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- Title
Perspective: The fix is in.
- Authors
Pemberton, Stephen
- Abstract
The author discusses reasons why haemophilia researchers are wary of a possible cure for the disease. Haemophilia treatment-related tragedies such as the death of clinical trial patient Jesse Gelsinger in 1999 and transfusion of HIV-infected blood among hemophilia patients in the 1980s are mentioned. Other topics are clotting-factor-replacement injections, ethical issues, a gene therapy involving transfer of an adeno-associated virus (AAV), and the challenge of finding a cure for Haemophilia A.
- Subjects
HEMOPHILIA; HEMOPHILIA treatment; GELSINGER, Jesse; ADENO-associated virus; ETHICS; GENE therapy; THERAPEUTICS
- Publication
Nature, 2014, Vol 515, Issue s7528, pS165
- ISSN
0028-0836
- Publication type
Article
- DOI
10.1038/515S165a