Back to matchesWe found a matchYour institution may have access to this item. Find your institution then sign in to continue.TitleFDA Approval of Eteplirsen for Muscular Dystrophy-Reply.AuthorsKesselheim, Aaron S.; Avorn, JerrySubjectsUNITED States. Food &; Drug Administration; DRUG approval; MUSCULAR dystrophy treatmentPublicationJAMA: Journal of the American Medical Association, 2017, Vol 317, Issue 14, p1481ISSN0098-7484Publication typeletterDOI10.1001/jama.2017.2605