Found: 16
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Gene Therapy for Pediatric AIDS.
- Published in:
- Annals of the New York Academy of Sciences, 2000, v. 918, n. 1, p. 318, doi. 10.1111/j.1749-6632.2000.tb05501.x
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- Publication type:
- Article
Efficient Characterization of Retro-, Lenti-, and Foamyvector-Transduced Cell Populations by High-Accuracy Insertion Site Sequencing.
- Published in:
- Annals of the New York Academy of Sciences, 2003, v. 996, n. 1, p. 112, doi. 10.1111/j.1749-6632.2003.tb03239.x
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- Publication type:
- Article
Effects of Vector Backbone and Pseudotype on Lentiviral Vector-mediated Gene Transfer: Studies in Infant ADA-Deficient Mice and Rhesus Monkeys.
- Published in:
- Molecular Therapy, 2014, v. 22, n. 10, p. 1803, doi. 10.1038/mt.2014.88
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- Publication type:
- Article
Preclinical Demonstration of Lentiviral Vector-mediated Correction of Immunological and Metabolic Abnormalities in Models of Adenosine Deaminase Deficiency.
- Published in:
- Molecular Therapy, 2014, v. 22, n. 3, p. 607, doi. 10.1038/mt.2013.265
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- Publication type:
- Article
1089. Neonatal BMT of ADA-Deficient SCID Mice Results in Phenotypic Correction Despite Low Levels of Engraftment and Absence of the Selective T Lymphoid Expansion Seen in γc Gene Knock-Out Mice.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S418, doi. 10.1016/j.ymthe.2006.08.1191
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- Publication type:
- Article
1090. Enzyme Replacement Therapy with Pegylated Adenosine Deaminase (PEG-ADA) Does Not Impede Immune Reconstitution Following Transplantation of Gene-Corrected Bone Marrow Cells in the Murine Model of ADA-SCID.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S419, doi. 10.1016/j.ymthe.2006.08.1192
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- Publication type:
- Article
In Vivo Transduction by Intravenous Injection of a Lentiviral Vector Expressing Human ADA into Neonatal ADA Gene Knockout Mice: A Novel Form of Enzyme Replacement Therapy for ADA Deficiency.
- Published in:
- Molecular Therapy, 2006, v. 13, n. 6, p. 1110, doi. 10.1016/j.ymthe.2006.02.013
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- Publication type:
- Article
Selective survival of peripheral blood lymphocytes in children with HIV-1 following delivery of an anti-HIV gene to bone marrow CD34<sup>+</sup> cells
- Published in:
- Molecular Therapy, 2005, v. 12, n. 1, p. 77, doi. 10.1016/j.ymthe.2005.02.024
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- Publication type:
- Article
805. Effective Suicide Gene Therapy of Leukemia in a Novel Model of Retroviral Insertion
- Published in:
- 2005
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- Publication type:
- Abstract
37. A Novel Form of Enzyme Replacement Therapy for ADA-Deficiency: In Vivo Transduction by Neonatal Injection of Lentivirus Expressing ADA
- Published in:
- 2005
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- Publication type:
- Abstract
Neonatal Gene Therapy of MPS I Mice by Intravenous Injection of a Lentiviral Vector
- Published in:
- Molecular Therapy, 2005, v. 11, n. 5, p. 776, doi. 10.1016/j.ymthe.2004.10.006
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- Publication type:
- Article
Expression from Second-Generation Feline Immunodeficiency Virus Vectors Is Impaired in Human Hematopoietic Cells
- Published in:
- Molecular Therapy, 2002, v. 6, n. 5, p. 645, doi. 10.1006/mthe.2002.0725
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- Publication type:
- Article
Adenosine Deaminase (ADA)-Deficient Severe Combined Immune Deficiency (SCID): Molecular Pathogenesis and Clinical Manifestations.
- Published in:
- Journal of Clinical Immunology, 2017, v. 37, n. 7, p. 626, doi. 10.1007/s10875-017-0433-3
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- Publication type:
- Article
Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiency.
- Published in:
- 2017
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- Publication type:
- journal article
Clonality analysis after retroviral-mediated gene transfer to CD34<sup>+</sup> cells from the cord blood of ADA-deficient SCID neonates.
- Published in:
- Nature Medicine, 2003, v. 9, n. 4, p. 463, doi. 10.1038/nm844
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- Publication type:
- Article
Differences between lentiviral vector--mediated ex vivo hematopoietic stem cell and adeno-associated virus gene therapies for neurological disorders.
- Published in:
- Journal of Neurosurgery, 2022, v. 136, n. 5, p. 1501, doi. 10.3171/2021.10.JNS212456
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- Publication type:
- Article