Miglustat therapy in the French cohort of paediatric patients with Niemann-Pick disease type C.Published in:Orphanet Journal of Rare Diseases, 2012, v. 7, n. 1, p. 36, doi. 10.1186/1750-1172-7-36By:H�ron, B�n�dicte;Valayannopoulos, Vassili;Baruteau, Julien;Chabrol, Brigitte;Ogier, H�l�ne;Latour, Philippe;Dobbelaere, Dries;Eyer, Didier;Labarthe, Fran�ois;Maurey, H�l�ne;Cuisset, Jean-Marie;de Villemeur, Thierry Billette;Sedel, Fr�d�ric;Vanier, Marie T.Publication type:Article