Back to matchesWe found a matchYour institution may have access to this item. Find your institution then sign in to continue.TitleTransplantation as disease modifying therapy in adults with inherited metabolic disorders.AuthorsSirrs, Sandra; Hannah-Shmouni, Fady; Nantel, Stephen; Neuberger, James; Yoshida, Eric M.PublicationJournal of Inherited Metabolic Disease, 2018, Vol 41, Issue 5, p885ISSN0141-8955Publication typeArticleDOI10.1007/s10545-018-0141-z