Back to matchesWe found a matchYour institution may have rights to this item. Sign in to continue.TitleSpending on Targeted Therapies for Duchenne Muscular Dystrophy.AuthorsBendicksen, Liam; Kesselheim, Aaron S.; Rome, Benjamin N.AbstractThis study estimates public and private spending on genetically targeted treatments for Duchenne muscular dystrophy during years in which the drugs were marketed without completed confirmatory studies.SubjectsDUCHENNE muscular dystrophy; DRUG marketing; PUBLIC spendingPublicationJAMA: Journal of the American Medical Association, 2024, p1151ISSN0098-7484Publication typeArticleDOI10.1001/jama.2024.2776