Found: 52
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Use of the oxygen gradient ektacytometry in the dose titration of hydroxyurea therapy in children with sickle cell disease.
- Published in:
- 2024
- By:
- Publication type:
- Letter to the Editor
Platelet degranulation and bleeding phenotype in a large cohort of Von Willebrand disease patients.
- Published in:
- British Journal of Haematology, 2022, v. 197, n. 4, p. 497, doi. 10.1111/bjh.18145
- By:
- Publication type:
- Article
Comorbidities associated with higher von Willebrand factor (VWF) levels may explain the age‐related increase of VWF in von Willebrand disease.
- Published in:
- British Journal of Haematology, 2018, v. 182, n. 1, p. 93, doi. 10.1111/bjh.15277
- By:
- Publication type:
- Article
Intracranial 4D flow magnetic resonance imaging reveals altered haemodynamics in sickle cell disease.
- Published in:
- British Journal of Haematology, 2018, v. 180, n. 3, p. 432, doi. 10.1111/bjh.15043
- By:
- Publication type:
- Article
Adherence to prophylaxis and bleeding outcome in haemophilia: a multicentre study.
- Published in:
- British Journal of Haematology, 2016, v. 174, n. 3, p. 454, doi. 10.1111/bjh.14072
- By:
- Publication type:
- Article
Risk factor analysis of cerebral white matter hyperintensities in children with sickle cell disease.
- Published in:
- British Journal of Haematology, 2016, v. 172, n. 2, p. 274, doi. 10.1111/bjh.13819
- By:
- Publication type:
- Article
Volume of white matter hyperintensities is an independent predictor of intelligence quotient and processing speed in children with sickle cell disease.
- Published in:
- British Journal of Haematology, 2015, v. 168, n. 4, p. 553, doi. 10.1111/bjh.13179
- By:
- Publication type:
- Article
Silent cerebral infarcts in patients with sickle cell disease: a systematic review and meta-analysis.
- Published in:
- 2020
- By:
- Publication type:
- journal article
Long‐term follow‐up of children with sickle cell disease diagnosed by newborn screening in the Netherlands: Overview of morbidity and mortality.
- Published in:
- American Journal of Hematology, 2024, v. 99, n. 8, p. 1606, doi. 10.1002/ajh.27351
- By:
- Publication type:
- Article
Safety and efficacy of mitapivat, an oral pyruvate kinase activator, in sickle cell disease: A phase 2, open‐label study.
- Published in:
- American Journal of Hematology, 2022, v. 97, n. 7, p. E226, doi. 10.1002/ajh.26554
- By:
- Publication type:
- Article
Paediatric arterial ischaemic stroke: functional outcome and risk factors.
- Published in:
- Developmental Medicine & Child Neurology, 2010, v. 52, n. 4, p. 394, doi. 10.1111/j.1469-8749.2009.03580.x
- By:
- Publication type:
- Article
ChatGPT in pharmacometrics? Potential opportunities and limitations.
- Published in:
- British Journal of Clinical Pharmacology, 2024, v. 90, n. 1, p. 360, doi. 10.1111/bcp.15895
- By:
- Publication type:
- Article
A new population pharmacokinetic model for recombinant factor IX‐Fc fusion concentrate including young children with haemophilia B.
- Published in:
- British Journal of Clinical Pharmacology, 2024, v. 90, n. 1, p. 220, doi. 10.1111/bcp.15881
- By:
- Publication type:
- Article
Combining factor VIII levels and thrombin/plasmin generation: A population pharmacokinetic‐pharmacodynamic model for patients with haemophilia A.
- Published in:
- British Journal of Clinical Pharmacology, 2022, v. 88, n. 6, p. 2757, doi. 10.1111/bcp.15185
- By:
- Publication type:
- Article
Validation of a perioperative population factor VIII pharmacokinetic model with a large cohort of pediatric hemophilia a patients.
- Published in:
- British Journal of Clinical Pharmacology, 2021, v. 87, n. 11, p. 4408, doi. 10.1111/bcp.14864
- By:
- Publication type:
- Article
Dosing of factor VIII concentrate by ideal body weight is more accurate in overweight and obese haemophilia A patients.
- Published in:
- British Journal of Clinical Pharmacology, 2021, v. 87, n. 6, p. 2602, doi. 10.1111/bcp.14670
- By:
- Publication type:
- Article
Improving access to healthcare for paediatric sickle cell disease patients: a qualitative study on healthcare professionals' views.
- Published in:
- 2021
- By:
- Publication type:
- journal article
Patients with Chromosome 11q Deletions Are Characterized by Inborn Errors of Immunity Involving both B and T Lymphocytes.
