Back to matchesWe found a matchYour institution may have access to this item. Find your institution then sign in to continue.TitleThe Case for the Use of Patient and Caregiver Perception of Change Assessments in Rare Disease Clinical Trials: A Methodologic Overview.AuthorsContesse, Marielle G.; Valentine, James E.; Wall, Tracy E.; Leffler, Mindy G.PublicationAdvances in Therapy, 2019, Vol 36, Issue 5, p997ISSN0741-238XPublication typejournal articleDOI10.1007/s12325-019-00920-x