiari, Antonella;
    • Lucibello, Simona;
    • Finkel, Richard;
    • Pane, Marika;
    • Mercuri, Eugenio
    Publication type:
    Article
  • Early neurological signs in infants identified through neonatal screening for SMA: do they predict outcome?

    Published in:
    European Journal of Pediatrics, 2024, v. 183, n. 7, p. 2995, doi. 10.1007/s00431-024-05546-y
    By:
    • Pane, Marika;
    • Stanca, Giulia;
    • Ticci, Chiara;
    • Cutrona, Costanza;
    • De Sanctis, Roberto;
    • Pirinu, Matteo;
    • Coratti, Giorgia;
    • Palermo, Concetta;
    • Berti, Beatrice;
    • Leone, Daniela;
    • Sacchini, Michele;
    • Cerboneschi, Margherita;
    • Fanelli, Lavinia;
    • Norcia, Giulia;
    • Forcina, Nicola;
    • Capasso, Anna;
    • Cicala, Gianpaolo;
    • Antonaci, Laura;
    • Ricci, Martina;
    • Pera, Maria Carmela
    Publication type:
    Article
  • Assessing floppy infants: a new module.

    Published in:
    European Journal of Pediatrics, 2022, v. 181, n. 7, p. 2771, doi. 10.1007/s00431-022-04476-x
    By:
    • Cutrona, Costanza;
    • Pede, Elisa;
    • De Sanctis, Roberto;
    • Coratti, Giorgia;
    • Tiberi, Eloisa;
    • Luciano, Rita;
    • Pera, Maria Carmela;
    • Velli, Chiara;
    • Capasso, Anna;
    • Vento, Giovanni;
    • Romeo, Domenico M.;
    • Pane, Marika;
    • Mercuri, Eugenio
    Publication type:
    Article
  • Neurological assessment of newborns with spinal muscular atrophy identified through neonatal screening.

    Published in:
    European Journal of Pediatrics, 2022, v. 181, n. 7, p. 2821, doi. 10.1007/s00431-022-04470-3
    By:
    • Pane, Marika;
    • Donati, Maria Alice;
    • Cutrona, Costanza;
    • De Sanctis, Roberto;
    • Pirinu, Matteo;
    • Coratti, Giorgia;
    • Ricci, Martina;
    • Palermo, Concetta;
    • Berti, Beatrice;
    • Leone, Daniela;
    • Ticci, Chiara;
    • Sacchini, Michele;
    • Cerboneschi, Margherita;
    • Capasso, Anna;
    • Cicala, Gianpaolo;
    • Pera, Maria Carmela;
    • Bravetti, Chiara;
    • Abiusi, Emanuela;
    • Vaisfeld, Alessandro;
    • Vento, Giovanni
    Publication type:
    Article
  • The 6 Minute Walk Test and Performance of Upper Limb in Ambulant Duchenne Muscular Dystrophy Boys.

    Published in:
    PLoS Currents, 2014, p. 497, doi. 10.1371/currents.md.a93d9904d57dcb08936f2ea89bca6fe6
    By:
    • Pane, Marika;
    • Mazzone, Elena Stacy;
    • Sivo, Serena;
    • Fanelli, Lavinia;
    • De Sanctis, Roberto;
    • D'Amico, Adele;
    • Messina, Sonia;
    • Battini, Roberta;
    • Bianco, Flaviana;
    • Scutifero, Marianna;
    • Petillo, Roberta;
    • Frosini, Silvia;
    • Scalise, Roberta;
    • Vita, Gian Luca;
    • Bruno, Claudio;
    • Pedemonte, Marina;
    • Mongini, Tiziana;
    • Pegoraro, Elena;
    • Brustia, Francesca;
    • Gardani, Alice
    Publication type:
    Article
  • Ambulatory function in spinal muscular atrophy: Age-related patterns of progression.

