Found: 16
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Splice-correcting oligonucleotides restore BTK function in X-linked agammaglobulinemia model.
- Published in:
- Journal of Clinical Investigation, 2014, v. 124, n. 9, p. 4067, doi. 10.1172/JCI76175
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- Article
Bi-specific splice-switching PMO oligonucleotides conjugated via a single peptide active in a mouse model of Duchenne muscular dystrophy.
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- Nucleic Acids Research, 2015, v. 43, n. 1, p. 29, doi. 10.1093/nar/gku1256
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- Article
Corrigendum: Identification of novel, therapy-responsive protein biomarkers in a mouse model of Duchenne muscular dystrophy by aptamer-based serum proteomics.
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- Scientific Reports, 2016, p. 37047, doi. 10.1038/srep37047
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- Article
Identification of novel, therapy-responsive protein biomarkers in a mouse model of Duchenne muscular dystrophy by aptamer-based serum proteomics.
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- Scientific Reports, 2015, p. 17014, doi. 10.1038/srep17014
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- Article
Dystrophin involvement in peripheral circadian SRF signalling.
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- Life Science Alliance, 2021, v. 4, n. 10, p. 1, doi. 10.26508/lsa.202101014
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- Article
Combination Antisense Treatment for Destructive Exon Skipping of Myostatin and Open Reading Frame Rescue of Dystrophin in Neonatal mdx Mice.
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- Molecular Therapy, 2015, v. 23, n. 8, p. 1341, doi. 10.1038/mt.2015.88
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- Article
In vitro evaluation of novel antisense oligonucleotides is predictive of in vivo exon skipping activity for Duchenne muscular dystrophy.
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- Journal of Gene Medicine, 2010, v. 12, n. 4, p. 354, doi. 10.1002/jgm.1446
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- Article
Enhancement of gene transfer using YIGSR analog of Tat-derived peptide.
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- Biopolymers, 2008, v. 89, n. 1, p. 62, doi. 10.1002/bip.20854
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- Article
Pip5 Transduction Peptides Direct High Efficiency Oligonucleotide-mediated Dystrophin Exon Skipping in Heart and Phenotypic Correction in mdx Mice.
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- Molecular Therapy, 2011, v. 19, n. 7, p. 1295, doi. 10.1038/mt.2011.79
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- Article
Optimization of Peptide Nucleic Acid Antisense Oligonucleotides for Local and Systemic Dystrophin Splice Correction in the mdx Mouse.
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- Molecular Therapy, 2010, v. 18, n. 4, p. 819, doi. 10.1038/mt.2009.310
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- Article
Implications for Cardiac Function Following Rescue of the Dystrophic Diaphragm in a Mouse Model of Duchenne Muscular Dystrophy.
- Published in:
- Scientific Reports, 2015, p. 11632, doi. 10.1038/srep11632
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- Article
Prevention of exercised induced cardiomyopathy following Pip-PMO treatment in dystrophic mdx mice.
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- Scientific Reports, 2015, p. 8986, doi. 10.1038/srep08986
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- Article
Diaphragm rescue alone prevents heart dysfunction in dystrophic mice.
- Published in:
- Human Molecular Genetics, 2011, v. 20, n. 3, p. 413, doi. 10.1093/hmg/ddq477
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- Article
2'-O-(2-Methoxyethyl) Nucleosides Are Not Phosphorylated or Incorporated Into the Genome of Human Lymphoblastoid TK6 Cells.
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- Toxicological Sciences, 2018, v. 163, n. 1, p. 70, doi. 10.1093/toxsci/kfy005
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- Article
The Lack of Mutagenic Potential of a Guanine-Rich Triplex Forming Oligonucleotide in Physiological Conditions.
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- Toxicological Sciences, 2017, v. 155, n. 1, p. 101, doi. 10.1093/toxsci/kfw179
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- Article
Re-evaluation of the Mutagenic Response to Phosphorothioate Nucleotides in Human Lymphoblastoid TK6 Cells.
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- Toxicological Sciences, 2015, v. 145, n. 1, p. 169, doi. 10.1093/toxsci/kfv043
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- Article