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- Title
Trofinetide--a new chapter in rett syndrome's treatment.
- Authors
Furqan, Muhammad
- Abstract
Trofinetide is the first drug approved by the FDA to treat Rett Syndrome in children aged 2 years or above. The drug significantly improved Rett syndrome behavioral scores Rett syndrome behavioral questionnaire in clinical studies. Although further research is needed to assess potential adverse events, Trofinetide's notable efficacy signifies a significant advancement in Rett syndrome treatment, offering a new therapeutic avenue with the potential to ameliorate the condition.
- Subjects
UNITED States. Food &; Drug Administration; RETT syndrome; SYNDROMES in children
- Publication
Frontiers in Pharmacology, 2023, p01
- ISSN
1663-9812
- Publication type
Article
- DOI
10.3389/fphar.2023.1284035