    Published in:
    PLoS ONE, 2018, v. 13, n. 6, p. 1, doi. 10.1371/journal.pone.0199657
    By:
    • Montes, Jacqueline;
    • McDermott, Michael P.;
    • Mirek, Elizabeth;
    • Mazzone, Elena S.;
    • Main, Marion;
    • Glanzman, Allan M.;
    • Duong, Tina;
    • Young, Sally Dunaway;
    • Salazar, Rachel;
    • Pasternak, Amy;
    • Gee, Richard;
    • De Sanctis, Roberto;
    • Coratti, Giorgia;
    • Forcina, Nicola;
    • Fanelli, Lavinia;
    • Ramsey, Danielle;
    • Milev, Evelin;
    • Civitello, Matthew;
    • Pane, Marika;
    • Pera, Maria Carmela
    Publication type:
    Article
  • Upper limb function in Duchenne muscular dystrophy: 24 month longitudinal data.

    Published in:
    PLoS ONE, 2018, v. 13, n. 6, p. 1, doi. 10.1371/journal.pone.0199223
    By:
    • Pane, Marika;
    • Coratti, Giorgia;
    • Brogna, Claudia;
    • Mazzone, Elena Stacy;
    • Fanelli, Lavinia;
    • De Sanctis, Roberto;
    • Forcina, Nicola;
    • Mercuri, Eugenio;
    • Gardani, Alice;
    • Berardinelli, Angela;
    • Pini, Antonella;
    • Monaco, Giulia;
    • D'Angelo, Maria Grazia;
    • Zanin, Riccardo;
    • Baranello, Giovanni;
    • Sansone, Valeria;
    • Albamonte, Emilio;
    • Sormani, Maria Pia;
    • Mayhew, Anna;
    • Messina, Sonia
    Publication type:
    Article
  • Content validity and clinical meaningfulness of the HFMSE in spinal muscular atrophy.

    Published in:
    2017
    By:
    • Pera, Maria C.;
    • Coratti^, Giorgia;
    • Forcina, Nicola;
    • Mazzone, Elena S.;
    • Scoto, Mariacristina;
    • Montes, Jacqueline;
    • Pasternak, Amy;
    • Mayhew, Anna;
    • Messina, Sonia;
    • Sframeli, Maria;
    • Main, Marion;
    • Lofra, Robert Muni;
    • Duong, Tina;
    • Ramsey, Danielle;
    • Dunaway, Sally;
    • Salazar, Rachel;
    • Fanelli^, Lavinia;
    • Civitello, Matthew;
    • de Sanctis, Roberto;
    • Antonaci, Laura
    Publication type:
    journal article
  • Clinical Variability in Spinal Muscular Atrophy Type III.

    Published in:
    Annals of Neurology, 2020, v. 88, n. 6, p. 1109, doi. 10.1002/ana.25900
    By:
    • Coratti, Giorgia;
    • Messina, Sonia;
    • Lucibello, Simona;
    • Pera, Maria Carmela;
    • Montes, Jacqueline;
    • Pasternak, Amy;
    • Bovis, Francesca;
    • Exposito Escudero, Jessica;
    • Mazzone, Elena Stacy;
    • Mayhew, Anna;
    • Glanzman, Allan M.;
    • Young, Sally Dunaway;
    • Salazar, Rachel;
    • Duong, Tina;
    • Muni Lofra, Robert;
    • De Sanctis, Roberto;
    • Carnicella, Sara;
    • Milev, Evelin;
    • Civitello, Matthew;
    • Pane, Marika
    Publication type:
    Article
  • Nusinersen in type 1 spinal muscular atrophy: Twelve-month real-world data.

    Published in:
    2019
    By:
    • Pane, Marika;
    • Coratti, Giorgia;
    • Sansone, Valeria A.;
    • Messina, Sonia;
    • Bruno, Claudio;
    • Catteruccia, Michela;
    • Sframeli, Maria;
    • Albamonte, Emilio;
    • Pedemonte, Marina;
    • D'Amico, Adele;
    • Bravetti, Chiara;
    • Berti, Beatrice;
    • Brigati, Giorgia;
    • Tacchetti, Paola;
    • Salmin, Francesca;
    • de Sanctis, Roberto;
    • Lucibello, Simona;
    • Piastra, Marco;
    • Genovese, Orazio;
    • Bertini, Enrico
    Publication type:
    journal article
  • Nusinersen efficacy data for 24‐month in type 2 and 3 spinal muscular atrophy.

