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Association of Severe Autoimmune Thrombocytopenic Purpura and Crohn's Disease.
- Published in:
- 1997
- By:
- Publication type:
- Letter
A zymogen-like factor Xa variant corrects the coagulation defect in hemophilia.
- Published in:
- Nature Biotechnology, 2011, v. 29, n. 11, p. 1028, doi. 10.1038/nbt.1995
- By:
- Publication type:
- Article
CORRIGENDUM: Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response.
- Published in:
- 2006
- By:
- Publication type:
- Correction Notice
Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response.
- Published in:
- Nature Medicine, 2006, v. 12, n. 3, p. 342, doi. 10.1038/nm1358
- By:
- Publication type:
- Article
Characterization of Naturally-Occurring Humoral Immunity to AAV in Sheep.
- Published in:
- PLoS ONE, 2013, v. 8, n. 9, p. 1, doi. 10.1371/journal.pone.0075142
- By:
- Publication type:
- Article
Translational Potential of Immune Tolerance Induction by AAV Liver-Directed Factor VIII Gene Therapy for Hemophilia A.
- Published in:
- Frontiers in Immunology, 2020, v. 11, p. 1, doi. 10.3389/fimmu.2020.00618
- By:
- Publication type:
- Article
Gene therapy for hemophilia: what does the future hold?
- Published in:
- Therapeutic Advances in Hematology, 2018, v. 9, n. 9, p. 273, doi. 10.1177/2040620718791933
- By:
- Publication type:
- Article
Prevalence of the prothrombin gene variant 20210 G→A among patients with myocardial infarction.
- Published in:
- Cardiovascular Research, 1998, v. 37, n. 1, p. 42, doi. 10.1016/S0008-6363(97)00211-3
- By:
- Publication type:
- Article
B cell-activating factor modulates the factor VIII immune response in hemophilia A.
- Published in:
- 2021
- By:
- Publication type:
- journal article
Factor V Leiden (FVQ 506) is common in a Brazilian population.
- Published in:
- American Journal of Hematology, 1995, v. 49, n. 3, p. 242, doi. 10.1002/ajh.2830490312
- By:
- Publication type:
- Article
Association of severe haemophilia A and factor V Leiden: report of three cases.
- Published in:
- Haemophilia, 1996, v. 2, n. 1, p. 51, doi. 10.1111/j.1365-2516.1996.tb00011.x
- By:
- Publication type:
- Article
Gene therapy matures to medicines.
- Published in:
- Human Molecular Genetics, 2019, v. 28, p. R1, doi. 10.1093/hmg/ddz182
- By:
- Publication type:
- Article
Successful Phenotype Improvement following Gene Therapy for Severe Hemophilia A in Privately Owned Dogs.
- Published in:
- PLoS ONE, 2016, v. 11, n. 3, p. 1, doi. 10.1371/journal.pone.0151800
- By:
- Publication type:
- Article
A prospective study on the prevalence and risk factors for neonatal thrombocytopenia and platelet alloimmunization among 9332 unselected Brazilian newborns.
- Published in:
- Transfusion, 2007, v. 47, n. 1, p. 59, doi. 10.1111/j.1537-2995.2007.01064.x
- By:
- Publication type:
- Article
Genetic variability of platelet glycoprotein Ibα gene.
- Published in:
- American Journal of Hematology, 2004, v. 77, n. 2, p. 107, doi. 10.1002/ajh.20148
- By:
- Publication type:
- Article
Follow?up of sickle cell disease patients with priapism treated by hydroxyurea.
- Published in:
- American Journal of Hematology, 2004, v. 77, n. 1, p. 45, doi. 10.1002/ajh.20142
- By:
- Publication type:
- Article
β-thalassemia trait might increase the severity of hemochromatosis in subjects with the C282Y mutation in the HFE gene.
