Found: 32
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Dysregulation of Multiple Facets of Glycogen Metabolism in a Murine Model of Pompe Disease.
- Published in:
- PLoS ONE, 2013, v. 8, n. 2, p. 1, doi. 10.1371/journal.pone.0056181
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- Publication type:
- Article
Systemic Delivery of a Glucosylceramide Synthase Inhibitor Reduces CNS Substrates and Increases Lifespan in a Mouse Model of Type 2 Gaucher Disease.
- Published in:
- PLoS ONE, 2012, v. 7, n. 8, p. 1, doi. 10.1371/journal.pone.0043310
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- Publication type:
- Article
Iminosugar-Based Inhibitors of Glucosylceramide Synthase Increase Brain Glycosphingolipids and Survival in a Mouse Model of Sandhoff Disease.
- Published in:
- PLoS ONE, 2011, v. 6, n. 6, p. 1, doi. 10.1371/journal.pone.0021758
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- Publication type:
- Article
Substrate Reduction Augments the Efficacy of Enzyme Therapy in a Mouse Model of Fabry Disease.
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- PLoS ONE, 2010, v. 5, n. 11, p. 1, doi. 10.1371/journal.pone.0015033
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- Publication type:
- Article
Role of viral hemagglutinin glycosylation in anti-influenza activities of recombinant surfactant protein D.
- Published in:
- Respiratory Research, 2008, v. 9, p. 1, doi. 10.1186/1465-9921-9-65
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- Publication type:
- Article
Inefficient cationic lipid-mediated siRNA and antisense oligonucleotide transfer to airway epithelial cells in vivo.
- Published in:
- Respiratory Research, 2006, v. 7, p. 26, doi. 10.1186/1465-9921-7-26
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- Publication type:
- Article
Gene therapy for lung cancer--an application for cationic lipid-mediated gene delivery?
- Published in:
- 1998
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- Publication type:
- commentary
Endostatin gene transfection using a cationic lipid: advantages of transfection before tumor cell inoculation and repeated transfection.
- Published in:
- Cancer Gene Therapy, 2004, v. 11, n. 5, p. 354, doi. 10.1038/sj.cgt.7700704
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- Publication type:
- Article
Effects of continuous high dose rhgm-csf infusion on human monocyte activity.
- Published in:
- American Journal of Hematology, 1993, v. 43, n. 4, p. 279, doi. 10.1002/ajh.2830430410
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- Publication type:
- Article
Intratracheal recombinant surfactant protein d prevents endotoxin shock in the newborn preterm lamb.
- Published in:
- 2006
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- Publication type:
- journal article
Intratracheal Recombinant Surfactant Protein D Prevents Endotoxin Shock in the Newborn Preterm Lamb.
- Published in:
- American Journal of Respiratory & Critical Care Medicine, 2006, v. 173, n. 12, p. 1342, doi. 10.1164/rccm.200509-1485OC
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- Publication type:
- Article
Low-frequency ultrasound increases non-viral gene transfer to the mouse lung.
- Published in:
- Acta Biochimica et Biophysica Sinica, 2010, v. 42, n. 1, p. 45, doi. 10.1093/abbs/gmp100
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- Publication type:
- Article
Efficacy of Enzyme and Substrate Reduction Therapy with a Novel Antagonist of Glucosylceramide Synthase for Fabry Disease.
- Published in:
- Molecular Medicine, 2015, v. 21, n. 1, p. 389, doi. 10.2119/molmed.2015.00088
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- Publication type:
- Article
Assessment of the nuclear pore dilating agent trans-cyclohexane-1,2-diol in differentiated airway epithelium.
- Published in:
- Journal of Gene Medicine, 2012, v. 14, n. 7, p. 491, doi. 10.1002/jgm.2643
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- Publication type:
- Article
Detection of CFTR transgene mRNA expression in respiratory epithelium isolated from the murine nasal cavity.
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- Journal of Gene Medicine, 2010, v. 12, n. 1, p. 55, doi. 10.1002/jgm.1413
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- Publication type:
- Article
Partial correction of the α-galactosidase A deficiency and reduction of glycolipid storage in Fabry mice using synthetic vectors.
- Published in:
- Journal of Gene Medicine, 2004, v. 6, n. 1, p. 85, doi. 10.1002/jgm.468
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- Publication type:
- Article
Systemic Administration of AAV8-α-galactosidase A Induces Humoral Tolerance in Nonhuman Primates Despite Low Hepatic Expression.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 11, p. 1999, doi. 10.1038/mt.2011.119
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- Publication type:
- Article
Induction of Immune Tolerance to a Therapeutic Protein by Intrathymic Gene Delivery.