    Published in:
    Annals of Clinical & Translational Neurology, 2022, v. 9, n. 3, p. 404, doi. 10.1002/acn3.51514
    By:
    • Pane, Marika;
    • Coratti, Giorgia;
    • Pera, Maria Carmela;
    • Sansone, Valeria A.;
    • Messina, Sonia;
    • d'Amico, Adele;
    • Bruno, Claudio;
    • Salmin, Francesca;
    • Albamonte, Emilio;
    • De Sanctis, Roberto;
    • Sframeli, Maria;
    • Di Bella, Vincenzo;
    • Morando, Simone;
    • Palermo, Concetta;
    • Frongia, Anna Lia;
    • Antonaci, Laura;
    • Capasso, Anna;
    • Catteruccia, Michela;
    • Longo, Antonella;
    • Ricci, Martina
    Publication type:
    Article
  • Reply to: The need for evidence‐based treatment decisions in spinal muscular atrophy type 0.

    Published in:
    Annals of Clinical & Translational Neurology, 2021, v. 8, n. 10, p. 2093, doi. 10.1002/acn3.51458
    By:
    • Mercuri, Eugenio;
    • Tiberi, Eloisa;
    • Costa, Simonetta;
    • Pane, Marika;
    • Priolo, Francesca;
    • Romeo, Domenico;
    • de Sanctis, Roberto;
    • Tiziano, Danilo;
    • Conti, Giorgio;
    • Vento, Giovanni
    Publication type:
    Article
  • Nusinersen in pediatric and adult patients with type III spinal muscular atrophy.

    Published in:
    Annals of Clinical & Translational Neurology, 2021, v. 8, n. 8, p. 1622, doi. 10.1002/acn3.51411
    By:
    • Pera, Maria Carmela;
    • Coratti, Giorgia;
    • Bovis, Francesca;
    • Pane, Marika;
    • Pasternak, Amy;
    • Montes, Jacqueline;
    • Sansone, Valeria A.;
    • Dunaway Young, Sally;
    • Duong, Tina;
    • Messina, Sonia;
    • Mizzoni, Irene;
    • D'Amico, Adele;
    • Civitello, Matthew;
    • Glanzman, Allan M.;
    • Bruno, Claudio;
    • Salmin, Francesca;
    • Morando, Simone;
    • De Sanctis, Roberto;
    • Sframeli, Maria;
    • Antonaci, Laura
    Publication type:
    Article
  • Type I SMA "new natural history": long‐term data in nusinersen‐treated patients.

    Published in:
    Annals of Clinical & Translational Neurology, 2021, v. 8, n. 3, p. 548, doi. 10.1002/acn3.51276
    By:
    • Pane, Marika;
    • Coratti, Giorgia;
    • Sansone, Valeria A.;
    • Messina, Sonia;
    • Catteruccia, Michela;
    • Bruno, Claudio;
    • Sframeli, Maria;
    • Albamonte, Emilio;
    • Pedemonte, Marina;
    • D'Amico, Adele;
    • Bravetti, Chiara;
    • Berti, Beatrice;
    • Palermo, Concetta;
    • Leone, Daniela;
    • Brigati, Giorgia;
    • Tacchetti, Paola;
    • Salmin, Francesca;
    • De Sanctis, Roberto;
    • Lucibello, Simona;
    • Pera, Maria Carmela
    Publication type:
    Article
  • Needleless inhaled anesthesia with sevoflurane: Advantages of a simplified approach for children with spinal muscular atrophy undergoing intrathecal administration of nusinersen.