- Published in:
- Journal of Clinical Immunology, 2022, v. 42, n. 7, p. 1521, doi. 10.1007/s10875-022-01303-8
- By:
- Publication type:
- Article
A Generative and Causal Pharmacokinetic Model for Factor VIII in Hemophilia A: A Machine Learning Framework for Continuous Model Refinement.
- Published in:
- Clinical Pharmacology & Therapeutics, 2024, v. 115, n. 4, p. 881, doi. 10.1002/cpt.3203
- By:
- Publication type:
- Article
PBPK modeling of recombinant factor IX Fc fusion protein (rFIXFc) and rFIX to characterize the binding to type 4 collagen in the extravascular space.
- Published in:
- CPT: Pharmacometrics & Systems Pharmacology, 2024, v. 13, n. 10, p. 1630, doi. 10.1002/psp4.13159
- By:
- Publication type:
- Article
Relationship between factor VIII levels and bleeding for rFVIII‐SingleChain in severe hemophilia A: A repeated time‐to‐event analysis.
- Published in:
- CPT: Pharmacometrics & Systems Pharmacology, 2023, v. 12, n. 5, p. 706, doi. 10.1002/psp4.12938
- By:
- Publication type:
- Article
Application of SHAP values for inferring the optimal functional form of covariates in pharmacokinetic modeling.
- Published in:
- CPT: Pharmacometrics & Systems Pharmacology, 2022, v. 11, n. 8, p. 1100, doi. 10.1002/psp4.12828
- By:
- Publication type:
- Article
Deep compartment models: A deep learning approach for the reliable prediction of time‐series data in pharmacokinetic modeling.
- Published in:
- CPT: Pharmacometrics & Systems Pharmacology, 2022, v. 11, n. 7, p. 934, doi. 10.1002/psp4.12808
- By:
- Publication type:
- Article
Circadian Variation of Plasminogen-Activator-Inhibitor-1 Levels in Children with Meningococcal Sepsis.
- Published in:
- PLoS ONE, 2016, v. 11, n. 11, p. 1, doi. 10.1371/journal.pone.0167004
- By:
- Publication type:
- Article
Should HLA and HPA‐matched platelet transfusions for patients with Glanzmann Thrombasthenia or Bernard‐Soulier syndrome be standardized care? A Dutch survey and recommendations.
- Published in:
- Transfusion, 2024, v. 64, n. 5, p. 824, doi. 10.1111/trf.17824
- By:
- Publication type:
- Article
Health‐related quality of life in infants, toddlers and young children with sickle cell disease.
- Published in:
- Pediatric Blood & Cancer, 2022, v. 69, n. 1, p. 1, doi. 10.1002/pbc.29358
- By:
- Publication type:
- Article
Cost of health care for paediatric patients with sickle cell disease: An analysis of resource use and costs in a European country.
- Published in:
- 2020
- By:
- Publication type:
- journal article
Pitfalls in the diagnosis of hemophilia severity: What to do?
- Published in:
- 2017
- By:
- Publication type:
- journal article
On inductive biases for the robust and interpretable prediction of drug concentrations using deep compartment models.
- Published in:
- Journal of Pharmacokinetics & Pharmacodynamics, 2024, v. 51, n. 4, p. 355, doi. 10.1007/s10928-024-09906-x
- By:
- Publication type:
- Article
Oxygen gradient ektacytometry‐derived biomarkers are associated with vaso‐occlusive crises and correlate with treatment response in sickle cell disease.
- Published in:
- American Journal of Hematology, 2021, v. 96, n. 1, p. E29, doi. 10.1002/ajh.26031
- By:
- Publication type:
- Article
BMI is an important determinant of VWF and FVIII levels and bleeding phenotype in patients with von Willebrand disease.
- Published in:
- American Journal of Hematology, 2019, v. 94, n. 8, p. E201, doi. 10.1002/ajh.25499
- By:
- Publication type:
- Article
Rapid and reproducible characterization of sickling during automated deoxygenation in sickle cell disease patients.
- Published in:
- American Journal of Hematology, 2019, v. 94, n. 5, p. 575, doi. 10.1002/ajh.25443
- By:
- Publication type:
- Article
Early occurrence of red blood cell alloimmunization in patients with sickle cell disease.
- Published in:
- American Journal of Hematology, 2016, v. 91, n. 8, p. 763, doi. 10.1002/ajh.24397
- By:
- Publication type:
- Article
Bleeding spectrum in children with moderate or severe von Willebrand disease: Relevance of pediatric-specific bleeding.
