Found: 3

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  • Clinician Perspectives of Gene Therapy as a Treatment Option for Duchenne Muscular Dystrophy.

    Published in:
    Journal of Neuromuscular Diseases, 2024, v. 11, n. 5, p. 1085, doi. 10.3233/JND-240033
    By:
    • Cope, Heidi;
    • Fischer, Ryan;
    • Heslop, Emma;
    • McNiff, Megan;
    • Johnson, Alexandra;
    • Camino, Eric;
    • Denger, Brian;
    • Armstrong, Niki;
    • Thakrar, Sejal;
    • Bateman-House, Alison;
    • Beaverson, Katherine L.;
    • Woollacott, Ione O.C.;
    • Phillips, Dawn;
    • Fernandez, Vivian;
    • Ganot, Annie;
    • Donisa-Dreghici, Roxana;
    • Mansfield, Carol;
    • Peay, Holly
    Publication type:
    Article

  • The IRDiRC Chrysalis Task Force: making rare disease research attractive to companies.

    Published in:
    Therapeutic Advances in Rare Disease, 2023, v. 4, p. 1, doi. 10.1177/26330040231188979
    By:
    • Beaverson, Katherine L.;
    • Julkowska, Daria;
    • Letinturier, Mary Catherine V.;
    • Aartsma-Rus, Annemieke;
    • Austin, Jennifer;
    • Bueren, Juan;
    • Frost, Simon;
    • Hamamura, Misako;
    • Larkindale, Jane;
    • LaRosa, Greg;
    • Magenheim, Rita;
    • Merico, Annamaria;
    • Gerdina Pasmooij, Anna Maria;
    • Pirard, Vinciane;
    • Ekow Thomford, Nicholas;
    • Wada, Michihiko;
    • Wong-Rieger, Durhane;
    • Hartman, Adam L.
    Publication type:
    Article

  • A phase II trial of carboplatin for intraocular retinoblastoma.

    Published in:
    Pediatric Blood & Cancer, 2007, v. 49, n. 5, p. 643, doi. 10.1002/pbc.21163
    By:
    • Dunkel, Ira J.;
    • Lee, Thomas C.;
    • Shi, Weiji;
    • Beaverson, Katherine L.;
    • Novetsky, Danielle;
    • Lyden, David;
    • Finlay, Jonathan L.;
    • McCormick, Beryl;
    • Abramson, David H.
    Publication type:
    Article