    Published in:
    Pediatric Anesthesia, 2023, v. 33, n. 4, p. 282, doi. 10.1111/pan.14630
    By:
    • Salerno, Annalisa;
    • Picconi, Enzo;
    • Genovese, Orazio;
    • Piastra, Marco;
    • Pulitanò, Silvia M.;
    • Tosi, Federica;
    • Mancino, Aldo;
    • Pane, Marika;
    • De Sanctis, Roberto;
    • Carlini, Debora;
    • Mercuri, Eugenio M.;
    • Conti, Giorgio
    Publication type:
    Article
  • Long Term Natural History Data in Ambulant Boys with Duchenne Muscular Dystrophy: 36-Month Changes.

    Published in:
    PLoS ONE, 2014, v. 9, n. 10, p. 1, doi. 10.1371/journal.pone.0108205
    By:
    • Pane, Marika;
    • Mazzone, Elena Stacy;
    • Sivo, Serena;
    • Sormani, Maria Pia;
    • Messina, Sonia;
    • D′Amico, Adele;
    • Carlesi, Adelina;
    • Vita, Gianluca;
    • Fanelli, Lavinia;
    • Berardinelli, Angela;
    • Torrente, Yvan;
    • Lanzillotta, Valentina;
    • Viggiano, Emanuela;
    • D′Ambrosio, Paola;
    • Cavallaro, Filippo;
    • Frosini, Silvia;
    • Barp, Andrea;
    • Bonfiglio, Serena;
    • Scalise, Roberta;
    • De Sanctis, Roberto
    Publication type:
    Article
  • 6 Minute Walk Test in Duchenne MD Patients with Different Mutations: 12 Month Changes.

    Published in:
    PLoS ONE, 2014, v. 9, n. 1, p. 1, doi. 10.1371/journal.pone.0083400
    By:
    • Pane, Marika;
    • Mazzone, Elena S.;
    • Sormani, Maria Pia;
    • Messina, Sonia;
    • Vita, Gian Luca;
    • Fanelli, Lavinia;
    • Berardinelli, Angela;
    • Torrente, Yvan;
    • D'Amico, Adele;
    • Lanzillotta, Valentina;
    • Viggiano, Emanuela;
    • D'Ambrosio, Paola;
    • Cavallaro, Filippo;
    • Frosini, Silvia;
    • Bello, Luca;
    • Bonfiglio, Serena;
    • Scalise, Roberta;
    • De Sanctis, Roberto;
    • Rolle, Enrica;
    • Bianco, Flaviana
    Publication type:
    Article
  • 24 Month Longitudinal Data in Ambulant Boys with Duchenne Muscular Dystrophy.

    Published in:
    PLoS ONE, 2013, v. 8, n. 1, p. 1, doi. 10.1371/journal.pone.0052512
    By:
    • Mazzone, Elena Stacy;
    • Pane, Marika;
    • Sormani, Maria Pia;
    • Scalise, Roberta;
    • Berardinelli, Angela;
    • Messina, Sonia;
    • Torrente, Yvan;
    • D'Amico, Adele;
    • Doglio, Luca;
    • Viggiano, Emanuela;
    • D'Ambrosio, Paola;
    • Cavallaro, Filippo;
    • Frosini, Silvia;
    • Bello, Luca;
    • Bonfiglio, Serena;
    • De Sanctis, Roberto;
    • Rolle, Enrica;
    • Bianco, Flaviana;
    • Magri, Francesca;
    • Rossi, Francesca
    Publication type:
    Article
  • De Novo Partial 13q22-q34 Trisomy with Typical Neurological and Immunological Findings: A Case Report with New Genetic Insights.

    Published in:
    Brain Sciences (2076-3425), 2021, v. 11, n. 1, p. 21, doi. 10.3390/brainsci11010021
    By:
    • Brogna, Claudia;
    • Milano, Valentina;
    • Brogna, Barbara;
    • Cristiano, Lara;
    • Rovere, Giuseppe;
    • De Sanctis, Roberto;
    • Romeo, Domenico M.;
    • Mercuri, Eugenio;
    • Zampino, Giuseppe
    Publication type:
    Article
  • Revised Hammersmith Scale for spinal muscular atrophy: A SMA specific clinical outcome assessment tool.