- Published in:
- American Journal of Hematology, 2015, v. 90, n. 12, p. 1142, doi. 10.1002/ajh.24195
- By:
- Publication type:
- Article
Population Pharmacokinetics of Clotting Factor Concentrates and Desmopressin in Hemophilia.
- Published in:
- Clinical Pharmacokinetics, 2021, v. 60, n. 1, p. 1, doi. 10.1007/s40262-020-00936-5
- By:
- Publication type:
- Article
Peri‐operative desmopressin combined with pharmacokinetic‐guided factor VIII concentrate in non‐severe haemophilia A patients.
- Published in:
- Haemophilia, 2024, v. 30, n. 2, p. 355, doi. 10.1111/hae.14946
- By:
- Publication type:
- Article
Knowledge gaps in health‐related quality of life research performed in children with bleeding disorders – A scoping review.
- Published in:
- Haemophilia, 2024, v. 30, n. 2, p. 295, doi. 10.1111/hae.14941
- By:
- Publication type:
- Article
Transition readiness among adolescents and young adults with haemophilia in the Netherlands: Nationwide questionnaire study.
- Published in:
- Haemophilia, 2023, v. 29, n. 5, p. 1191, doi. 10.1111/hae.14834
- By:
- Publication type:
- Article
Harmonizing patient‐reported outcome measurements in inherited bleeding disorders with PROMIS.
- Published in:
- Haemophilia, 2023, v. 29, n. 1, p. 357, doi. 10.1111/hae.14694
- By:
- Publication type:
- Article
Quantification of the relationship between desmopressin concentration and Von Willebrand factor in Von Willebrand disease type 1: A pharmacodynamic study.
- Published in:
- Haemophilia, 2022, v. 28, n. 5, p. 814, doi. 10.1111/hae.14582
- By:
- Publication type:
- Article
Does difference between label and actual potency of factor VIII concentrate affect pharmacokinetic‐guided dosing of replacement therapy in haemophilia A?
- Published in:
- Haemophilia, 2022, v. 28, n. 4, p. 610, doi. 10.1111/hae.14575
- By:
- Publication type:
- Article
Patient‐reported outcomes in autosomal inherited bleeding disorders: A systematic literature review.
- Published in:
- Haemophilia, 2022, v. 28, n. 2, p. 197, doi. 10.1111/hae.14492
- By:
- Publication type:
- Article
Social participation is reduced in type 3 Von Willebrand disease patients and in patients with a severe bleeding phenotype.
- Published in:
- Haemophilia, 2022, v. 28, n. 2, p. 278, doi. 10.1111/hae.14475
- By:
- Publication type:
- Article
Pharmacokinetics of perioperative FVIII in adult patients with haemophilia A: An external validation and development of an alternative population pharmacokinetic model.
- Published in:
- Haemophilia, 2021, v. 27, n. 6, p. 974, doi. 10.1111/hae.14393
- By:
- Publication type:
- Article
The association between desmopressin exposure, FVIII response and side effects.
- Published in:
- Haemophilia, 2021, v. 27, n. 4, p. e506, doi. 10.1111/hae.14227
- By:
- Publication type:
- Article
The one‐stage assay or chromogenic assay to monitor baseline factor VIII levels and desmopressin effect in non‐severe haemophilia A: Superiority or non‐inferiority?
- Published in:
- Haemophilia, 2020, v. 26, n. 5, p. 916, doi. 10.1111/hae.14106
- By:
- Publication type:
- Article
Evaluation of thromboelastometry, thrombin generation and plasma clot lysis time in patients with bleeding of unknown cause: A prospective cohort study.
- Published in:
- Haemophilia, 2020, v. 26, n. 3, p. e106, doi. 10.1111/hae.13991
- By:
- Publication type:
- Article
Current dosing practices for perioperative factor VIII concentrate treatment in mild haemophilia A patients result in FVIII levels above target.
- Published in:
- Haemophilia, 2019, v. 25, n. 6, p. 960, doi. 10.1111/hae.13838
- By:
- Publication type:
- Article
Analytical variation in factor VIII one‐stage and chromogenic assays: Experiences from the ECAT external quality assessment programme.
- Published in:
- Haemophilia, 2019, v. 25, n. 1, p. 162, doi. 10.1111/hae.13643
- By:
- Publication type:
- Article
Sports participation and physical activity in patients with von Willebrand disease.
- Published in:
- Haemophilia, 2019, v. 25, n. 1, p. 101, doi. 10.1111/hae.13629
- By:
- Publication type:
- Article