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Therapeutic expression of human clotting factors IX and X following adeno-associated viral vector-mediated intrauterine gene transfer in early-gestation fetal macaques.
Published in:
FASEB Journal, 2019, v. 33, n. 3, p. 3954, doi. 10.1096/fj.201801391R
By:
- Chan, Jerry K. Y.;
- Gil-Farina, Irene;
- Johana, Nuryanti;
- Rosales, Cecilia;
- Yi Wan Tan;
- Ceiler, Jessika;
- Mcintosh, Jenny;
- Ogden, Bryan;
- Waddington, Simon N.;
- Schmidt, Manfred;
- Biswas, Arijit;
- Choolani, Mahesh;
- Nathwani, Amit C.;
- Mattar, Citra N. Z.
Publication type:
Article
Feasibility of combined upper and lower gastrointestinal endoscopic biopsy in the common marmoset (Callithrix jacchus) to evaluate gastrointestinal diseases.
Published in:
Journal of Medical Primatology, 2022, v. 51, n. 3, p. 172, doi. 10.1111/jmp.12580
By:
- Heilmann, Romy M.;
- McIntosh, Jenny;
- Acke, Els;
- Reitemeier, Susanne;
- Pfannkuche, Helga;
- Erdmann, Sabrina;
- Roedler, Frauke S.;
- Einspanier, Almuth
Publication type:
Article
Performance of AAV8 vectors expressing human factor IX from a hepatic-selective promoter following intravenous injection into rats.
Published in:
Genetic Vaccines & Therapy, 2008, v. 6, p. 1, doi. 10.1186/1479-0556-6-9
By:
- Graham, Tracey;
- McIntosh, Jenny;
- Work, Lorraine M.;
- Nathwani, Amit;
- Baker, Andrew H.
Publication type:
Article
Coating of adeno-associated virus with reactive polymers can ablate virus tropism, enable retargeting and provide resistance to neutralising antisera.
Published in:
Journal of Gene Medicine, 2008, v. 10, n. 4, p. 400, doi. 10.1002/jgm.1161
By:
- Carlisle, Robert C.;
- Benjamin, Reuben;
- Briggs, Simon S.;
- Sumner-Jones, Stephanie;
- McIntosh, Jenny;
- Gill, Deborah;
- Hyde, Steve;
- Nathwani, Amit;
- Subr, Vladimir;
- Ulbrich, Karel;
- Seymour, Leonard W.;
- Fisher, Kerry D.
Publication type:
Article
Stable Human FIX Expression After 0.9G Intrauterine Gene Transfer of Self-complementary Adeno-associated Viral Vector 5 and 8 in Macaques.
Published in:
Molecular Therapy, 2011, v. 19, n. 11, p. 1950, doi. 10.1038/mt.2011.107
By:
- Mattar, Citra NZ;
- Nathwani, Amit C;
- Waddington, Simon N;
- Dighe, Niraja;
- Kaeppel, Christine;
- Nowrouzi, Ali;
- Mcintosh, Jenny;
- Johana, Nuryanti B;
- Ogden, Bryan;
- Fisk, Nicholas M;
- Davidoff, Andrew M;
- David, Anna;
- Peebles, Donald;
- Valentine, Marcus B;
- Appelt, Jens-Uwe;
- von Kalle, Christof;
- Schmidt, Manfred;
- Biswas, Arijit;
- Choolani, Mahesh;
- Chan, Jerry KY
Publication type:
Article
Long-term Safety and Efficacy Following Systemic Administration of a Self-complementary AAV Vector Encoding Human FIX Pseudotyped With Serotype 5 and 8 Capsid Proteins.