    Published in:
    PLoS ONE, 2017, v. 12, n. 2, p. 1, doi. 10.1371/journal.pone.0172346
    By:
    • Ramsey, Danielle;
    • Scoto, Mariacristina;
    • Mayhew, Anna;
    • Main, Marion;
    • Mazzone, Elena S.;
    • Montes, Jacqueline;
    • de Sanctis, Roberto;
    • Dunaway Young, Sally;
    • Salazar, Rachel;
    • Glanzman, Allan M.;
    • Pasternak, Amy;
    • Quigley, Janet;
    • Mirek, Elizabeth;
    • Duong, Tina;
    • Gee, Richard;
    • Civitello, Matthew;
    • Tennekoon, Gihan;
    • Pane, Marika;
    • Pera, Maria Carmela;
    • Bushby, Kate
    Publication type:
    Article
  • Ultrasound assessment of diaphragmatic function in type 1 spinal muscular atrophy.

    Published in:
    Pediatric Pulmonology, 2020, v. 55, n. 7, p. 1781, doi. 10.1002/ppul.24814
    By:
    • Buonsenso, Danilo;
    • Berti, Beatrice;
    • Palermo, Concetta;
    • Leone, Daniela;
    • Ferrantini, Gloria;
    • De Sanctis, Roberto;
    • Onesimo, Roberta;
    • Curatola, Antonietta;
    • Fanelli, Lavinia;
    • Forcina, Nicola;
    • Norcia, Giulia;
    • Carnicella, Sara;
    • Lucibello, Simona;
    • Mercuri, Eugenio;
    • Pane, Marika
    Publication type:
    Article
  • Diagnostic journey in Spinal Muscular Atrophy: Is it still an odyssey?

    Published in:
    PLoS ONE, 2020, v. 15, n. 3, p. 1, doi. 10.1371/journal.pone.0230677
    By:
    • Pera, Maria Carmela;
    • Coratti, Giorgia;
    • Berti, Beatrice;
    • D'Amico, Adele;
    • Sframeli, Maria;
    • Albamonte, Emilio;
    • de Sanctis, Roberto;
    • Messina, Sonia;
    • Catteruccia, Michela;
    • Brigati, Giorgia;
    • Antonaci, Laura;
    • Lucibello, Simona;
    • Bruno, Claudio;
    • Sansone, Valeria A.;
    • Bertini, Enrico;
    • Tiziano, Danilo;
    • Pane, Marika;
    • Mercuri, Eugenio
    Publication type:
    Article
  • Longitudinal natural history of type I spinal muscular atrophy: a critical review.

    Published in:
    2020
    By:
    • Mercuri, Eugenio;
    • Lucibello, Simona;
    • Perulli, Marco;
    • Coratti, Giorgia;
    • de Sanctis, Roberto;
    • Pera, Maria Carmela;
    • Pane, Marika;
    • Montes, Jacqueline;
    • de Vivo, Darryl C.;
    • Darras, Basil T.;
    • Kolb, Stephen J.;
    • Finkel, Richard S.
    Publication type:
    journal article
  • Different trajectories in upper limb and gross motor function in spinal muscular atrophy.

    Published in:
    Muscle & Nerve, 2021, v. 64, n. 5, p. 552, doi. 10.1002/mus.27384
    By:
    • Coratti, Giorgia;
    • Pera, Maria Carmela;
    • Montes, Jacqueline;
    • Pasternak, Amy;
    • Scoto, Mariacristina;
    • Baranello, Giovanni;
    • Messina, Sonia;
    • Dunaway Young, Sally;
    • Glanzman, Allan M.;
    • Duong, Tina;
    • De Sanctis, Roberto;
    • Mazzone, Elena Stacy;
    • Milev, Evelin;
    • Rohwer, Annemarie;
    • Civitello, Matthew;
    • Pane, Marika;
    • Antonaci, Laura;
    • Frongia, Anna Lia;
    • Sframeli, Maria;
    • Vita, Gian Luca
    Publication type:
    Article
  • Revised upper limb module for spinal muscular atrophy: 12 month changes.

