Modifications to toxic CUG RNAs induce structural stability, rescue mis-splicing in a myotonic dystrophy cell model and reduce toxicity in a myotonic dystrophy zebrafish model.

Published in:

Nucleic Acids Research, 2014, v. 42, n. 20, p. 12768, doi. 10.1093/nar/gku941

By:

• deLorimier, Elaine;
• Coonrod, Leslie A.;
• Copperman, Jeremy;
• Taber, Alex;
• Reister, Emily E.;
• Sharma, Kush;
• Todd, Peter K.;
• Guenza, Marina G.;
• Berglund, J. Andrew

Publication type:

Article