- Published in:
- American Journal of Hematology, 2000, v. 63, n. 4, p. 230, doi. 10.1002/(SICI)1096-8652(200004)63:4<230::AID-AJH12>3.0.CO;2-5
- By:
- Publication type:
- Article
Prothrombin mutant, factor V Leiden, and thermolabile variant of methylenetetrahidrofolate reductase among patients with sickle cell disease in Brazil.
- Published in:
- American Journal of Hematology, 1998, v. 59, n. 1, p. 46, doi. 10.1002/(SICI)1096-8652(199809)59:1<46::AID-AJH9>3.0.CO;2-#
- By:
- Publication type:
- Article
Efficacy and Safety of Long-term Prophylaxis in Severe Hemophilia A Dogs Following Liver Gene Therapy Using AAV Vectors.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 3, p. 442, doi. 10.1038/mt.2010.240
- By:
- Publication type:
- Article
Safety of AAV Factor IX Peripheral Transvenular Gene Delivery to Muscle in Hemophilia B Dogs.
- Published in:
- Molecular Therapy, 2010, v. 18, n. 7, p. 1318, doi. 10.1038/mt.2010.73
- By:
- Publication type:
- Article
Strategies to Modulate Immune Responses: A New Frontier for Gene Therapy.
- Published in:
- Molecular Therapy, 2009, v. 17, n. 9, p. 1492, doi. 10.1038/mt.2009.150
- By:
- Publication type:
- Article
Host and Vector-dependent Effects on the Risk of Germline Transmission of AAV Vectors.
- Published in:
- Molecular Therapy, 2009, v. 17, n. 6, p. 1022, doi. 10.1038/mt.2009.56
- By:
- Publication type:
- Article
Safety and Efficacy of Regional Intravenous (RI) Versus Intramuscular (IM) Delivery of rAAV1 and rAAV8 to Nonhuman Primate Skeletal Muscle.
- Published in:
- Molecular Therapy, 2008, v. 16, n. 7, p. 1291, doi. 10.1038/mt.2008.87
- By:
- Publication type:
- Article
Reversal of Blindness in Animal Models of Leber Congenital Amaurosis Using Optimized AAV2-mediated Gene Transfer.
- Published in:
- Molecular Therapy, 2008, v. 16, n. 3, p. 458, doi. 10.1038/sj.mt.6300389
- By:
- Publication type:
- Article
The Enhancing Effects of the Light Chain on Heavy Chain Secretion in Split Delivery of Factor VIII Gene.
- Published in:
- Molecular Therapy, 2007, v. 15, n. 10, p. 1856, doi. 10.1038/sj.mt.6300268
- By:
- Publication type:
- Article
The Role of Immunosuppression in Gene- and Cell-Based Treatments for Duchenne Muscular Dystrophy.
- Published in:
- Molecular Therapy, 2007, v. 15, n. 6, p. 1040, doi. 10.1038/sj.mt.6300194
- By:
- Publication type:
- Article
Corrigendum to “Inadvertent Germline Transmission of AAV2 Vector: Findings in a Rabbit Model Correlate with Those in a Human Clinical Trial”.
- Published in:
- 2006
- By:
- Publication type:
- Correction Notice
Evidence of Multiyear Factor IX Expression by AAV-Mediated Gene Transfer to Skeletal Muscle in an Individual with Severe Hemophilia B.
