Found: 26
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In vivo adenine base editing reverts C282Y and improves iron metabolism in hemochromatosis mice.
- Published in:
- Nature Communications, 2022, v. 13, n. 1, p. 1, doi. 10.1038/s41467-022-32906-9
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- Publication type:
- Article
Pathological mechanism and antisense oligonucleotide-mediated rescue of a non-coding variant suppressing factor 9 RNA biogenesis leading to hemophilia B.
- Published in:
- PLoS Genetics, 2020, v. 16, n. 4, p. 1, doi. 10.1371/journal.pgen.1008690
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- Publication type:
- Article
Site specific target binding controls RNA cleavage efficiency by the Kaposi's sarcoma-associated herpesvirus endonuclease SOX.
- Published in:
- Nucleic Acids Research, 2018, v. 46, n. 22, p. 11968, doi. 10.1093/nar/gky932
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- Publication type:
- Article
Limited complementarity between U1 snRNA and a retroviral 5′ splice site permits its attenuation via RNA secondary structure.
- Published in:
- Nucleic Acids Research, 2009, v. 37, n. 22, p. 7429, doi. 10.1093/nar/gkp694
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- Publication type:
- Article
Correction: Pathological mechanism and antisense oligonucleotide-mediated rescue of a non-coding variant suppressing factor 9 RNA biogenesis leading to hemophilia B.
- Published in:
- 2021
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- Publication type:
- Correction Notice
The retroviral vector family: something for everyone.
- Published in:
- Virus Genes, 2017, v. 53, n. 5, p. 714, doi. 10.1007/s11262-017-1489-0
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- Publication type:
- Article
Training the Next Generation of Infectious Disease Researchers: A Biorisk Management Module Embedded in a European Master Program.
- Published in:
- Applied Biosafety: Journal of the American Biological Safety Association, 2024, v. 29, n. 2, p. 26, doi. 10.1089/apb.2023.0015
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- Publication type:
- Article
Peptide nanofibrils boost retroviral gene transfer and provide a rapid means for concentrating viruses.
- Published in:
- Nature Nanotechnology, 2013, v. 8, n. 2, p. 130, doi. 10.1038/nnano.2012.248
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- Article
A complex immunodeficiency is based on U1 snRNP-mediated poly(A) site suppression.
- Published in:
- EMBO Journal, 2012, v. 31, n. 20, p. 4035, doi. 10.1038/emboj.2012.252
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- Publication type:
- Article
Splicing of human immunodeficiency virus RNA is position-dependent suggesting sequential removal of introns from the 5′ end.
- Published in:
- Nucleic Acids Research, 2005, v. 33, n. 3, p. 825, doi. 10.1093/nar/gki185
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- Publication type:
- Article
Assembly of infectious Kaposi's sarcoma-associated herpesvirus progeny requires formation of a pORF19 pentamer.
- Published in:
- PLoS Biology, 2021, v. 19, n. 11, p. 1, doi. 10.1371/journal.pbio.3001423
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- Publication type:
- Article
The Inhibition of Gag-Pol Expression by the Restriction Factor Shiftless Is Dispensable for the Restriction of HIV-1 Infection.
- Published in:
- Viruses (1999-4915), 2024, v. 16, n. 4, p. 583, doi. 10.3390/v16040583
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- Publication type:
- Article
The HIV 5′ Gag Region Displays a Specific Nucleotide Bias Regulating Viral Splicing and Infectivity.
- Published in:
- Viruses (1999-4915), 2021, v. 13, n. 6, p. 997, doi. 10.3390/v13060997
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- Publication type:
- Article
Functional characterization of a JAG1 5'UTR variant in a patient with clinically observed Alagille syndrome.
- Published in:
- Clinical Genetics, 2022, v. 102, n. 3, p. 248, doi. 10.1111/cge.14179
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- Publication type:
- Article
A transposable element prevents severe hemophilia B and provides insights into the evolution of new- and old world primates.
- Published in:
- PLoS ONE, 2024, v. 19, n. 10, p. 1, doi. 10.1371/journal.pone.0312303
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- Publication type:
- Article
Alternative Splicing Rescues Loss of Common Gamma Chain Function and Results in IL-21R-like Deficiency.
- Published in:
- Journal of Clinical Immunology, 2019, v. 39, n. 2, p. 207, doi. 10.1007/s10875-019-00606-7
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- Publication type:
- Article
Very Early Onset Inflammatory Bowel Disease Associated with Aberrant Trafficking of IL-10R1 and Cure by T Cell Replete Haploidentical Bone Marrow Transplantation.
- Published in:
- Journal of Clinical Immunology, 2014, v. 34, n. 3, p. 331, doi. 10.1007/s10875-014-9992-8
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- Publication type:
- Article
Expression analysis and mapping of the mouse and human transcriptional regulator CA150.
- Published in:
- Mammalian Genome, 2000, v. 11, n. 10, p. 930, doi. 10.1007/s003350010162
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- Publication type:
- Article
Retrovirus Vectors: Toward the Plentivirus?
- Published in:
- Molecular Therapy, 2006, v. 13, n. 6, p. 1050, doi. 10.1016/j.ymthe.2006.03.007
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- Publication type:
- Article
Equal Potency of Gammaretroviral and Lentiviral SIN Vectors for Expression of O<sup>6</sup>-Methylguanine–DNA Methyltransferase in Hematopoietic cells.
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- Molecular Therapy, 2006, v. 13, n. 2, p. 391, doi. 10.1016/j.ymthe.2005.08.012
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- Publication type:
- Article
829. Design of a Safe and Efficient Vector for Bone Marrow Chemoprotection by O<sup>6</sup>-Methyl-Guanine-DNA-MethylTransferase
- Published in:
- 2005
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- Publication type:
- Abstract
A Novel Alu Element Insertion in ATM Induces Exon Skipping in Suspected HBOC Patients.
- Published in:
- Human Mutation, 2023, p. 1, doi. 10.1155/2023/6623515
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- Publication type:
- Article
Mutation of the major 5′ splice site renders a CMV-driven HIV-1 proviral clone Tat-dependent: connections between transcription and splicing
- Published in:
- FEBS Letters, 2004, v. 563, n. 1-3, p. 113, doi. 10.1016/S0014-5793(04)00277-7
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- Publication type:
- Article
Two sides of the same medal: Noncoding mutations reveal new pathological mechanisms and insights into the regulation of gene expression.
- Published in:
- Wiley Interdisciplinary Reviews: RNA, 2021, v. 12, n. 1, p. 1, doi. 10.1002/wrna.1616
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- Publication type:
- Article
The KSHV RNA regulator ORF57: target specificity and its role in the viral life cycle.
- Published in:
- Wiley Interdisciplinary Reviews: RNA, 2016, v. 7, n. 2, p. 173, doi. 10.1002/wrna.1323
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- Publication type:
- Article
U1snRNP-mediated suppression of polyadenylation in conjunction with the RNA structure controls poly (A) site selection in foamy viruses.
- Published in:
- Retrovirology, 2013, v. 10, n. 1, p. 1, doi. 10.1186/1742-4690-10-55
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- Publication type:
- Article