Found: 4
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Haematopoietic cell transplantation (HCT) in combination with enzyme replacement therapy (ERT) in patients with Hurler syndrome.
- Published in:
- Bone Marrow Transplantation, 2006, v. 38, n. 1, p. 17, doi. 10.1038/sj.bmt.1705401
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- Article
Potential efficacy of enzyme replacement and substrate reduction therapy in three siblings with Gaucher disease type III.
- Published in:
- Journal of Inherited Metabolic Disease, 2008, v. 31, n. 6, p. 745, doi. 10.1007/s10545-008-0873-2
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- Article
Home treatment with enzyme replacement therapy for mucopolysaccharidosis type I is feasible and safe.
- Published in:
- Journal of Inherited Metabolic Disease, 2007, v. 30, n. 6, p. 984, doi. 10.1007/s10545-007-0686-8
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- Publication type:
- Article
Restricted upper extremity range of motion in mucopolysaccharidosis type I: no response to one year of enzyme replacement therapy.
- Published in:
- Journal of Inherited Metabolic Disease, 2007, v. 30, n. 1, p. 47, doi. 10.1007/s10545-006-0490-x
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- Article