- Published in:
- Molecular Therapy, 2006, v. 14, n. 3, p. 452, doi. 10.1016/j.ymthe.2006.05.004
- By:
- Publication type:
- Article
879. Effects of Continuous Expression of Activated Protein C (APC) in Novel Murine Thrombosis Models.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S338, doi. 10.1016/j.ymthe.2006.08.967
- By:
- Publication type:
- Article
1086. T Cell Responses to Canine Factor IX and AAV Capsid Antigens in Hemophilia B Dogs after Intravascular Gene Delivery to Skeletal Muscle.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S417, doi. 10.1016/j.ymthe.2006.08.1188
- By:
- Publication type:
- Article
39. Evaluation of rAAV-1 vs rAAV-8 Vectors and Their Mode of Delivery in Nonhuman Primate Skeletal Muscle<sup>*</sup>.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S16, doi. 10.1016/j.ymthe.2006.08.052
- By:
- Publication type:
- Article
66. Gene Transfer-Mediated Expression of Murine Factor VIIa Improves Clot Formation in a Mouse Model for Bernard-Soulier Syndrome.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S28, doi. 10.1016/j.ymthe.2006.08.082
- By:
- Publication type:
- Article
75. Protease-Activated Receptor 2 as a Novel Target for Immune Modulation for AAV-Mediated Gene Transfer to Skeletal Muscle.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S32, doi. 10.1016/j.ymthe.2006.08.092
- By:
- Publication type:
- Article
Inadvertent Germline Transmission of AAV2 Vector: Findings in a Rabbit Model Correlate with Those in a Human Clinical Trial.
- Published in:
- Molecular Therapy, 2006, v. 13, n. 6, p. 1064, doi. 10.1016/j.ymthe.2006.03.002
- By:
- Publication type:
- Article
The Inhibitory Effects of Anticoagulation on in Vivo Gene Transfer by Adeno-associated Viral or Adenoviral Vectors.
- Published in:
- Molecular Therapy, 2006, v. 13, n. 1, p. 88, doi. 10.1016/j.ymthe.2005.08.004
- By:
- Publication type:
- Article
1114. Antithrombotic Effects of Endogenous Expressed Activated Protein C (aPC) in Murine Models
- Published in:
- 2005
- By:
- Publication type:
- Abstract
Inhibitors—Recent insights.
- Published in:
- Haemophilia, 2021, v. 27, p. 28, doi. 10.1111/hae.14077
- By:
- Publication type:
- Article
Possible Association between Cytomegalovirus Infection and Gastrointestinal Bleeding in Hemophiliac Patients.
- Published in:
- Acta Haematologica, 2000, v. 103, n. 2, p. 73, doi. 10.1159/000041023
- By:
- Publication type:
- Article
Cytomegalovirus Infection as Cause of Severe Thrombocytopenia in a Nonimmunosuppressed Patient.
- Published in:
- Acta Haematologica, 1997, v. 98, n. 4, p. 228, doi. 10.1159/000203630
- By:
- Publication type:
- Article
G6PD Sumaré: A novel mutation in the G6PD gene (1292 T→G) associated with chronic nonspherocytic anemia.
- Published in:
- Human Mutation, 1997, v. 10, n. 3, p. 245, doi. 10.1002/(SICI)1098-1004(1997)10:3<245::AID-HUMU13>3.0.CO;2-#
- By:
- Publication type:
- Article
A Novel Splice Site Mutation in a Brazilian Patient with Hereditary Antithrombin Deficiency Type I.
- Published in:
- Human Heredity, 1999, v. 49, n. 2, p. 119, doi. 10.1159/000022856
- By:
- Publication type:
- Article
A Novel Nonsense Mutation 6, E - X in the Protein S Gene Causes Type I Deficiency.
- Published in:
- Human Heredity, 1999, v. 49, n. 2, p. 121, doi. 10.1159/000022857
- By:
- Publication type:
- Article
Determination of the Allele Frequencies of Three Polymorphisms in the Promoter Region of the Human Protein C Gene in Three Brazilian Ethnic Groups.
- Published in:
- Human Heredity, 1999, v. 49, n. 1, p. 27, doi. 10.1159/000022836
- By:
- Publication type:
- Article
The release of nitric oxide and superoxide anion by neutrophils and mononuclear cells from patients with sickle cell anaemia.
- Published in:
- British Journal of Haematology, 1996, v. 93, n. 2, p. 333, doi. 10.1046/j.1365-2141.1996.4951036.x
- By:
- Publication type:
- Article