Published in:
Molecular Therapy, 2011, v. 19, n. 5, p. 876, doi. 10.1038/mt.2010.274
By:
- Nathwani, Amit C;
- Rosales, Cecilia;
- McIntosh, Jenny;
- Rastegarlari, Ghasem;
- Nathwani, Devhrut;
- Raj, Deepak;
- Nawathe, Sushmita;
- Waddington, Simon N;
- Bronson, Roderick;
- Jackson, Scott;
- Donahue, Robert E;
- High, Katherine A;
- Mingozzi, Federico;
- Ng, Catherine YC;
- Zhou, Junfang;
- Spence, Yunyu;
- McCarville, M Beth;
- Valentine, Marc;
- Allay, James;
- Coleman, John
Publication type:
Article
490. Successful Readministration of AAV8 Following Administration of Nondepleting CD4 Antibody at the Time of Vector Administration.
Published in:
Molecular Therapy, 2006, v. 13, p. S190, doi. 10.1016/j.ymthe.2006.08.560
By:
- McIntosh, Jenny H.;
- Cochrane, Melanie;
- Prizzey, Arnold;
- Waldmann, Herman;
- Davidoff, Andrew M.;
- Nathwani, Amit C.
Publication type:
Article
711. Treatment of Acute Myeloid Leukemia by rAAV 8 Vector Mediated Human Interferon-β Gene Transfer
Published in:
2005
By:
- Benjamin, Reuben;
- Davidoff, Andrew M.;
- Arnold, Pizzey;
- Singh, Nalini;
- Khwaja, Asim;
- McIntosh, Jenny;
- Ng, Cathy C.Y.;
- Meager, Tony;
- Wadhwa, Meenu;
- Nathwani, Amit C.
Publication type:
Abstract
Potential limits of AAV‐based gene therapy with the use of new transgenes expressing factor IX fusion proteins.
Published in:
Haemophilia, 2019, v. 25, n. 1, p. e11, doi. 10.1111/hae.13651
By:
- Le Quellec, Sandra;
- Enjolras, Nathalie;
- Negrier, Claude;
- Dane, Allison;
- McIntosh, Jenny;
- Rosales, Cecilia;
- Nathwani, Amit
Publication type:
Article
Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors.
Published in:
Human Molecular Genetics, 2010, v. 19, n. 4, p. 735, doi. 10.1093/hmg/ddp540
By:
- Tan, Mei Hong;
- Smith, Alexander J.;
- Pawlyk, Basil;
- Xu, Xiaoyun;
- Liu, Xiaoqing;
- Bainbridge, James B.;
- Basche, Mark;
- McIntosh, Jenny;
- Tran, Hoai Viet;
- Nathwani, Amit;
- Li, Tiansen;
- Ali, Robin R.
Publication type:
Article
Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors.
Published in:
Human Molecular Genetics, 2009, v. 18, n. 12, p. 2099, doi. 10.1093/hmg/ddp133
By:
- Tan, Mei Hong;
- Smith, Alexander J.;
- Pawlyk, Basil;
- Xu, Xiaoyun;
- Liu, Xiaoqing;
- Bainbridge, James B.;
- Basche, Mark;
- McIntosh, Jenny;
- Tran, Hoai Viet;
- Nathwani, Amit;
- Li, Tiansen;
- Ali, Robin R.
Publication type:
Article
Adeno-associated virus gene therapy prevents progression of kidney disease in genetic models of nephrotic syndrome.
Published in:
Science Translational Medicine, 2023, v. 15, n. 708, p. 1, doi. 10.1126/scitranslmed.abc8226
By:
- Ding, Wen Y.;
- Kuzmuk, Valeryia;
- Hunter, Sarah;
- Lay, Abigail;
- Hayes, Bryony;
- Beesley, Matthew;
- Rollason, Ruth;
- Hurcombe, Jennifer A.;
- Barrington, Fern;
- Masson, Catrin;
- Cathery, William;
- May, Carl;
- Tuffin, Jack;
- Roberts, Timothy;
- Mollet, Geraldine;
- Chu, Colin J.;
- McIntosh, Jenny;
- Coward, Richard J.;
- Antignac, Corinne;
- Nathwani, Amit
Publication type:
Article

Found: 12