- Published in:
- Molecular Therapy, 2010, v. 18, n. 12, p. 2146, doi. 10.1038/mt.2010.164
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- Publication type:
- Article
Preexisting Immunity and Low Expression in Primates Highlight Translational Challenges for Liver-directed AAV8-mediated Gene Therapy.
- Published in:
- Molecular Therapy, 2010, v. 18, n. 11, p. 1983, doi. 10.1038/mt.2010.175
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- Publication type:
- Article
Evaluation of Systemic Follistatin as an Adjuvant to Stimulate Muscle Repair and Improve Motor Function in Pompe Mice.
- Published in:
- Molecular Therapy, 2010, v. 18, n. 9, p. 1584, doi. 10.1038/mt.2010.110
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- Publication type:
- Article
Systemic Insulin-like Growth Factor-1 Reverses Hypoalgesia and Improves Mobility in a Mouse Model of Diabetic Peripheral Neuropathy.
- Published in:
- Molecular Therapy, 2008, v. 16, n. 8, p. 1400, doi. 10.1038/mt.2008.115
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- Publication type:
- Article
Timing of Therapeutic Intervention Determines Functional and Survival Outcomes in a Mouse Model of Late Infantile Batten Disease.
- Published in:
- Molecular Therapy, 2007, v. 15, n. 10, p. 1782, doi. 10.1038/sj.mt.6300249
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- Publication type:
- Article
893. Second Generation Gene Therapy Vector for Classical Late Infantile Neuronal Ceroid Lipofuscinosis.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S344, doi. 10.1016/j.ymthe.2006.08.982
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- Publication type:
- Article
217. Comparison of Hepatic Vein and Peripheral Vein Delivery of an AAV2/8 Vector Encoding Human a-Galactosidase A to Rhesus Macaques.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S84, doi. 10.1016/j.ymthe.2006.08.242
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- Publication type:
- Article
695. Low-Frequency Ultrasound Increases Non-Viral Lung Gene Transfer.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S269, doi. 10.1016/j.ymthe.2006.08.773
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- Publication type:
- Article
Local Delivery of a Viral Vector Mitigates Neutralization by Antiviral Antibodies and Results in Efficient Transduction of Rabbit Liver
- Published in:
- Molecular Therapy, 2005, v. 12, n. 6, p. 1043, doi. 10.1016/j.ymthe.2005.06.475
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- Publication type:
- Article
Transient siRNA-Mediated Attenuation of Liver Expression from an α-Galactosidase a Plasmid Reduces Subsequent Humoral Immune Responses to the Transgene Product in Mice
- Published in:
- Molecular Therapy, 2005, v. 12, n. 2, p. 264, doi. 10.1016/j.ymthe.2005.04.007
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- Publication type:
- Article
531. Balloon Catheter-Mediated Hepatic Vein Delivery of a Viral Vector Mitigates Neutralization by Anti-Viral Antibodies and Results in Efficient Transduction of Rabbit Liver
- Published in:
- 2005
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- Publication type:
- Abstract
Long-term Transgene Expression from Plasmid DNA Gene Therapy Vectors Is Negatively Affected by CpG Dinucleotides
- Published in:
- Molecular Therapy, 2004, v. 10, n. 2, p. 269, doi. 10.1016/j.ymthe.2004.04.018
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- Publication type:
- Article
Contribution of Toll-like Receptor 9 Signaling to the Acute Inflammatory Response to Nonviral Vectors
- Published in:
- Molecular Therapy, 2004, v. 9, n. 2, p. 241, doi. 10.1016/j.ymthe.2003.11.012
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- Publication type:
- Article
Tumor Treatment with Complexes of Cationic Lipid and Noncoding Plasmid DNA Results in the Induction of Cytotoxic T Cells and Systemic Tumor Elimination
- Published in:
- Molecular Therapy, 2002, v. 6, n. 4, p. 519, doi. 10.1006/mthe.2002.0697
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- Publication type:
- Article
CpG-Depleted Plasmid DNA Vectors with Enhanced Safety and Long-Term Gene Expression in Vivo
- Published in:
- Molecular Therapy, 2002, v. 5, n. 6, p. 731, doi. 10.1006/mthe.2002.0598
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- Publication type:
- Article