Migalastat HCl Reduces Globotriaosylsphingosine (Lyso-Gb₃) in Fabry Transgenic Mice and in the Plasma of Fabry Patients.

Published in:

PLoS ONE, 2013, v. 8, n. 3, p. 1, doi. 10.1371/journal.pone.0057631

By:

• Young-Gqamana, Brandy;
• Brignol, Nastry;
• Chang, Hui-Hwa;
• Khanna, Richie;
• Soska, Rebecca;
• Fuller, Maria;
• Sitaraman, Sheela A.;
• Germain, Dominique P.;
• Giugliani, Roberto;
• Hughes, Derralynn A.;
• Mehta, Atul;
• Nicholls, Kathy;
• Boudes, Pol;
• Lockhart, David J.;
• Valenzano, Kenneth J.;
• Benjamin, Elfrida R.

Publication type:

Article