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  • Gene Therapy for Leber's Congenital Amaurosis is Safe and Effective Through 1.5 Years After Vector Administration.

    Published in:
    Molecular Therapy, 2010, v. 18, n. 3, p. 643, doi. 10.1038/mt.2009.277
    By:
    • Simonelli, Francesca;
    • Maguire, Albert M.;
    • Testa, Francesco;
    • Pierce, Eric A.;
    • Mingozzi, Federico;
    • Bennicelli, Jeannette L.;
    • Rossi, Settimio;
    • Marshall, Kathleen;
    • Banfi, Sandro;
    • Surace, Enrico M.;
    • Sun, Junwei;
    • Redmond, T. Michael;
    • Xiaosong Zhu;
    • Shindler, Kenneth S.;
    • Gui-Shuang Ying;
    • Ziviello, Carmela;
    • Acerra, Carmela;
    • Wright, J. Fraser;
    • McDonnell, Jennifer Wellman;
    • High, Katherine A.
    Publication type:
    Article