    Published in:
    2019
    By:
    • Pera, Maria Carmela;
    • Coratti, Giorgia;
    • Mazzone, Elena S.;
    • Montes, Jacqueline;
    • Scoto, Mariacristina;
    • De Sanctis, Roberto;
    • Main, Marion;
    • Mayhew, Anna;
    • Muni Lofra, Robert;
    • Dunaway Young, Sally;
    • Glanzman, Allan M.;
    • Duong, Tina;
    • Pasternak, Amy;
    • Ramsey, Danielle;
    • Darras, Basil;
    • Day, John W.;
    • Finkel, Richard S.;
    • De Vivo, Darryl C.;
    • Sormani, Maria Pia;
    • Bovis, Francesca
    Publication type:
    journal article
  • Revised upper limb module for spinal muscular atrophy: Development of a new module.

    Published in:
    2017
    By:
    • Mazzone, Elena S.;
    • Mayhew, Anna;
    • Montes, Jacqueline;
    • Ramsey, Danielle;
    • Fanelli, Lavinia;
    • Young, Sally Dunaway;
    • Salazar, Rachel;
    • De Sanctis, Roberto;
    • Pasternak, Amy;
    • Glanzman, Allan;
    • Coratti, Giorgia;
    • Civitello, Matthew;
    • Forcina, Nicola;
    • Gee, Richard;
    • Duong, Tina;
    • Pane, Marika;
    • Scoto, Mariacristina;
    • Pera, Maria Carmela;
    • Messina, Sonia;
    • Tennekoon, Gihan
    Publication type:
    journal article
  • Type I spinal muscular atrophy patients treated with nusinersen: 4‐year follow‐up of motor, respiratory and bulbar function.

    Published in:
    European Journal of Neurology, 2023, v. 30, n. 6, p. 1755, doi. 10.1111/ene.15768
    By:
    • Pane, Marika;
    • Coratti, Giorgia;
    • Sansone, Valeria A.;
    • Messina, Sonia;
    • Catteruccia, Michela;
    • Bruno, Claudio;
    • Sframeli, Maria;
    • Albamonte, Emilio;
    • Pedemonte, Marina;
    • Brolatti, Noemi;
    • Mizzoni, Irene;
    • D'Amico, Adele;
    • Bravetti, Chiara;
    • Berti, Beatrice;
    • Palermo, Concetta;
    • Leone, Daniela;
    • Salmin, Francesca;
    • De Sanctis, Roberto;
    • Pera, Maria Carmela;
    • Piastra, Marco
    Publication type:
    Article
  • Revised North Star Ambulatory Assessment for Young Boys with Duchenne Muscular Dystrophy.

    Published in:
    PLoS ONE, 2016, v. 11, n. 8, p. 1, doi. 10.1371/journal.pone.0160195
    By:
    • Mercuri, Eugenio;
    • Coratti, Giorgia;
    • Messina, Sonia;
    • Ricotti, Valeria;
    • Baranello, Giovanni;
    • D’Amico, Adele;
    • Pera, Maria Carmela;
    • Albamonte, Emilio;
    • Sivo, Serena;
    • Mazzone, Elena Stacy;
    • Arnoldi, Maria Teresa;
    • Fanelli, Lavinia;
    • De Sanctis, Roberto;
    • Romeo, Domenico M;
    • Vita, Gian Luca;
    • Battini, Roberta;
    • Bertini, Enrico;
    • Muntoni, Francesco;
    • Pane, Marika
    Publication type:
    Article
  • Timed Rise from Floor as a Predictor of Disease Progression in Duchenne Muscular Dystrophy: An Observational Study.

    Published in:
    PLoS ONE, 2016, v. 11, n. 3, p. 1, doi. 10.1371/journal.pone.0151445
    By:
    • Mazzone, Elena S.;
    • Coratti, Giorgia;
    • Sormani, Maria Pia;
    • Messina, Sonia;
    • Pane, Marika;
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    PLoS ONE, 2015, v. 10, n. 12, p. 1, doi. 10.1371/journal.pone.0144079
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